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Clinical Trials on Mukopolysakkaridose IV in United States
Totalt 2391 resultater
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...FullførtMukopolysakkaridose VI | Mukopolysakkaridose IV AForente stater
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Nadia Ali, PhDBioMarin PharmaceuticalFullførtMorquio A syndrom | Mukopolysakkaridose IV AForente stater
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VI | Mukopolysakkaridose Type IV | Mukopolysakkaridose type VIIForente stater, Canada
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IV A | Mukopolysakkaridose IVAStorbritannia
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringMukopolysakkaridose IV Type A | Morquio A syndrom | MPS IVAForente stater
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BioMarin PharmaceuticalICON plcFullførtMukopolysakkaridose IV Type A | Morquio A syndrom | MPS IVAForente stater, Storbritannia, Australia, Taiwan, Belgia, Malaysia, Østerrike, Canada, Portugal, Frankrike, Irland, Tsjekkia, Danmark, Italia, Nederland, Polen, Puerto Rico
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IV A | Mukopolysakkaridose IVAFrankrike, Storbritannia, Taiwan, Forente stater, Argentina, Nederland, Canada, Brasil, Tyskland, Italia
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BioMarin PharmaceuticalFullførtMorquio A syndrom | MPS IVA | Mukopolysakkaridose IV AForente stater, Canada, Frankrike, Taiwan, Argentina, Colombia, Spania, Tyrkia, Japan, Saudi-Arabia, Nederland, Danmark, Korea, Republikken, Brasil, Storbritannia, Tyskland, Norge, Portugal, Italia, Qatar
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Emory UniversityBioMarin PharmaceuticalAvsluttetMukopolysakkaridose type IVAForente stater
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Emory UniversityBioMarin PharmaceuticalFullførtMPS - Mukopolysakkaridose | Morquio sykdomForente stater
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BioMarin PharmaceuticalFullførtMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVATaiwan, Forente stater, Italia, Storbritannia
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAForente stater, Storbritannia, Canada, Tyskland
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BioMarin PharmaceuticalGodkjent for markedsføringMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAForente stater, Puerto Rico
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAStorbritannia, Forente stater, Tyskland
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Nadia Ali, PhDBioMarin PharmaceuticalFullførtMukopolysakkaridose IV | Morquio sykdomForente stater
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTilbaketrukketMukopolysakkaridose IV | Morquio A DiseaseStorbritannia
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National MPS SocietyMediResource Inc.AvsluttetMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridoser | Mukopolysakkaridose VI | Mukopolysakkaridose IVForente stater
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University of California, San FranciscoRekruttering
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University of California, San FranciscoRekrutteringMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridose VI | Wolman sykdom | Pompes sykdom infantil | Mukopolysakkaridose IV A | Mukopolysakkaridose VII | Nevronopatisk Gauchers sykdomForente stater
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SanofiFullførtOsteochondrodysplasiForente stater
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Immusoft of CA, Inc.RekrutteringMukopolysakkaridose IH/S | Mukopolysakkaridose ISForente stater
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalFullført
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BioMarin PharmaceuticalFullført
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalFullførtMPS IVA | Maroteaux Lamy syndrom | MPS VI | Morquio syndrom AForente stater
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BioMarin PharmaceuticalFullførtMPS IV AForente stater, Canada, Frankrike, Storbritannia, Taiwan, Argentina, Colombia, Japan, Saudi-Arabia, Nederland, Danmark, Korea, Republikken, Brasil, Tyskland, Portugal, Italia, Qatar
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbeidspartnereFullførtMukopolysakkaridose type IIIA | Mukopolysakkaridose Type IIIBForente stater
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Masonic Cancer Center, University of MinnesotaRekrutteringMukopolysakkaridose type I | Hematopoetisk celletransplantasjonForente stater
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Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMukopolysakkaridose III-AForente stater
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Abeona Therapeutics, IncAvsluttetMukopolysakkaridose III-BForente stater, Tyskland, Frankrike
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncPåmelding etter invitasjonMukopolysakkaridose III-AForente stater, Australia, Spania
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Abeona Therapeutics, IncAvsluttetMukopolysakkaridose type 3 BForente stater, Tyskland, Frankrike, Spania
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Allievex CorporationFullførtMukopolysakkaridose Type IIIB | Mukopolysakkaridose type 3 B | MPS III B | MPS 3 BForente stater, Spania, Tyrkia, Taiwan, Australia, Colombia, Tyskland, Storbritannia
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Lundquist Institute for Biomedical Innovation at...FullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VIForente stater
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Jerome Canady, M.D.Aktiv, ikke rekrutterendeStadium IV lungekreft | Stadium IV blærekreft | Stadium IV Bukspyttkjertelkreft | Tilbakevendende ondartet fast neoplasma | Stage IV brystkreft | Stadium IV nyrecellekreft | Stage IV prostatakreft | Trinn IV tykktarmskreft | Stadium IV endetarmskreft | Stage IV Magekreft | Stadium IV Ikke-småcellet lungekreft | Stadium... og andre forholdForente stater
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Peter SzmukLuminex Corporation; Outcomes Research ConsortiumFullførtIV kanyleringForente stater
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose type IForente stater
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Alexion PharmaceuticalsFullførtMukopolysakkaridose IIIBForente stater, Storbritannia, Spania
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ivWatch, LLCFullført
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Masonic Cancer Center, University of MinnesotaAvsluttetHurler syndrom | Mukopolysakkaridose Type IH | MPS IForente stater
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HealthPartners InstituteFullførtVanskelig IV-tilgangForente stater
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Allievex CorporationFullførtMukopolysakkaridose Type IIIB | MPS III BForente stater, Taiwan, Spania, Colombia, Tyskland, Storbritannia, Tyrkia
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LYSOGENEAktiv, ikke rekrutterendeMukopolysakkaridose type IIIATyskland, Forente stater, Storbritannia, Frankrike, Nederland
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationFullført
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BioMarin PharmaceuticalFullført
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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Denali Therapeutics Inc.RekrutteringMukopolysakkaridose type IIIAForente stater
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ShireAvsluttetSanfilippo syndrom | Mukopolysakkaridose (MPS)Forente stater, Storbritannia, Spania, Tyskland, Frankrike, Italia, Nederland
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Brigham and Women's HospitalFullførtVanskelig Perifer IV-tilgangForente stater