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Kliniske forsøg med Aniridia-intellektuelt handicapsyndrom
I alt 1062 resultater
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Garvan Institute of Medical ResearchAfsluttetPrader-Willi syndromAustralien
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University of FloridaPrader-Willi Syndrome AssociationAfsluttet
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GeneScience Pharmaceuticals Co., Ltd.Peking University First Hospital; Peking Union Medical College Hospital; Children... og andre samarbejdspartnereUkendt
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Essentialis, Inc.AfsluttetPrader-Willi syndromForenede Stater
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Children's Mercy Hospital Kansas CityAfsluttetPrader-Willi syndrom
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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Brigham and Women's HospitalFoundation for Prader-Willi ResearchRekruttering
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Aardvark Therapeutics, Inc.Children's Hospital Colorado; Stanford UniversityRekrutteringPrader-Willi syndromForenede Stater
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UMC UtrechtSanquin Research & Blood Bank Divisions; National Institute for Public... og andre samarbejdspartnereRekrutteringDowns syndrom | SARS-CoV-2-vaccinationHolland
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University Hospital, ToulouseRekruttering
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); National Institutes...AfsluttetBradykardi | Downs syndromForenede Stater
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Soleno Therapeutics, Inc.AfsluttetPrader-Willi syndromForenede Stater, Det Forenede Kongerige
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SanionaTrukket tilbagePrader-Willi syndromForenede Stater
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Corporacion Parc TauliAfsluttetPrader-Willi syndromSpanien
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Soleno Therapeutics, Inc.Trukket tilbagePrader-Willi syndrom
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University Hospital, ToulouseAfsluttetPrader-Willi syndromFrankrig
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University Hospital, ToulouseEuropean Society for Paediatric EndocrinologyAfsluttetPrader-Willi syndromSverige, Belgien, Frankrig, Tyskland, Holland, Det Forenede Kongerige
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University Hospital, ToulouseAfsluttetPrader-Willi syndromFrankrig
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GLWL Research Inc.AfsluttetPrader-Willi syndromForenede Stater, Canada
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LG Life SciencesAfsluttetPrader-Willi syndromKorea, Republikken
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Zafgen, Inc.AfsluttetFedme | Prader-Willi syndromForenede Stater
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Karolinska University HospitalNovo Nordisk A/SAfsluttetPrader-Willi syndromDanmark, Norge, Sverige
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Samsung Medical CenterAfsluttetFedme | Prader-Willi syndrom
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CHU de ReimsUkendt
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Northwestern UniversityArchieMDAfsluttetGraviditet | Downs syndromForenede Stater
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Sequenom, Inc.PRA Health SciencesAfsluttetGraviditet | Downs syndrom | Aneuploidi | Edwards syndromForenede Stater, Frankrig
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Université de Reims Champagne-ArdenneIkke rekrutterer endnu
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Christopher Hartnick, M.D.University of Pittsburgh; Emory University; Children's Hospital Medical Center... og andre samarbejdspartnereAfsluttetSøvnapnø, obstruktiv | Downs syndromForenede Stater
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom, bevaret talevariant | Mecp2 duplikationssyndrom | Rett-relaterede lidelserForenede Stater
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Parc de Salut MarAfsluttet
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University... og andre samarbejdspartnereRekrutteringSygdomme i nervesystemet | Neurologiske manifestationer | Neuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Neuroudviklingsforstyrrelser | Neurologisk lidelse | Rett syndrom | Genetisk sygdom | Rett syndrom, atypiskForenede Stater
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SanionaAfsluttetBekræftet genetisk diagnose af Prader-Willi syndromTjekkiet, Ungarn
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH); PWSAUSAAfsluttetPrader-willi syndromForenede Stater
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University of FloridaFoundation for Prader-Willi ResearchAfsluttet
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Ovid Therapeutics Inc.AfsluttetFragilt X-syndrom (FXS)Forenede Stater
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University of Wisconsin, MadisonUltragenyx Pharmaceutical IncAfsluttetPrader-Willi syndrom | Angelman syndromForenede Stater
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Guido A. Davidzon, MD, SMTrukket tilbage
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Tetra Discovery PartnersAfsluttetFragilt X syndrom | Fra(X) syndrom | FXSForenede Stater
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LuMind IDSC FoundationAlzheimer's Disease Cooperative Study (ADCS)Aktiv, ikke rekrutterendeAlzheimers sygdom i Downs syndromForenede Stater
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Life Molecular Imaging SAAfsluttetDowns syndrom | Amyloid Beta-proteinForenede Stater
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University Hospital, ToulouseIkke rekrutterer endnu
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Erasmus Medical CenterFoundation for Prader-Willi Research; Prader-Willi FondsIkke rekrutterer endnu
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The Hospital for Sick ChildrenUniversity of Western Ontario, Canada; Holland Bloorview Kids Rehabilitation...Rekruttering
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The Hospital for Sick ChildrenFoundation for Prader-Willi ResearchIkke rekrutterer endnu
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi ResearchAktiv, ikke rekrutterendePrader-Willi syndromForenede Stater
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Harmony Biosciences, LLCAktiv, ikke rekrutterende
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ConSynance TherapeuticsAfsluttetPrader-Willi syndromForenede Stater
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Radius Pharmaceuticals, Inc.AfsluttetPrader-Willi syndromForenede Stater
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Rhythm Pharmaceuticals, Inc.AfsluttetPrader-Willi syndromForenede Stater
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Radius Pharmaceuticals, Inc.Benuvia Therapeutics Inc.Afsluttet