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Kliniske forsøg med Brydningsfejl
I alt 4717 resultater
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Boston Children's HospitalAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttetFanconi AnæmiForenede Stater
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERAfsluttet
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PfizerAfsluttetCerebral amyloid angiopatiCanada, Forenede Stater, Holland, Frankrig, Det Forenede Kongerige
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiAfsluttet
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Baylor College of MedicineAfsluttet
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Novartis PharmaceuticalsAfsluttet
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University...AfsluttetFANCONI AnæmiForenede Stater
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Walter Reed Army Medical CenterUkendtLevator Ani syndrom med smerter og/eller forstoppelse symptomer.Forenede Stater
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University of MinnesotaAfsluttet
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Alnylam PharmaceuticalsRekrutteringCerebral amyloid angiopatiCanada
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Boston Children's HospitalChildren's Hospital Medical Center, CincinnatiRekrutteringShwachman-diamant syndrom | Shwachman-Diamond Syndrome-lignendeForenede Stater
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Shenzhen Second People's HospitalIkke rekrutterer endnuCerebral amyloid angiopati
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Centre Hospitalier Universitaire de NīmesAfsluttetCerebral amyloid angiopati | Hypertensiv arteriopatiFrankrig
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Assistance Publique - Hôpitaux de ParisEuroFancolenAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttet
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Anna OlczakAfsluttetCerebral amyloid angiopatiPolen
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)AfsluttetFanconi AnæmiForenede Stater
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Shenzhen Geno-Immune Medical InstituteUkendt
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterAfsluttet
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Neena Kapoor, M.D.Trukket tilbage
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National Heart, Lung, and Blood Institute (NHLBI)Afsluttet
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital...Afsluttet
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The Hospital for Sick ChildrenAfsluttet
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)AfsluttetFanconi AnæmiForenede Stater, Brasilien
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Ukendt
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University of MinnesotaUkendt
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Rekruttering
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Leiden University Medical CenterRekruttering
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PfizerAfsluttetTransthyretin familiær amyloidose polyneuropati (TTR-FAP) | Transthyretin kardiomyopati (TTR-CM) | Familiær amyloid kardiomyopati | Senil systemisk amyloidose (SSA)
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Masonic Cancer Center, University of MinnesotaAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttet
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Alnylam PharmaceuticalsAfsluttetAmyloide neuropatier | Amyloide neuropatier, familiær | Amyloidose, arvelig | Transthyretin (TTR) medieret familiær amyloidotisk kardiomyopati (FAC) | Amyloidose, arvelig, transthyretin-relateret | Familiær transthyretin hjerteamyloidoseForenede Stater, Frankrig, Italien, Spanien, Canada, Tyskland, Belgien, Sverige, Det Forenede Kongerige
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Yungjin Pharm. Co., Ltd.AfsluttetMELAS syndrom | Mitokondrielle respiratoriske kædedefekterKorea, Republikken
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)AfsluttetFanconi AnæmiForenede Stater
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Afsluttet
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Fairview University Medical CenterAfsluttet
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Dana-Farber Cancer InstituteUkendtFanconis anæmiForenede Stater
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Ikke rekrutterer endnuCerebral amyloid angiopati
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Second Affiliated Hospital, School of Medicine,...Ikke rekrutterer endnu
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRekrutteringKardiomyopatier | Polyneuropatier | Transthyretin amyloidose | Transthyretin-relateret (ATTR) familiær amyloid kardiomyopati | Transthyretin-relateret (ATTR) familiær amyloid polyneuropatiTyskland, Østrig, Schweiz
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Hospital Universitario 12 de OctubreAktiv, ikke rekrutterende
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Khondrion BVJulius ClinicalAfsluttetMitokondrielle sygdomme | Mitokondrielle myopatier | MELAS syndrom | Mitokondrielle encefalomyopatier | MIDDHolland, Danmark, Tyskland, Det Forenede Kongerige
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Rocket Pharmaceuticals Inc.UkendtFanconi Anæmi Komplementeringsgruppe AForenede Stater
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Children's Hospital Medical Center, CincinnatiAmgenAfsluttet
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Rocket Pharmaceuticals Inc.Tilmelding efter invitationFanconi Anæmi | Fanconi Anæmi Komplementeringsgruppe ASpanien
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Stanford UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetMELAS syndromForenede Stater
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The University of Texas Health Science Center,...Afsluttet
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Universidade do PortoCentro Hospitalar Universitário São João, E.P.E. (CHUSJ); Centro de Investigação... og andre samarbejdspartnereRekrutteringKarpaltunnelsyndrom | Transthyretin amyloidosePortugal