Heredodegeneratív rendellenességek, idegrendszerの臨床試験
合計1772件
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National Human Genome Research Institute (NHGRI)完了
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University of NancyCentral Hospital, Nancy, France完了
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University of VersaillesAssistance Publique - Hôpitaux de Paris; Association Française contre les Myopathies (AFM),...完了
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University of Texas募集
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Beyond Batten Disease FoundationTheranexus積極的、募集していない
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO Milano完了
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AMO Pharma Limited募集
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)完了
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena...募集
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione Policlinico Universitario... と他の協力者積極的、募集していない
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Centre Hospitalier Universitaire de Nice引きこもった筋緊張性ジストロフィー 1
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AMO Pharma Limited完了
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Newcastle-upon-Tyne Hospitals NHS Trust完了
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University of Florida; Stanford... と他の協力者完了
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Stanford Universityわからない
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed Incorporated完了
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Institut de Myologie, France招待による登録
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)積極的、募集していない
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Insmed IncorporatedMuscular Dystrophy Association完了
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer Children's Hospital...募集
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University of Iowa; University... と他の協力者募集筋緊張性ジストロフィー 1アメリカ, オランダ, イギリス, ニュージーランド, ドイツ, イタリア, カナダ, フランス
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Rett Syndrome Research TrustVanderbilt University Medical Center完了