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X-연관 중증 복합 면역결핍에 대한 임상 시험
총 1624 건
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Edimer Pharmaceuticals완전한X-연관 저발한성 외배엽 이형성증 | 저발한성 외배엽 이형성증미국
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Edimer Pharmaceuticals완전한X-연관 저발한성 외배엽 이형성증 | 저발한성 외배엽 이형성증스페인
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Soma JyonouchiBaylor College of Medicine완전한
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Applied Genetic Technologies Corp완전한
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Novartis Pharmaceuticals종료됨
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NightstaRx Ltd, a Biogen Company초대로 등록맥락막결절증 | X-연관 색소성 망막염미국, 영국, 네덜란드, 독일, 프랑스, 브라질, 캐나다, 덴마크, 핀란드
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Viking Therapeutics, Inc.모병X-연관 부신백질이영양증(X-ALD)의 부신척수신경병증 형태(AMN)미국, 프랑스, 독일, 이탈리아, 영국
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National Institute of Allergy and Infectious Diseases...종료됨
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Sheba Medical CenterElMindA Ltd모병
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Tetra Discovery Partners완전한
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National Human Genome Research Institute (NHGRI)National Institute of Allergy and Infectious Diseases (NIAID); National Institute of Arthritis...완전한
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National Human Genome Research Institute (NHGRI)빼는
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IRCCS San RaffaeleFondazione Telethon모병
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Applied Genetic Technologies CorpFoundation Fighting Blindness완전한
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California... 그리고 다른 협력자들모병
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)완전한
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development Command완전한
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Children's Hospital Medical Center, Cincinnati모병
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Esoterix Genetic Laboratories, LLC알려지지 않은
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University of South FloridaMerck Sharp & Dohme LLC종료됨
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SpinogenixAvance Clinical Pty Ltd.아직 모집하지 않음
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Specila hospital for cerebral palsy and developmental...FRAXA Research Foundation모병
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)모병
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Zynerba Pharmaceuticals, Inc.모병
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Zynerba Pharmaceuticals, Inc.초대로 등록
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis Pharmaceuticals완전한
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Zynerba Pharmaceuticals, Inc.완전한
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Children's Hospital Medical Center, CincinnatiRush University Medical Center완전한
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Novartis Pharmaceuticals완전한
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Parc de Salut Mar완전한
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Université de SherbrookeFRAXA Research Foundation완전한
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University of California, DavisThe National Fragile X Foundation완전한
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Novartis Pharmaceuticals종료됨취약 X 증후군독일, 미국, 스위스, 호주, 캐나다, 덴마크, 프랑스, 이탈리아, 영국, 스페인
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Seaside Therapeutics, Inc.완전한