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Kliniske forsøg med X-Linked Charcot-Marie-Tooth Disease
I alt 1638 resultater
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Sheba Medical CenterUkendt
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Maastricht University Medical CenterAfsluttet
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUkendtWiskott-Aldrich syndrom | Leukocytadhæsionsmangelsyndrom | X-forbundet agammaglobulinæmi | X-Linked Hyper IgM SyndromeForenede Stater
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Edimer PharmaceuticalsAfsluttetX-forbundet hypohidrotisk ektodermal dysplasiForenede Stater
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University Hospital, Basel, SwitzerlandNovartisAfsluttet
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Hacettepe UniversityAfsluttet
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Stanford UniversityAfsluttetIntellektuel handicap | Fragilt X syndromForenede Stater
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... og andre samarbejdspartnereAfsluttetDowns syndrom | Fragilt X syndromSpanien
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Nova Mentis Life Science CorpFourthWall TestingRekrutteringAutismespektrumforstyrrelse | Fra(X) syndromForenede Stater
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Fundación Pública Andaluza para la Investigación...Delos ClinicalAfsluttet
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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Pitié-Salpêtrière HospitalRekrutteringLaminopatier | EmerinopatierFrankrig
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Ovid Therapeutics Inc.Afsluttet
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RekrutteringRett syndrom | Rett syndrom, atypisk | RTTForenede Stater
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD) | Adrenoleukodystrofi (ALD) | X-forbundet adrenoleukodystrofi (X-ALD)Forenede Stater, Det Forenede Kongerige, Argentina, Canada, Tyskland, Italien, Holland
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University Hospital, ToursAfsluttetSunde frivillige | Autisme | Fragilt-X syndrom (FXS)Frankrig
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GenethonAktiv, ikke rekrutterende
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bluebird bioAktiv, ikke rekrutterendeCerebral adrenoleukodystrofi (CALD) | Adrenoleukodystrofi (ALD) | X-forbundet adrenoleukodystrofi (X-ALD)Forenede Stater, Argentina, Australien, Brasilien, Frankrig, Tyskland, Holland, Det Forenede Kongerige, Italien
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...AfsluttetAlvorlig kombineret immundefekt | Adenosindeaminase mangel | Immunsystem lidelse | Autosomal recessiv lidelse | Purin-nukleosid phosphorylase mangel | Alvorlig kombineret immundefekt med fravær af T- og B-celler | X-forbundet svær kombineret immundefektForenede Stater
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyAfsluttetEpilepsi | Livskvalitet | Dysbiose | Rett syndromItalien
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Newron Pharmaceuticals SPAAfsluttetRett syndromForenede Stater, Indien, Det Forenede Kongerige, Australien, Italien
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCDKL5 | Rett syndrom | MECP2 duplikering | FOXG1 lidelserForenede Stater