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Kliniske forsøg med MPS - Mucopolysaccharidosis
I alt 813 resultater
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Ultragenyx Pharmaceutical IncAfsluttet
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Joyce FoxUltragenyx Pharmaceutical IncIkke længere tilgængeligMucopolysaccharidosis type 7Forenede Stater
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ShireCovance; PRA Health Sciences; PharmaNetAfsluttetMucopolysaccharidosis II | Hunters syndrom | MPS IIBrasilien, Polen, Taiwan
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National MPS SocietyMediResource Inc.AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoser | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVForenede Stater
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ArmaGen, IncAfsluttetMucopolysaccharidosis IBrasilien
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMorquio A syndrom | Mucopolysaccharidosis IV AForenede Stater
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Lundquist Institute for Biomedical Innovation at...Aktiv, ikke rekrutterendeMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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Institut National de la Santé Et de la Recherche...RekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multipel Sulfatase mangel sygdom | Mucopolysaccharidosis IXFrankrig
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis I | Hurler syndromForenede Stater
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTrukket tilbageMucopolysaccharidosis IV | Morquio A DiseaseDet Forenede Kongerige
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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Lundquist Institute for Biomedical Innovation at...Ikke rekrutterer endnuMucopolysaccharidosis III | Sanfilippo syndromForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI | Maroteaux-Lamy syndromForenede Stater, Portugal, Frankrig
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudIkke rekrutterer endnuSanfilippo syndrom type CForenede Stater, Frankrig
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological... og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Kognitiv tilbagegangForenede Stater
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JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMucopolysaccharidosis IIJapan
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JCR Pharmaceuticals Co., Ltd.AfsluttetMucopolysaccharidosis IIJapan
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurler syndrom | Hurler-Scheie syndromHolland, Frankrig, Tyskland, Det Forenede Kongerige
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University of LeipzigDeutsche Krebshilfe e.V., Bonn (Germany)RekrutteringMDS | MDS/MPNTyskland, Østrig
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IV | Morquios sygdomForenede Stater
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ShireAfsluttetSanfilippo syndrom type BForenede Stater, Det Forenede Kongerige, Tyskland
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IVA (Morquio A syndrom)Australien
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis IIForenede Stater, Spanien, Det Forenede Kongerige, Tjekkiet, Frankrig, Canada, Italien, Belgien, Holland, Tyskland, Argentina, Sverige, Kalkun, Brasilien, Colombia
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AO GENERIUMAfsluttetMetaboliske sygdomme | Mucopolysaccharidosis Type IIDen Russiske Føderation
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Lysosomale opbevaringssygdomme | RygmarvskompressionForenede Stater, Finland
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AO GENERIUMRekrutteringMetaboliske sygdomme | Mucopolysaccharidosis Type IIDen Russiske Føderation
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Denali Therapeutics Inc.Tilmelding efter invitationMucopolysaccharidosis IIForenede Stater, Canada, Belgien, Tjekkiet, Holland
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JCR Pharmaceuticals Co., Ltd.Tilmelding efter invitation
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REGENXBIO Inc.AfsluttetMucopolysaccharidosis IIBrasilien, Forenede Stater, Det Forenede Kongerige
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurler syndrom | Hurler-Scheie syndromJapan
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University of California, San FranciscoRekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolmans sygdom | Pompes sygdom infantil | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopatisk Gauchers sygdomForenede Stater
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Hurlers syndrom | Hurler-Scheie syndrom | Scheies syndromForenede Stater
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Hurler-Scheie syndrom | Hurlers syndromForenede Stater, Canada, Tyskland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Hurlers syndrom | Hurler-Scheie syndrom | ScheieItalien
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurlers syndrom | Hurler-Scheie syndromForenede Stater, Canada, Det Forenede Kongerige, Brasilien, Tyskland, Italien, Holland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurlers syndrom | Hurler-Scheie syndromBrasilien, Canada
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Assiut UniversityUkendt
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Tehran University of Medical SciencesUkendtMucopolysaccharidosisIran, Islamisk Republik
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Michael SavonaIncyte Corporation; Astex Pharmaceuticals, Inc.; TheradexRekruttering
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Manchester University NHS Foundation TrustOrchard TherapeuticsRekrutteringMucopolysaccharidoserDet Forenede Kongerige
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Hacettepe UniversityAfsluttetMucopolysaccharidoserKalkun
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Mackay Memorial HospitalBioMarin PharmaceuticalUkendt
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DKMS gemeinnützige GmbHRekrutteringAML | MDS | Perifer blodstamcelletransplantation | Graft vs værtssygdom | CMML | MDS/MPNTyskland
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Shrouk Shaban BakrRekrutteringOftalmiske manifestationerEgypten
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis VI | Mannosidose | Mucolipidose type II (I-celle sygdom)Forenede Stater
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Manchester Royal Eye HospitalBioMarin PharmaceuticalUkendtMucopolysaccharidoserDet Forenede Kongerige
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Manchester University NHS Foundation TrustAfsluttetMucopolysaccharidosis Type IIDet Forenede Kongerige
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Hasan Kalyoncu UniversityAfsluttet
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The First Affiliated Hospital with Nanjing Medical...Jiangbin Hospital Affiliated to Jiangsu University; Nanjing Second Hospital og andre samarbejdspartnereRekruttering
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetHurler syndrom | Sanfilippo syndrom type A | Sanfilippo syndrom type BForenede Stater