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Clinical Trials on Genetiske sygdomme, X-forbundet in United States
I alt 7929 resultater
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Wyeth is now a wholly owned subsidiary of PfizerAfsluttet
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater, Canada
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National Institute of Allergy and Infectious Diseases...AfsluttetKronisk granulomatøs sygdomForenede Stater
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National Institute of Allergy and Infectious Diseases...Afsluttet
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National Institute of Allergy and Infectious Diseases...AfsluttetKronisk granulomatøs sygdomForenede Stater
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Children's Mercy Hospital Kansas CityAfsluttetHæmofili A | Hæmofili B | Hæmofili | Faktor IX mangel | Faktor VIII mangelForenede Stater
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Massachusetts General HospitalAfsluttetDuchennes muskeldystrofi | Dystrofinopati | Beckers muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...Ukendt
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Joanne Kurtzberg, MDThe Marcus FoundationRekrutteringMucopolysaccharidosis II | Hjernesygdomme, metaboliske, medfødte | Adrenoleukodystrofi | Battens sygdom | Leukodystrofi, Metakromatisk | Leukodystrofi, globoidcelle | Alpha-Mannosidose | Tay-Sachs sygdom | Pelizaeus-Merzbachers sygdom | Sandhoffs sygdom | Neimann Pick sygdom | Sanfilippo MucopolysaccharidoserForenede Stater
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CSL BehringRekruttering
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater, Canada
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Baylor College of MedicineAicardi Syndrome FoundationRekrutteringHjernelidelser | Aicardis syndromForenede Stater
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University of Colorado, DenverAfsluttet
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Summit TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater, Det Forenede Kongerige
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FibroGenAfsluttetDuchennes muskeldystrofiForenede Stater
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Edgewise Therapeutics, Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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Ultragenyx Pharmaceutical IncAfsluttetHæmofili BForenede Stater, Det Forenede Kongerige, Bulgarien
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Shriners Hospitals for ChildrenAfsluttetDuchennes muskeldystrofiForenede Stater
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OPKO Health, Inc.AfsluttetHæmofili A | Hæmofili BForenede Stater
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Regeneron PharmaceuticalsRekrutteringHæmofili BForenede Stater, Tyskland, Det Forenede Kongerige, Canada
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Cooperative International Neuromuscular Research...AfsluttetMuskeldystrofi, DuchenneForenede Stater, Canada, Argentina, Australien, Israel, Italien
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Sarepta Therapeutics, Inc.Hoffmann-La RocheTilmelding efter invitationDuchennes muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...UkendtBeckers muskeldystrofiForenede Stater, Canada, Italien, Det Forenede Kongerige
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PfizerAktiv, ikke rekrutterendeMuskeldystrofi, DuchenneForenede Stater, Australien
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater, Canada, Det Forenede Kongerige, Sverige, Australien, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater, Canada, Det Forenede Kongerige, Sverige, Australien, Israel
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Capricor Inc.RekrutteringSygdomme i nervesystemet | Genetiske sygdomme, medfødte | Genetiske sygdomme, X-forbundet | Muskelsygdomme | Neuromuskulære sygdomme | Muskeldystrofier | Muskellidelser, atrofisk | Muskeldystrofi, DuchenneForenede Stater
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National Institute of Allergy and Infectious Diseases...RekrutteringKronisk granulomatøs sygdomForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetKronisk granulomatøs sygdomForenede Stater
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Baylor College of MedicineAfsluttetKronisk granulomatøs sygdomForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetKronisk granulomatøs sygdomForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetKronisk granulomatøs sygdomForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetBehandling af kronisk granulomatøs sygdom med allogen stamcelletransplantation versus standard plejeKronisk granulomatøs sygdomForenede Stater
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PTC TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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Bio Products LaboratoryAfsluttetPrimær immundefekt | Wiskott-Aldrich syndrom | Hypogammaglobulinæmi | Almindelig variabel hypogammaglobulinæmi | X-bundet hypogammaglobulinæmi | Immundefekt med Hyper-IgMForenede Stater
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Santhera PharmaceuticalsLedigDuchennes muskeldystrofiForenede Stater, Canada, Israel
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University of California, San FranciscoUniversity of Washington; California Institute of TechnologyRekruttering
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Wyeth is now a wholly owned subsidiary of PfizerAfsluttet
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National Institute of Allergy and Infectious Diseases...RekrutteringKronisk granulomatøs sygdom | CGDForenede Stater
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Sanguine BiosciencesAfsluttetKronisk granulomatøs sygdomForenede Stater
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StemCells, Inc.AfsluttetPelizaeus-Merzbachers sygdomForenede Stater
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RekrutteringDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater
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PTC TherapeuticsMuscular Dystrophy AssociationAfsluttetDuchennes muskeldystrofiForenede Stater
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... og andre samarbejdspartnereAktiv, ikke rekrutterende
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GenethonInstitute of MyologyUkendtDuchennes muskeldystrofiDet Forenede Kongerige, Frankrig
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New York Presbyterian HospitalAfsluttetHæmofili A | Hæmofili BForenede Stater
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Edgewise Therapeutics, Inc.Medpace, Inc.Tilmelding efter invitationBeckers muskeldystrofiForenede Stater, Holland
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CureDuchenneRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater