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- 미국 임상 시험 레지스트리
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선천성 아미노산 대사 장애에 대한 임상 시험
총 44117 건
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University of Southern CaliforniaNational PKU Alliance모집하지 않고 적극적으로
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Boston Children's HospitalBioMarin Pharmaceutical완전한
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University of Missouri-ColumbiaBioMarin Pharmaceutical초대로 등록
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APR Applied Pharma Research s.a.종료됨
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University Hospitals Cleveland Medical CenterBioMarin Pharmaceutical완전한
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The University of Texas Medical Branch, Galveston종료됨
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Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do Porto완전한
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University of British ColumbiaVitaflo International, Ltd알려지지 않은
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BioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한
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University of Wisconsin, MadisonBoston Children's Hospital완전한
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science Institute완전한
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Children's National Research InstituteGeorgetown University빼는
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Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono Norway완전한
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The Kennedy Institute-National Eye ClinicSygekassernes Helsefond완전한
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)빼는우레아 순환 장애, 선천적 | 대사의 선천적 오류 | 프로피온산혈증 | 메틸말론산혈증 | 카르바밀 인산염 합성효소 결핍증
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Dr. Schär AG / SPA완전한
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University of Novi Sad, Faculty of Sport and Physical...완전한
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Baylor College of Medicine완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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National Center for Research Resources (NCRR)Baylor College of Medicine알려지지 않은
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University Hospital, Clermont-Ferrand알려지지 않은
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Aeglea Biotherapeutics완전한
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University of TorontoIovate Health Sciences International Inc완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare Diseases Clinical Research Network종료됨
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S.LAB (SOLOWAYS)Center of New Medical Technologies모병
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Peking UniversityNational Natural Science Foundation of China; Institute of reproductive and Child Health완전한
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The Hospital for Sick ChildrenBioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical모병
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PTC Therapeutics완전한
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Homology Medicines, Inc종료됨