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Kliniske forsøg med Bulbo-Spinal Atrofi, X-Linked
I alt 1842 resultater
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRekruttering
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TakedaRekruttering
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Novartis PharmaceuticalsAfsluttetSpinal og Bulbar muskelatrofiForenede Stater, Tyskland, Italien, Danmark
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Rigshospitalet, DenmarkAfsluttet
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National Institute of Neurological Disorders and...AfsluttetSpinal og Bulbar muskelatrofi | Kennedys sygdomForenede Stater
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AnnJi Pharmaceutical Co., Ltd.Aktiv, ikke rekrutterendeSpinal og Bulbar muskelatrofi | Kennedys sygdomForenede Stater
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Karen Brorup Heje PedersenAfsluttetSunde emner | Spinal og Bulbar muskelatrofiDanmark
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Ramathibodi HospitalAstraZenecaAfsluttetSpinobulbar muskelatrofi | Kennedys sygdomThailand
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National Institute of Neurological Disorders and...AfsluttetMotor neuron sygdom | Spinal og bulbar muskelatrofi (SBMA)Forenede Stater
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National Institute of Neurological Disorders and...RekrutteringMotor neuron sygdom | Spinal og Bulbar muskelatrofi | Kennedys sygdomForenede Stater
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National Institute of Neurological Disorders and...AfsluttetMotor neuron sygdomForenede Stater
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RekrutteringAmyotrofisk lateral sklerose | Kennedys sygdomFrankrig
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National Center for Research Resources (NCRR)Ohio State UniversityAfsluttetAmyotrofisk lateral sklerose | Spinal muskelatrofi | Spinobulbar muskelatrofi
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... og andre samarbejdspartnereRekrutteringALS | Kennedys sygdom | MND (motorisk neuronsygdom) | PLS | PMA - Progressiv muskelatrofi | PBP - Progressiv Bulbar PareseForenede Stater, Italien
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Assistance Publique - Hôpitaux de ParisCentre National de la Recherche Scientifique, FranceAfsluttetAmyotrofisk lateral sklerose | Primær lateral sklerose | Kennedys sygdomFrankrig
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Gillette Children's Specialty HealthcareAfsluttetCerebral Parese | Muskeldystrofi | Osteopeni | Rett syndrom | Spinal muskelatrofi | Spina BifidaForenede Stater
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VegaVect, Inc.National Eye Institute (NEI)Aktiv, ikke rekrutterendeRetinoschisis | X-LinkedForenede Stater
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National Eye Institute (NEI)AfsluttetRetinoschisis | X-LinkedForenede Stater
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National Eye Institute (NEI)AfsluttetRetinoschisis | X-LinkedForenede Stater
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyAfsluttetDuchennes muskeldystrofi | Spinal muskelatrofi type 3Forenede Stater
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Ariel UniversityASST Santi Paolo e CarloAfsluttet
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... og andre samarbejdspartnereRekrutteringX Linked Myotubular MyopatiDet Forenede Kongerige, Canada, Forenede Stater
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Newcastle-upon-Tyne Hospitals NHS TrustRekrutteringX-bundet myotubulær myopati | Centronukleær myopati | Myotubulær myopati | Myotubulær myopati 1 | Myotubulær (Centronuclear) myopati | Centronuclear Myopati, X-LinkedDet Forenede Kongerige
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Bahçeşehir UniversityIkke rekrutterer endnuDuchennes muskeldystrofi | Spinal muskelatrofi | Sunde individer
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Merve KurtRekrutteringDuchennes muskeldystrofi | Virtual reality | Spinal muskelatrofi | Neuromuskulær sygdom | BiofeedbackKalkun
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRekrutteringNeuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Fragilt X syndrom | Kønskromosomforstyrrelser | Fragilt X Mental Retardation Syndrome | Trinukleotid Gentag Udvidelse | Fra(X) syndrom | FXS | Mental retardering, X LinkedForenede Stater, Canada
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Children's Hospital Medical Center, CincinnatiAfsluttetDuchennes muskeldystrofi | Spinal muskelatrofi | Medfødt muskeldystrofi
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Icahn School of Medicine at Mount SinaiRekrutteringAutismespektrumforstyrrelse | DDX3X | Mental retardering, X-linked 102Forenede Stater
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Assistance Publique - Hôpitaux de ParisAfsluttetDuchennes muskeldystrofi | Spinal muskelatrofiFrankrig
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Shenzhen Geno-Immune Medical InstituteUkendt
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Rare Thyroid Therapeutics International ABVitaccess LtdAfsluttetAllan-Herndon-Dudley syndrom | Monocarboxylat Transporter 8 (MCT8) mangelDet Forenede Kongerige
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Universität Duisburg-EssenWeinmann Geräte für Medizin GmbH + Co. KGAfsluttetDuchennes muskeldystrofi | Spinal muskelatrofi | Kronisk respiratorisk insufficiensTyskland
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Pitié-Salpêtrière HospitalRekrutteringLaminopatier | EmerinopatierFrankrig
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRekrutteringMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater, Det Forenede Kongerige, Holland
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Hospices Civils de LyonUkendtX-bundet mental retarderingFrankrig
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRekrutteringX-Linked Hypohidrotisk ektodermal dysplasi (XLHED)Forenede Stater, Spanien, Frankrig, Tyskland, Italien, Det Forenede Kongerige
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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NightstaRx Ltd, a Biogen CompanyTilmelding efter invitationChoroideræmi | X-Linked Retinitis PigmentosaForenede Stater, Det Forenede Kongerige, Holland, Tyskland, Frankrig, Brasilien, Canada, Danmark, Finland
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRekrutteringCerebral Parese | Muskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofi | Spinal muskelatrofi | Lembælte muskeldystrofi | FSHDForenede Stater
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Sheba Medical CenterElMindA LtdRekrutteringFragilt X Associeret Tremor-ataxia Syndrome | FXTASIsrael
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Ovid Therapeutics Inc.AfsluttetFragilt X-syndrom (FXS)Forenede Stater
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Guido A. Davidzon, MD, SMTrukket tilbage
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Tetra Discovery PartnersAfsluttetFragilt X syndrom | Fra(X) syndrom | FXSForenede Stater
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Novartis PharmaceuticalsAfsluttet
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)AfsluttetFragilt X syndromForenede Stater
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Afsluttet
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetFragilt X-syndrom (FXS)Forenede Stater
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X syndromForenede Stater