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Clinical Trials on 피루브산 대사, 선천적 오류 in United States
총 2366 건
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California...모병
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Alexion Pharmaceuticals, Inc.Xcenda, LLC모집하지 않고 적극적으로
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Mendel TuchmanEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)알려지지 않은
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.모집하지 않고 적극적으로
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.모병
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Poudre Valley Health System초대로 등록
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University of PennsylvaniaNorthwestern University; Family Heart Foundation초대로 등록
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Northwestern UniversityUniversity of Pennsylvania; Family Heart Foundation초대로 등록
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Emory UniversityKaneka Medical America LLC완전한
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc모병
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Geisinger ClinicNational Heart, Lung, and Blood Institute (NHLBI)초대로 등록
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)모병
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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Northwestern UniversityUniversity of Pennsylvania; Family Heart Foundation완전한
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PTC Therapeutics완전한미토콘드리아 질병 | 약물 내성 간질 | 레이병 | 레이 증후군 | 미토콘드리아 뇌병증(MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | 알퍼스병 | 알퍼스 증후군미국, 스페인, 영국, 캐나다, 프랑스, 이탈리아, 폴란드, 스웨덴, 일본
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University of Texas Southwestern Medical Center완전한
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Alexion Pharmaceuticals완전한
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)정지된
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Alexion Pharmaceuticals마케팅 승인
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The Familial Hypercholesterolemia Foundation모병
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University of PennsylvaniaLancaster General Hospital; The Familial Hypercholesterolemia Foundation완전한
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Origin Biosciences완전한몰리브덴 보조인자 결핍미국, 호주, 영국, 독일, 네덜란드, 칠면조
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Alexion Pharmaceuticals완전한
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University of Wisconsin, MadisonJohns Hopkins University; National Institute of Diabetes and Digestive and Kidney Diseases... 그리고 다른 협력자들초대로 등록
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Boston Children's HospitalWellth Inc.; MMAS-8 with permission from Dr Donald Morisky. as written below모병
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National Center for Research Resources (NCRR)Oregon Health and Science University알려지지 않은
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Alexion Pharmaceuticals완전한
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University of PennsylvaniaRegeneron Pharmaceuticals완전한
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University of Wisconsin, MadisonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Stanford University완전한
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Dr. Schär AG / SPA완전한
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Vanderbilt University Medical CenterHarvard University모병
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals, Inc.완전한