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Clinical Trials on Myotonisk dystrofi in United States
I alt 804 resultater
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Michael D. Straiko, MDLions VisionGift Research; Eye Bank Association of AmericaRekrutteringFuchs endoteldystrofiForenede Stater
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aTyr Pharma, Inc.AfsluttetFacioscapulohumeral muskeldystrofi (FSHD)Forenede Stater, Frankrig, Italien
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Children's National Research InstituteFoundation to Eradicate DuchenneAktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)AfsluttetMuskeldystrofi, DuchenneForenede Stater
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Cooperative International Neuromuscular Research...Afsluttet
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Cedars-Sinai Medical CenterAfsluttet
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater
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Benitec Biopharma, Inc.RekrutteringOculopharyngeal muskeldystrofiForenede Stater
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University of FloridaAfsluttet
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Sarepta Therapeutics, Inc.Rekruttering
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aTyr Pharma, Inc.AfsluttetFacioscapulohumeral muskeldystrofiForenede Stater, Italien, Holland
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University of Kansas Medical CenterNational Institutes of Health (NIH)AfsluttetFacioscapulohumeral muskeldystrofiForenede Stater
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Rare Disease Research, LLCSarepta Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesIkke længere tilgængeligMedfødt muskeldystrofi på grund af Lamin A/C-mutationForenede Stater
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater
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Avidity Biosciences, Inc.Tilmelding efter invitationDuchennes muskeldystrofi | DMD | Exon 44 | DuchenneForenede Stater
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Children's Hospital Medical Center, CincinnatiAktiv, ikke rekrutterendeMuskuloskeletale abnormiteter | Duchennes muskeldystrofiForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetMeddelelse | Genetisk sygdomForenede Stater
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRekrutteringBeckers muskeldystrofiForenede Stater, Italien
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Cooperative International Neuromuscular Research...Afsluttet
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsAfsluttetBeckers muskeldystrofi | Sund frivilligForenede Stater
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Afsluttet
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aTyr Pharma, Inc.AfsluttetLem-Girdle muskeldystrofier | Facioscapulohumeral muskeldystrofiForenede Stater, Danmark, Frankrig
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Craig McDonald, MDCardero Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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CureDuchenneRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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PTC TherapeuticsGenzyme, a Sanofi CompanyAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater, Det Forenede Kongerige
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University of RochesterLivionex IncAfsluttetEn pilotundersøgelse for at vurdere den foreløbige effektivitet af EDTA øjendråber på båndkeratopatiHornhindedystrofi, båndformetForenede Stater
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Solid Biosciences Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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Solid Biosciences Inc.Aktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterende
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Sarepta Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National...AfsluttetDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiDet Forenede Kongerige, Forenede Stater, Frankrig, Italien
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Bioblast Pharma Ltd.AfsluttetOculopharyngeal muskeldystrofiForenede Stater, Israel, Canada
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Tissue Tech Inc.AfsluttetHornhindedystrofi, epitelial kældermembranForenede Stater
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Newcastle-upon-Tyne Hospitals NHS TrustRekrutteringBethlem myopati | Ullrich medfødt muskeldystrofi 1, Digenic, Col6A1/Col6A2 | Ullrich medfødt muskeldystrofi 1, autosomal recessiv | Ullrich medfødt muskeldystrofi 1, autosomal dominant | Bethlem Myopati 1, Autosomal Recessiv | UCMD | BTHLM1Det Forenede Kongerige
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National Institute of Neurological Disorders and...AfsluttetSund og rask | Dystonisk lidelseForenede Stater
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Epirium Bio Inc.AfsluttetBeckers muskeldystrofiForenede Stater
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital... og andre samarbejdspartnereRekruttering
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Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University of Iowa og andre samarbejdspartnereRekrutteringLembælte muskeldystrofi | Calpain-3-mangel ekstremitetsbælte Muskeldystrofi Type 2A | Lembælte muskeldystrofi Type R1 | LGMD2AForenede Stater, Holland, Det Forenede Kongerige
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Sarepta Therapeutics, Inc.AfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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Sarepta Therapeutics, Inc.AfsluttetSikkerhedsundersøgelse af Eteplirsen til behandling af Duchennes muskeldystrofi i det tidlige stadieDuchenne muskeldystrofi (DMD)Forenede Stater
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University of Texas Southwestern Medical CenterAfsluttetHornhindeødem Sekundært til hornhindeendoteldystrofiForenede Stater
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National Eye Institute (NEI)AfsluttetMakuladegenerationForenede Stater
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Fulcrum TherapeuticsAktiv, ikke rekrutterendeFacioscapulohumeral muskeldystrofi (FSHD)Forenede Stater, Canada, Frankrig, Spanien
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Fulcrum TherapeuticsAfsluttetFacioscapulohumeral muskeldystrofi (FSHD)Forenede Stater, Canada, Frankrig, Spanien
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PfizerRekrutteringDuchennes muskeldystrofiForenede Stater
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Akashi TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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National Institute of Neurological Disorders and...Afsluttet
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Oregon Health and Science UniversityNational Eye Institute (NEI)Rekruttering