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Clinical Trials on Anderson-Fabrys sygdom in United Kingdom
I alt 147178 resultater
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Baylor Research InstituteNational Institute of Neurological Disorders and Stroke (NINDS)Afsluttet
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Distal myopati med kantede vakuoler | Distal myopati, Nonaka TypeForenede Stater, Canada, Det Forenede Kongerige, Israel, Italien, Bulgarien, Frankrig
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Amicus TherapeuticsAfsluttetFabrys sygdomForenede Stater
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Research SourceTilmelding efter invitationCervikal diskus sygdomForenede Stater
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereUkendt
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Astellas Pharma Global Development, Inc.Ikke længere tilgængeligAkut myeloid leukæmi (AML) | FMS-lignende Tyrosinkinase-3 (FLT3) mutationerAustralien, Italien, Det Forenede Kongerige
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Hoffmann-La RocheChugai PharmaceuticalRekrutteringMyelin Oligodendrocyt Glycoprotein Antistof-Associated Disease (MOGAD)Canada, Forenede Stater, Korea, Republikken, Australien, Japan, Italien, Brasilien, Tyskland, Frankrig, Kina, Israel
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Ultragenyx Pharmaceutical IncNewcastle UniversityAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Nonaka sygdom | Quadriceps Sparing Myopati (QSM) | Distal myopati med kantede vakuoler (DMRV)Forenede Stater, Bulgarien, Canada, Frankrig, Det Forenede Kongerige
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University of MinnesotaGenzyme, a Sanofi CompanyTrukket tilbageNeuropatisk smerte | Fabrys sygdomForenede Stater
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Distal myopati med kantede vakuoler | Distal myopati, Nonaka Type | Quadriceps sparende myopatiForenede Stater, Canada, Det Forenede Kongerige, Israel, Italien, Bulgarien, Frankrig
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NYU Langone HealthAfsluttet
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Amicus TherapeuticsEngage Health Inc.Afsluttet
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Baylor Research InstituteAfsluttet
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Optimal Health ResearchAfsluttetPost-Lyme Disease Syndrome (PLDS)Forenede Stater
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Alexion PharmaceuticalsAfsluttetLysosomal Acid Lipase-mangel | Cholesterol Ester Storage Disease (CESD) | LAL-mangelFrankrig, Forenede Stater, Det Forenede Kongerige, Tjekkiet
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University of Alabama at BirminghamAfsluttetProteinuri | Fabrys sygdomForenede Stater, Slovenien
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereRekruttering
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Spaulding Rehabilitation HospitalSuspenderet
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Optimal Health ResearchAfsluttetPost-Lyme Disease Syndrome (PLDS)Forenede Stater
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Mayo ClinicAfsluttetDistal pancreatektomiForenede Stater
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Baylor Research InstituteShireUkendtLivskvalitet | Nyreinsufficiens | HjertebegivenhedForenede Stater
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Freeman-Sheldon Research Group, Inc.AfsluttetKraniofaciale abnormiteter | Arthrogryposis | Freeman-Sheldon syndrom | Arthrogryposis Distal Type 2A | Whistling Face Syndrome | Kraniocarpotarsal dysplasi | Kraniocarpotarsal dystrofi | Freeman-Sheldon syndrom variant | Sheldon-Hall syndrom | Arthrogryposis Distal Type 2B | Gordon syndrom | Arthrogryposis Distal... og andre forholdForenede Stater
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National Institute of Allergy and Infectious Diseases...Rekruttering
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Kemin Foods LCDSM Nutritional Products, Inc.Afsluttet
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRekrutteringPyruvat dehydrogenase kompleks mangel | Pyruvat dehydrogenase E1 alfa-mangel | Pyruvat Dehydrogenase E1-Beta mangel | Pyruvat dehydrogenase E2 mangel | Pyruvat Dehydrogenase Phosphatase mangelDet Forenede Kongerige
