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Clinical Trials on 균질산 in Colombia
총 81 건
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare Diseases (ORD) 그리고 다른 협력자들초대로 등록
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune Deficiency...초대로 등록
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University of British ColumbiaCanadian Institutes of Health Research (CIHR)완전한
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International Food Policy Research InstituteFHI 360; AFRICSanté완전한
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International Food Policy Research InstituteFHI 360; Addis Continental Institute of Public Health완전한
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University of British Columbia알려지지 않은
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University of British ColumbiaGlaxoSmithKline; CIHR Canadian HIV Trials Network완전한
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National Human Genome Research Institute (NHGRI)모병
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University of British Columbia완전한
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University of California... 그리고 다른 협력자들종료됨
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.모병
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Ultragenyx Pharmaceutical Inc완전한
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Assistance Publique - Hôpitaux de Paris모병
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CENTOGENE GmbH Rostock빼는콜레스테롤 에스테르 축적병 | 산성 리파아제 결핍 | 산성 콜레스테롤 에스테르 가수분해효소 결핍증, 월만형독일, 인도, 스리랑카
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HemoShear Therapeutics종료됨
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau, Ottawa완전한
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University of Missouri-ColumbiaBioMarin Pharmaceutical완전한
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University of British ColumbiaVitaflo International, Ltd알려지지 않은
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada완전한
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University of Missouri-ColumbiaBioMarin Pharmaceutical초대로 등록
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Children's National Research InstituteGeorgetown University빼는
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Children's National Research InstituteBoston Children's Hospital모병
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)모병저산소-허혈성 뇌병증 | 우레아 순환 장애 | 유기산혈증 | 지방산 산화 장애 | 메이플 시럽 소변 질환 | 글루타르산혈증 I미국
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Children's National Research InstitutePatient-Centered Outcomes Research Institute; Eunice Kennedy Shriver National Institute... 그리고 다른 협력자들완전한
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National Institute of Neurological Disorders and...완전한
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National Institute of Neurological Disorders and...완전한
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science University 그리고 다른 협력자들종료됨
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research Network; Office...완전한
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Ultragenyx Pharmaceutical Inc완전한장쇄 지방산 산화 장애(LC-FAOD) | 초장쇄 아실-CoA 탈수소효소(VLCAD) 결핍증 | 삼중기능 단백질(TFP) 결핍 | 카르니틴 팔미토일전이효소(CPT II) 결핍 | 장쇄 3-하이드록시-아실-CoA 탈수소효소(LCHAD) 결핍증미국, 영국
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Sangart완전한쇼크, 출혈 | 산증, 젖산 | 충격, 외상성노르웨이, 싱가포르, 이스라엘, 프랑스, 영국, 독일, 스위스, 호주, 브라질, 남아프리카, 뉴질랜드, 콜롬비아, 오스트리아, 스페인
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn School... 그리고 다른 협력자들완전한메틸말론산혈증 | Carbamoyl-Phosphate Synthase I 결핍증 | 프로피온산혈증, 유형 I 및/또는 유형 II | 오르니틴 카르바모일전이효소 결핍증미국
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CENTOGENE GmbH Rostock빼는대사 장애 | 티로시노증 | 간신장티로신혈증 | Fumarylacetoacetase 결핍증 | Fah 결핍독일, 스리랑카, 인도
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research Institute완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Baylor College of MedicineChildren's National Research Institute모병오르니틴 트랜스카르바밀라아제 결핍증 | 우레아 순환 장애 | 카르바밀 인산염 합성효소 결핍증 | 아르기니노숙신산뇨증 | 고아르기닌혈증 | 시트룰린혈증 1 | ARGI 결핍 | ASL 결핍 | ASS 결핍 | NAGS 결핍미국
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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BioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한