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Kliniske forsøg med X-bundet adrenoleukodystrofi
I alt 3625 resultater
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University of North Carolina, Chapel HillAfsluttetFragilt X syndrom | Psykose | AutismespektrumforstyrrelserForenede Stater
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspenderetSvær kombineret immundefektsygdom, X-bundetForenede Stater
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterAfsluttetX-Linked Dystoni ParkinsonismeFilippinerne
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Ovid Therapeutics Inc.Afsluttet
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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Great Ormond Street Hospital for Children NHS Foundation...UkendtX-bundet svær kombineret immundefektDet Forenede Kongerige
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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University Hospital, Basel, SwitzerlandNovartisAfsluttet
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Stanford UniversityAfsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuel udviklingsforstyrrelse (IDD)Forenede Stater
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National Institute of Allergy and Infectious Diseases...RekrutteringX-bundet svær kombineret immundefekt (XSCID)Forenede Stater
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Assistance Publique - Hôpitaux de ParisAfsluttetX-bundet svær kombineret immundefektFrankrig
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Children's Hospital Medical Center, CincinnatiIkke rekrutterer endnuAutismespektrumforstyrrelse | Fragilt X syndrom
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University of the Philippines Manila - Philippine...LedigX-Linked Dystoni ParkinsonismeFilippinerne
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige
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Indiana UniversityAfsluttetFragilt X syndrom | AutismespektrumforstyrrelserForenede Stater
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUkendtWiskott-Aldrich syndrom | Leukocytadhæsionsmangelsyndrom | X-forbundet agammaglobulinæmi | X-Linked Hyper IgM SyndromeForenede Stater
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RekrutteringRett syndrom | Rett syndrom, atypisk | RTTForenede Stater
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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Universitaire Ziekenhuizen KU LeuvenKU LeuvenAfsluttetMeddelelse | Forældre-barn relationer | Opførsel, barnBelgien
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Astellas Gene TherapiesAfsluttetMænd med X-bundet myotubulær myopati (XLMTM)Forenede Stater, Det Forenede Kongerige
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Minoryx Therapeutics, S.L.Aktiv, ikke rekrutterendeAdrenoleukodystrofiSpanien, Forenede Stater, Ungarn, Frankrig, Tyskland, Italien, Holland, Det Forenede Kongerige
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National Taiwan University HospitalAfsluttet
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Masonic Cancer Center, University of MinnesotaTrukket tilbage
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Nova Mentis Life Science CorpKGK Science Inc.SuspenderetKognitiv dysfunktion | Fragilt X syndrom | OpførselCanada
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RespireRxFRAXA Research FoundationAfsluttetFragilt X syndrom | AutismeForenede Stater
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... og andre samarbejdspartnereAktiv, ikke rekrutterendeAutosomal recessiv lidelse | X-forbundne genetiske sygdommeAustralien
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyAfsluttetEpilepsi | Livskvalitet | Dysbiose | Rett syndromItalien
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Newron Pharmaceuticals SPAAfsluttetRett syndromForenede Stater, Indien, Det Forenede Kongerige, Australien, Italien