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Clinical Trials on Pyruvat metabolisme, medfødte fejl in United States
I alt 2366 resultater
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AlexionRekruttering
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Brigham and Women's HospitalAktiv, ikke rekrutterendeASCVD | Hyperlipæmi, blandetForenede Stater
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Dr. Schär AG / SPAAfsluttetFenylketonuri | Medfødte metabolismefejl | Metabolisk sygdom | PKUDet Forenede Kongerige
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldAktiv, ikke rekrutterende
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Lumos DiagnosticsAptatek BiosciencesRekruttering
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Emory UniversityBioMarin PharmaceuticalRekrutteringFenylketonuriForenede Stater
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Rubius TherapeuticsAfsluttet
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Boston Children's HospitalBrigham and Women's HospitalAfsluttet
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalAfsluttetFenylketonuriForenede Stater
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University of Missouri-ColumbiaBioMarin PharmaceuticalAfsluttetFenylketonuriForenede Stater
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Emory UniversityAtlanta Clinical and Translational Science InstituteAfsluttet
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The University of Texas Health Science Center,...BioMarin PharmaceuticalAfsluttetFenylketonuri | HyperphenylalaninæmiForenede Stater
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalAfsluttetFenylketonuriForenede Stater
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The University of Texas Health Science Center,...BioMarin PharmaceuticalAfsluttet
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationAfsluttetHomozygot familiær hyperkolesterolæmiForenede Stater
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Massachusetts General HospitalRekruttering
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PTC TherapeuticsRekrutteringFenylketonuriForenede Stater
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Boston Children's HospitalBioMarin PharmaceuticalAfsluttetFenylketonuriForenede Stater
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University of NebraskaAfsluttet
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University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalAfsluttet
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The University of Texas Medical Branch, GalvestonAfsluttet
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Boston Children's HospitalBioMarin PharmaceuticalAfsluttet
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Oregon Health and Science UniversityAfsluttet
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UniQure Biopharma B.V.Chiesi Farmaceutici S.p.A.Trukket tilbage
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University of California, San DiegoAfsluttetAlkaptonuriaForenede Stater
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Vanderbilt University Medical CenterRekrutteringPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofi | PseudohypoparathyroidismeForenede Stater
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Ashley ShoemakerTilmelding efter invitationPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofi | PseudohypoparathyroidismeForenede Stater
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Vanderbilt University Medical CenterMassachusetts General HospitalAfsluttetPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofiForenede Stater
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Medical Research Laboratories InternationalAfsluttetFamiliær hyperkolesterolæmiHolland, Forenede Stater, Norge
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Sheffield Teaching Hospitals NHS Foundation TrustAfsluttet
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National Human Genome Research Institute (NHGRI)RekrutteringPropionsyreacidæmi | Metabolisk sygdom | Organisk AcidæmiForenede Stater
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Vitaflo International, LtdAfsluttet
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalAfsluttet
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Shoji YanoBioMarin PharmaceuticalAfsluttetFenylketonuriForenede Stater
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Vitaflo International, LtdOregon Health and Science UniversityAfsluttet
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Children's Hospital Medical Center, CincinnatiBioMarin PharmaceuticalAfsluttet
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University of MiamiAfsluttetFenylketonuriForenede Stater
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Children's Hospital of PhiladelphiaAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Afsluttet
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University of Southern CaliforniaNational PKU AllianceAktiv, ikke rekrutterende
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteAfsluttet
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National Human Genome Research Institute (NHGRI)Rekruttering
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TakedaAfsluttetHyperkolesterolæmiFrankrig, Det Forenede Kongerige, Forenede Stater, Israel, Polen, Canada
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustAfsluttetFenylketonuri | Medfødte metabolismefejlDet Forenede Kongerige
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRekrutteringFamiliær hyperkolesterolæmi | Genetisk sygdom | Kolesterol, forhøjetForenede Stater
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National Heart, Lung, and Blood Institute (NHLBI)Afsluttet
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Alexion Pharmaceuticals, Inc.RekrutteringHypofosfatasiAustralien, Forenede Stater, Japan, Tyskland, Kalkun, Italien, Indien, Frankrig, Det Forenede Kongerige, Argentina, Canada
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University of South FloridaNational Institutes of Health (NIH)AfsluttetUrea cyklus lidelserForenede Stater