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X-연관 저발한성 외배엽 이형성증에 대한 임상 시험
총 1564 건
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Great Ormond Street Hospital for Children NHS Foundation...모병
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Fondation Ophtalmologique Adolphe de RothschildInstitut National de la Santé Et de la Recherche Médicale, France종료됨
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Icahn School of Medicine at Mount Sinai모병자폐 스펙트럼 장애 | DDX3X | 정신 지체, X-연관 102미국
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The Hospital for Sick Children완전한
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Shanghai General Hospital, Shanghai Jiao Tong University...Innostellar Biotherapeutics모병
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Applied Genetic Technologies Corp완전한
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NightstaRx Ltd, a Biogen Company초대로 등록맥락막결절증 | X-연관 색소성 망막염미국, 영국, 네덜란드, 독일, 프랑스, 브라질, 캐나다, 덴마크, 핀란드
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Novartis Pharmaceuticals종료됨
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Sheba Medical CenterElMindA Ltd모병
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Tetra Discovery Partners완전한
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Viking Therapeutics, Inc.모병X-연관 부신백질이영양증(X-ALD)의 부신척수신경병증 형태(AMN)미국, 프랑스, 독일, 이탈리아, 영국
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IRCCS San RaffaeleFondazione Telethon모병
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)완전한
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California... 그리고 다른 협력자들모병
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Applied Genetic Technologies CorpFoundation Fighting Blindness완전한
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development Command완전한
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Children's Hospital Medical Center, Cincinnati모병
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Esoterix Genetic Laboratories, LLC알려지지 않은
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Specila hospital for cerebral palsy and developmental...FRAXA Research Foundation모병
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)모병
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Zynerba Pharmaceuticals, Inc.모병
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Zynerba Pharmaceuticals, Inc.초대로 등록
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis Pharmaceuticals완전한
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Zynerba Pharmaceuticals, Inc.완전한
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Children's Hospital Medical Center, CincinnatiRush University Medical Center완전한
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Novartis Pharmaceuticals완전한
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Parc de Salut Mar완전한
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Université de SherbrookeFRAXA Research Foundation완전한
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University of California, DavisThe National Fragile X Foundation완전한
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Novartis Pharmaceuticals종료됨취약 X 증후군독일, 미국, 스위스, 호주, 캐나다, 덴마크, 프랑스, 이탈리아, 영국, 스페인
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Seaside Therapeutics, Inc.완전한