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Kliniske studier på X-linked Adrenal Hypoplasia Congenita
Totalt 2204 resultater
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Neurogene Inc.RekrutteringRett syndromForente stater
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University of SienaRekruttering
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Vyant BioHar ikke rekruttert ennå
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Rett Syndrome Research TrustVanderbilt University Medical CenterFullført
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHFullførtRett syndromCanada, Australia, Storbritannia
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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Rett Syndrome Research TrustFullført
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National Human Genome Research Institute (NHGRI)FullførtRett syndromForente stater
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Ukjent
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Assistance Publique Hopitaux De MarseilleUkjent
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationFullført
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Sheba Medical CenterUltragenyx Pharmaceutical IncUkjent
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Central Hospital, Nancy, FranceFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...Avsluttet
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Sheba Medical CenterUkjent
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Maastricht University Medical CenterFullført
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Faculdades Metropolitanas UnidasUniversity of Sao PauloFullført
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityFullførtRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkjentRett syndromForente stater
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IRCCS San RaffaeleFondazione TelethonRekrutteringKronisk granulomatøs sykdom X-bundet (X-CGD)Italia
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Pitié-Salpêtrière HospitalRekrutteringLaminopatier | EmerinopatierFrankrike
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Children's Hospital of Chongqing Medical UniversityRekruttering
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University Hospital, Basel, SwitzerlandNovartisFullført
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Crinetics Pharmaceuticals Inc.RekrutteringMedfødt binyrehyperplasi | Klassisk medfødt binyrehyperplasiBrasil, India, Forente stater, Argentina, Italia, Storbritannia
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Eunice Kennedy Shriver National Institute of Child...FullførtMedfødt binyrehyperplasi (CAH)Forente stater
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Hospices Civils de LyonFullførtKlassisk medfødt binyrehyperplasiFrankrike
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dr. Laura C. G. de Graaff-HerderHar ikke rekruttert ennåMedfødt binyrehyperplasi | Hypogonadotropisk hypogonadisme | Mangel på veksthormon | Turners syndrom | Addisons sykdom | Klinefelters syndrom | Kombinert hypofysehormonmangel | Androgen ufølsomhetssyndrom | Skjoldbrusk dysgeneseSpania, Storbritannia, Belgia, Nederland
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Fullført
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUkjentAdrenoleukodystrofiTaiwan
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Great Ormond Street Hospital for Children NHS Foundation...RekrutteringAlvorlig kombinert immunsvikt, X-kobletStorbritannia
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForente stater, Storbritannia
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForente stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbeidspartnereRekruttering
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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Edison Pharmaceuticals IncTilbaketrukket
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Anavex Life Sciences Corp.Fullført
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbeidspartnereFullført
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Neuren Pharmaceuticals Limitedrettsyndrome.orgFullført
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkjentRett syndromDanmark, Israel
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Rigshospitalet, DenmarkFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)FullførtRett syndromForente stater
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Edison Pharmaceuticals IncFullført
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Boston Children's HospitalInternational Rett Syndrome FoundationFullført
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The Cleveland ClinicAvsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationFullført
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National Taiwan University HospitalUkjent
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Maastricht University Medical CenterFullført
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineFullførtRett syndrom