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Kliniske forsøg med X-Linked Hypophosphatemic Rickets
I alt 1560 resultater
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ShireAfsluttetHunters syndromDet Forenede Kongerige, Forenede Stater, Brasilien
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis Type II (MPS II)Forenede Stater, Canada
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRekrutteringPyruvat dehydrogenase kompleks mangelForenede Stater
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAktiv, ikke rekrutterendePyruvat dehydrogenase kompleks mangelForenede Stater
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Fondazione TelethonAfsluttetPyruvat dehydrogenase kompleks mangelItalien
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston Children's Hospital og andre samarbejdspartnereAfsluttetPrader-Willi syndrom | Rett syndrom | Angelman syndrom | SøvnproblemerForenede Stater
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Eunice Kennedy Shriver National Institute of Child...Afsluttet
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Emalex Biosciences Inc.Psyadon PharmaAfsluttetLesch-Nyhans sygdom | Selvskadende adfærdSpanien, Forenede Stater
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ShireCovance; PRA Health Sciences; PharmaNetAfsluttetMucopolysaccharidosis II | Hunters syndrom | MPS IIBrasilien, Polen, Taiwan
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University of California, San DiegoBioMarin PharmaceuticalTrukket tilbageAdfærdsmanifestationer af Lesch-Nyhans sygdomForenede Stater
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The Chaim Sheba Medical CenterRekrutteringFragilt X syndrom | Williams syndrom | Velokardiofacialt syndromIsrael
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TakedaRekrutteringHunters syndromCanada, Frankrig
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CENTOGENE GmbH RostockAfsluttetMucopolysaccharidosis II | Hunters syndrom | Jægers syndrom, mild form | Hunter's Canal SyndromeMexico
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Oslo University HospitalAktiv, ikke rekrutterende
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National Institute of Neurological Disorders and...AfsluttetMotor neuron sygdom | Spinal og bulbar muskelatrofi (SBMA)Forenede Stater
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National MPS SocietyMediResource Inc.AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoser | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVForenede Stater
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Minoryx Therapeutics, S.L.Aktiv, ikke rekrutterendeAdrenoleukodystrofiSpanien, Forenede Stater, Ungarn, Frankrig, Tyskland, Italien, Holland, Det Forenede Kongerige
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National Taiwan University HospitalAfsluttet
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Masonic Cancer Center, University of MinnesotaTrukket tilbage
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Manchester University NHS Foundation TrustAfsluttetMucopolysaccharidosis Type IIDet Forenede Kongerige
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Kunming Hope of Health HospitalAfsluttet
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIForenede Stater
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Cyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetMenkes sygdom | Occipital Horn Syndrom | Uforklarlig kobbermangelForenede Stater
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MedDay Pharmaceuticals SAAfsluttetAdrenoleukodystrofi | Adrenomyeloneuropati | AMNFrankrig, Tyskland, Spanien
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)AfsluttetAdrenoleukodystrofi | AdrenomyeloneuropatiForenede Stater
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RekrutteringPyruvat Dehydrogenase Complex Deficiency DiseaseForenede Stater
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Assistance Publique - Hôpitaux de ParisCentre National de la Recherche Scientifique, FranceAfsluttetAmyotrofisk lateral sklerose | Primær lateral sklerose | Kennedys sygdomFrankrig
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University Hospital HeidelbergAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mestringsadfærd | Mucopolysaccharidosis Type III | AdfærdsforstyrrelserTyskland
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Afsluttet
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUkendtAdrenoleukodystrofiTaiwan
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National Center for Research Resources (NCRR)Ohio State UniversityAfsluttetAmyotrofisk lateral sklerose | Spinal muskelatrofi | Spinobulbar muskelatrofi
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ShireAfsluttetHunters syndrom | Mucopolysaccharidosis II (MPS II)Forenede Stater, Frankrig, Det Forenede Kongerige, Tyskland, Sverige, Spanien, Brasilien, Canada, Italien, Rumænien
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Hugo W. Moser Research Institute at Kennedy Krieger...AfsluttetAdrenoleukodystrofiForenede Stater
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Institute for Neurodegenerative DisordersAfsluttetParkinsons sygdom | Alzheimers sygdom | Mild kognitiv svækkelse | Fragilt X syndrom | Huntingtons sygdom | Autistiske Spektrum ForstyrrelserForenede Stater
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Masonic Cancer Center, University of MinnesotaRekruttering
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Minoryx Therapeutics, S.L.RekrutteringCerebral adrenoleukodystrofi (cALD)Forenede Stater, Brasilien, Argentina
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Poxel SAIkke rekrutterer endnu
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD)Forenede Stater, Frankrig, Tyskland, Italien, Holland, Det Forenede Kongerige
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD)Forenede Stater, Tyskland, Argentina, Australien, Frankrig, Det Forenede Kongerige
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ShireAfsluttetHunters syndromSpanien, Forenede Stater, Canada, Det Forenede Kongerige, Frankrig, Australien, Mexico
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Masonic Cancer Center, University of MinnesotaTrukket tilbageCerebral adrenoleukodystrofi
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRekrutteringCerebral adrenoleukodystrofi (CALD)Forenede Stater
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Poxel SAIkke rekrutterer endnu
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Masonic Cancer Center, University of MinnesotaRekrutteringCerebral adrenoleukodystrofi | Adrenoleukodystrofi | ALD (adrenoleukodystrofi)Forenede Stater
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige, Canada
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Onofre, Aurora Pujol, M.D.Afsluttet
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaAfsluttet
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West China HospitalRekruttering