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X-연관 근세관 근병증에 대한 임상 시험
총 1542 건
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Sheba Medical CenterElMindA Ltd모병
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Tetra Discovery Partners완전한
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IRCCS San RaffaeleFondazione Telethon모병
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Applied Genetic Technologies CorpFoundation Fighting Blindness완전한
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)완전한
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development Command완전한
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California... 그리고 다른 협력자들모병
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Children's Hospital Medical Center, Cincinnati모병
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Esoterix Genetic Laboratories, LLC알려지지 않은
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Massachusetts General HospitalNational Institutes of Health (NIH)알려지지 않은
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SpinogenixAvance Clinical Pty Ltd.아직 모집하지 않음
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Specila hospital for cerebral palsy and developmental...FRAXA Research Foundation모병
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)모병
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Zynerba Pharmaceuticals, Inc.모병
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Zynerba Pharmaceuticals, Inc.초대로 등록
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis Pharmaceuticals완전한
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Zynerba Pharmaceuticals, Inc.완전한
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Children's Hospital Medical Center, CincinnatiRush University Medical Center완전한
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Novartis Pharmaceuticals완전한
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Parc de Salut Mar완전한
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Université de SherbrookeFRAXA Research Foundation완전한
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University of California, DavisThe National Fragile X Foundation완전한
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Novartis Pharmaceuticals종료됨취약 X 증후군독일, 미국, 스위스, 호주, 캐나다, 덴마크, 프랑스, 이탈리아, 영국, 스페인
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Seaside Therapeutics, Inc.완전한
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Craig EricksonHealx Limited모병
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Elizabeth Berry-Kravis완전한
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Novartis Pharmaceuticals완전한
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research Foundation알려지지 않은
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Hoffmann-La Roche완전한
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study site완전한베커 근이영양증 | 지대근이영양증, 유형 2A(칼페인-3 결핍) | 지대근이영양증, 유형 2B(미요시 근병증, 디스페린 결핍증) | 지대근이영양증, 유형 2I(FKRP 결핍)미국