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Søg i kliniske forsøg efter: Natural History Study
I alt 121983 resultater
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Johns Hopkins UniversityRekrutteringRetinitis PigmentosaForenede Stater
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... og andre samarbejdspartnereRekruttering
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Sarepta Therapeutics, Inc.RekrutteringLem-bælte muskeldystrofiForenede Stater, Brasilien, Belgien, Canada, Tyskland, Italien, Spanien, Sverige, Kalkun, Det Forenede Kongerige
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University of Milano BicoccaRekruttering
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National Institute of Allergy and Infectious Diseases...Rekruttering
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National Institute of Allergy and Infectious Diseases...Rekruttering
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab...RekrutteringHæmofili | Trombose | Trombofili | Seglcellesygdom | Thalassæmi | Blødningsforstyrrelse | Von Willebrands Sygdomme | Faktor IX mangel | Bindevævsforstyrrelse | Faktor VIII mangel | Hæmatologisk lidelse | Sjælden blødningsforstyrrelse | BlodpladesygdomForenede Stater
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National Institute of Neurological Disorders and...RekrutteringAmyotrofisk lateral sklerose type 4 | Arvelige neurologiske lidelser ved RNA-behandlingForenede Stater
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National Institute on Alcohol Abuse and Alcoholism...RekrutteringAlkohol drikke | Alkohol-relaterede lidelser | Pandemi | Psykologisk stressForenede Stater
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases...RekrutteringSpastisk ataksiCanada, Frankrig, Tyskland, Italien, Holland, Kalkun, Det Forenede Kongerige
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Luca SangiorgiRekruttering
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Luca SangiorgiRekruttering
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Aspa TherapeuticsRekrutteringCanavans sygdomForenede Stater, Tyskland
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Luca SangiorgiRekruttering
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National Human Genome Research Institute (NHGRI)National Cancer Institute (NCI)Rekruttering
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University of PennsylvaniaPassage Bio, Inc.RekrutteringGM1 GangliosidosisForenede Stater, Kalkun, Brasilien, Canada, Det Forenede Kongerige
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National Heart, Lung, and Blood Institute (NHLBI)RekrutteringKardiovaskulær (CV) risikoForenede Stater
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Wan-Jin ChenChang Gung Memorial Hospital; Taipei Veterans General Hospital, TaiwanRekruttering
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First Affiliated Hospital of Fujian Medical UniversityRekrutteringAmyotrofisk lateral skleroseKina
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Disarm TherapeuticsEli Lilly and CompanyRekrutteringKemoterapi-induceret perifer neuropatiForenede Stater
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National Institute of Environmental Health Sciences...RekrutteringTeenagers sundhed | Pædiatri | Ungdomsudvikling | Reproduktive fysiologiske processerForenede Stater
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National Institute of Diabetes and Digestive and...Rekruttering
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Institute of Child HealthUniversity College, London; Great Ormond Street Hospital for Children NHS...RekrutteringAlternerende Hemiplegia of Childhood | ATP1A3-relateret sygdom | Hurtigt indsættende dystoni Parkinsonisme | CAPOSDet Forenede Kongerige
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Neurogene Inc.RekrutteringCeroid Lipofuscinose, Neuronal 5Forenede Stater
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Joshua Mann, MPHNational Organization for Rare DisordersRekrutteringVon Hippel-Lindau sygdom | Arvelig leiomyomatose og nyrecellekræft | Birt-Hogg-Dube syndrom | SDHB-genmutationForenede Stater
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Dai HuapingRekruttering
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Hugo W. Moser Research Institute at Kennedy Krieger...RekrutteringLeukoencefalopati | Genetisk sygdom | Hvidstof sygdom | Ataksi, cerebellar | LBSL | Leukoencefalopati med hjernestamme og rygmarvsinvolvering og laktatforhøjelseForenede Stater
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University of Alabama at BirminghamNational Cancer Institute (NCI)RekrutteringEndometriecancer | Forstadier til endometriecancerForenede Stater
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Columbia UniversityNew York University; Universitätsklinikum Hamburg-Eppendorf; Hackensack Meridian... og andre samarbejdspartnereRekrutteringIntellektuel handicap | Anfald | Neuroudviklingsforstyrrelser | Autismespektrumforstyrrelse | Udviklingsforsinkelse | Hypotoni | Hypertoni, muskelForenede Stater
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Nationwide Children's HospitalMyonexus TherapeuticsRekrutteringLimb-Girdle Muskeldystrofi, Type 2EForenede Stater
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National Institute of Diabetes and Digestive and...RekrutteringFedme | Diabetes mellitus | Fed leverForenede Stater
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National Institute of Neurological Disorders and...RekrutteringEpilepsi | Anfald | Epilepsi, temporallap | Delvis epilepsiForenede Stater
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Yassin Abdelghaffar Charity Center for Liver Disease...Society of Friends of Liver Patients in the Arab World (SLPAW)RekrutteringArvelig tyrosinæmi, type IEgypten
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University of Colorado, DenverRekrutteringKlinefelters syndrom | Trisomi X | XYY syndrom | XXXY og XXXXY syndrom | Xxyy syndrom | Xyyy syndrom | Xxxx syndrom | Xxxxx syndrom | Xxxyy syndrom | Xxyyy syndrom | Xyyyy syndrom | Mand med sexkromosommosaicismeForenede Stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringBattens sygdom | Juvenil Neuronal Ceroid Lipofuscinose (CLN3)Forenede Stater
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Centre Hospitalier Universitaire, AmiensRekruttering
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University of MichiganRekrutteringLipodystrofi (genetisk eller erhvervet, ikke-hiv)Forenede Stater, Kalkun
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RekrutteringPyruvat Dehydrogenase Complex Deficiency DiseaseForenede Stater
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National Cancer Institute (NCI)RekrutteringNeoplasmer i maven | Mavekræft | Gastrisk adenokarcinom og proksimal polypose i maven (GAPPS) | Arvelig diffus mavekræft (HDGC) | Familiær diffus mavekræftForenede Stater
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Travere Therapeutics, Inc.RekrutteringHomocystinuri på grund af CBS-mangelIrland, Qatar, Forenede Stater, Det Forenede Kongerige
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National Institute of Allergy and Infectious Diseases...RekrutteringDIRA | NLRC4-MAS | NOMID | SAVI | LYSForenede Stater
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Target PharmaSolutions, Inc.RekrutteringHepatocellulær kræftForenede Stater, Tyskland, Frankrig, Italien, Spanien
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University of Texas Southwestern Medical CenterThe Hersh FoundationRekrutteringDepression | Depression, BipolarForenede Stater
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Ataxia Study GroupGerman Center for Neurodegenerative Diseases (DZNE)RekrutteringSen indsættende sporadisk cerebellar ataksiNorge, Østrig, Tyskland, Holland, Italien
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Duke UniversityRekrutteringVoksen polyglucosan kropssygdom | Glykogenopbevaring Sygdom Type IV | GSD4 | GSD IV | APBDForenede Stater
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National Institute of Neurological Disorders and...RekrutteringNormal fysiologiForenede Stater
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National Institute of Environmental Health Sciences...RekrutteringFedme | Normal fysiologi | PubertetForenede Stater
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereRekrutteringAutisme | ASD | Makrocefali | PTEN | PTEN Hamartoma Tumor SyndromForenede Stater