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Kliniske studier på X-chromosomale schwere kombinierte Immunschwäche
Totalt 133 resultater
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Great Ormond Street Hospital for Children NHS Foundation...UkjentX-bundet alvorlig kombinert immunsviktStorbritannia
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendertAlvorlig kombinert immunsviktsykdom, X-bundetForente stater
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National Institute of Allergy and Infectious Diseases...RekrutteringX-bundet alvorlig kombinert immunsvikt (XSCID)Forente stater
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Assistance Publique - Hôpitaux de ParisFullførtX-bundet alvorlig kombinert immunsviktFrankrike
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University of MiamiJackson Health SystemIkke lenger tilgjengelig
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National Institute of Allergy and Infectious Diseases...AvsluttetVekstsvikt | X-bundet alvorlig kombinert immunsvikt (XSCID) | Resistens mot veksthormonForente stater
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Children's Hospital of Chongqing Medical UniversityRekruttering
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Great Ormond Street Hospital for Children NHS Foundation...RekrutteringAlvorlig kombinert immunsvikt, X-kobletStorbritannia
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David WilliamsAktiv, ikke rekrutterendeGenterapi | Alvorlig kombinert immunsvikt, X-kobletForente stater, Storbritannia
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National Institute of Allergy and Infectious Diseases...UkjentX-koblede kombinerte immunsviktsykdommerForente stater
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National Institute of Allergy and Infectious Diseases...FullførtAlvorlig kombinert immunsviktForente stater
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Novartis PharmaceuticalsAvsluttet
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Sheba Medical CenterElMindA LtdRekrutteringFragilt X Associated Tremor-ataxia Syndrome | FXTASIsrael
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Ovid Therapeutics Inc.FullførtFragilt X-syndrom (FXS)Forente stater
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Guido A. Davidzon, MD, SMTilbaketrukket
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Tetra Discovery PartnersFullførtFragilt X-syndrom | Fra(X) syndrom | FXSForente stater
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...FullførtFragilt X-syndromForente stater
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Seaside Therapeutics, Inc.Fullført
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)FullførtFragilt X-syndromForente stater
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Fullført
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...Fullført
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRekrutteringNevroatferdsmanifestasjoner | Genetiske sykdommer, X-linked | Intellektuell funksjonshemming | Fragilt X-syndrom | Kjønnskromosomforstyrrelser | Fragilt X Mental Retardation Syndrome | Trinukleotid gjentatt utvidelse | Fra(X) syndrom | FXS | Mental retardasjon, X LinkedForente stater, Canada
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X-syndromForente stater
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Esoterix Genetic Laboratories, LLCUkjentFragilt X-syndromForente stater
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...FullførtAlvorlig kombinert immunsvikt | Adenosindeaminase-mangel | Forstyrrelse i immunsystemet | Autosomal recessiv lidelse | Purin-nukleosid-fosforylase-mangel | Alvorlig kombinert immunsvikt med fravær av T- og B-celler | X-koblet alvorlig kombinert immunsviktForente stater
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Craig EricksonHealx LimitedRekrutteringFragilt X-syndromForente stater
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Elizabeth Berry-KravisFullførtFragilt X-syndromForente stater
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Novartis PharmaceuticalsFullførtFragilt X-syndromForente stater, Spania
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUkjent
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Hoffmann-La RocheFullførtFragilt X-syndromForente stater
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Hoffmann-La RocheFullførtFragilt X-syndromFrankrike, Spania, Forente stater, Peru, Canada, Storbritannia, Chile, Argentina, Mexico, Sverige
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Yolanda de Diego OteroFullført
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Seaside Therapeutics, Inc.FullførtFragilt X-syndromForente stater
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Seaside Therapeutics, Inc.AvsluttetFragilt X-syndromForente stater
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Washington University School of MedicineRekrutteringAlvorlig kombinert immunsvikt | Kronisk granulomatøs sykdom | DiGeorge syndrom | Hemofagocytisk lymfohistiocytose | Wiskott-Aldrich syndrom | X-koblet lymfoproliferativt syndrom | X-bundet agammaglobulinemi | Chediak-Higashi syndrom | IPEX | Autoimmunt lymfoproliferativt syndrom | Vanlig variabel immunsvikt | Im... og andre forholdForente stater
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Massachusetts General HospitalNational Institutes of Health (NIH)UkjentSunn | Fragilt X-syndromForente stater
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IRCCS Fondazione Stella MarisRekrutteringFragilt X-syndromItalia
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRekrutteringFragilt X-syndromSerbia
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringFragilt X-syndromForente stater
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Tetra Discovery PartnersRekrutteringFragilt X-syndromForente stater
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Zynerba Pharmaceuticals, Inc.RekrutteringFragilt X-syndromForente stater, Australia, Storbritannia, Irland
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National Institute of Mental Health (NIMH)FullførtFriske Frivillige | Fragilt X-syndromForente stater
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Zynerba Pharmaceuticals, Inc.Påmelding etter invitasjonFragilt X-syndromForente stater, Storbritannia, New Zealand, Australia
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis...Fullført
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Zynerba Pharmaceuticals, Inc.FullførtFragilt X-syndromForente stater, New Zealand, Australia
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterFullført
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Novartis PharmaceuticalsFullførtFragilt X-syndromForente stater, Sveits, Tyskland, Australia, Canada, Danmark, Frankrike, Italia, Spania, Storbritannia
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Stanford UniversityFullførtFragilt X-syndromForente stater
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University of California, DavisFullførtFragilt X-syndrom | Genetiske sykdommerForente stater
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Parc de Salut MarFullført