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대사, 선천적 오류에 대한 임상 시험
총 66537 건
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Icahn School of Medicine at Mount SinaiMayo Clinic; Baylor College of Medicine; Children's Hospital of Philadelphia; University of... 그리고 다른 협력자들모병
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical종료됨
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Rigshospitalet, DenmarkUniversity College, London완전한
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IRCCS Eugenio MedeaUniversity of Pisa; University of Messina완전한
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Children's National Research InstituteBoston Children's Hospital모병
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Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbH완전한
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Ultragenyx Pharmaceutical Inc종료됨
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APR Applied Pharma Research s.a.모병
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PTC Therapeutics모병페닐케톤뇨증미국, 독일, 스페인, 호주, 브라질, 영국, 덴마크, 멕시코, 포르투갈, 칠면조, 캐나다, 그루지야, 이탈리아, 네덜란드, 일본
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Ajinomoto Co., Inc.Great Ormond Street Hospital for Children NHS Foundation Trust; Birmingham Children's Hospital모집하지 않고 적극적으로
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PTC Therapeutics완전한페닐케톤뇨증스페인, 미국, 호주, 독일, 영국, 브라질, 덴마크, 캐나다, 프랑스, 그루지야, 이탈리아, 멕시코, 네덜란드, 포르투갈, 칠면조
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Birmingham Women's and Children's NHS Foundation...모집하지 않고 적극적으로
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BioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau, Ottawa완전한
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BioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin Pharmaceutical완전한
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Emory UniversityNational PKU Alliance완전한
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Children's Hospital of Philadelphia완전한
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Children's University Hospital, IrelandUniversity College Dublin; Health Research Board, Ireland; Medical Research Charities Group...완전한
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Chiesi Farmaceutici S.p.A.아직 모집하지 않음