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Swedish Orphan BiovitrumAfsluttetArthritis, Juvenil | Lymfohistiocytose, hæmofagocytisk | Makrofageaktiveringssyndrom | Stadig voksendebuterende sygdomForenede Stater, Spanien, Det Forenede Kongerige, Frankrig, Italien
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Mead Johnson NutritionTrukket tilbageKomælksallergi | Intolerance over for omfattende hydrolyserede formler | Intolerance over for modermælkDet Forenede Kongerige
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)AfsluttetGraft Versus Host Disease (GVHD)Forenede Stater
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Alexion PharmaceuticalsAfsluttetLysosomal Acid Lipase-mangel | LAL-mangel | Cholesterol Ester Storage Disease (CESD)Frankrig, Det Forenede Kongerige, Forenede Stater, Canada, Tjekkiet
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Massachusetts General HospitalGenzyme, a Sanofi Company; Scott and White Hospital & ClinicAfsluttetNyresygdomme | Genetiske sygdomme, X-forbundet | Slutstadie nyresygdom | ESRD | Fabrys sygdom | Sjældne sygdommeForenede Stater
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Massachusetts General HospitalAO foundationAfsluttetEkstraartikulær distal radius malunionForenede Stater
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Genzyme, a Sanofi CompanyCRL/MedinetAfsluttetFabrys sygdom | Kronisk nyresygdom, stadium IV (alvorlig)Forenede Stater
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Research Foundation for Mental Hygiene, Inc.AfsluttetEfterbehandling Lyme Disease SyndromeForenede Stater
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Loma Linda UniversityAfsluttetKnækirurgi | Distal lårben | Proksimal tibialForenede Stater
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Children's Hospital Medical Center, CincinnatiAfsluttetGraft Versus Host Disease (GVHD) | Diagnoser, der kræver stamcelletransplantationForenede Stater
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Hannah Choe, MDNational Cancer Institute (NCI); PlexxikonAfsluttetAkut graft versus værtssygdom | Steroid Refractory Graft Versus Host DiseaseForenede Stater
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CSL BehringNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... og andre samarbejdspartnereAktiv, ikke rekrutterendeGraft Versus Host Disease (GVHD)Forenede Stater
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AdventHealth Translational Research InstituteAfsluttetNASH - Ikke-alkoholisk Steatohepatitis; NAFLD - Nonalcoholic Fatty Lever DiseaseForenede Stater
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National Institute of Diabetes and Digestive and...Johns Hopkins UniversityAfsluttetNAFLD - Nonalcoholic Fatty Lever DiseaseForenede Stater
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Amicus TherapeuticsRekrutteringFabrys sygdomSpanien, Forenede Stater, Japan, Australien, Frankrig, Portugal
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Medrobotics CorporationUkendtSygdom eller læsioner i anus, rektum eller distal tyktarmForenede Stater
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M.D. Anderson Cancer CenterSuspenderetTyktarmskræft | Resected StageForenede Stater
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University of PennsylvaniaRekrutteringCastlemans sygdom | Castlemans sygdom, multicentriskForenede Stater
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Epizon Pharma, Inc.AfsluttetEnd-Stage Renal Disease (ESRD)Forenede Stater
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Johns Hopkins UniversityMedical University of South Carolina; University of Colorado, Denver; All... og andre samarbejdspartnereAfsluttetOndartet distal biliær obstruktionForenede Stater, Indien, Japan, Italien, Holland
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University of UtahAfsluttetDominantly Inherited Stargardt's Disease (STGD3)Forenede Stater
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NuVasiveAfsluttetCervikal diskus degenerativ lidelseForenede Stater
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NuVasiveTilmelding efter invitationDegenerativ diskussygdom | Cervikal diskus sygdomForenede Stater
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RekrutteringHæmatopoietisk og lymfoid celle-neoplasma | Steroid Refractory Graft Versus Host DiseaseForenede Stater
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Synthes USA HQ, Inc.AfsluttetCervikal diskus sygdomForenede Stater