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Søg i kliniske forsøg efter: Genetic Disorders
I alt 155019 resultater
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Ionis Pharmaceuticals, Inc.RekrutteringMethyl CpG Binding Protein 2 (MECP2) DuplikationssyndromForenede Stater
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University of ReginaProvincial Health Services Authority; Saskatchewan Health Authority - Regina...RekrutteringCystisk fibrose | Mentalt helbred | Søskende | Internetbaseret interventionCanada
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Jiangsu Gensciences lnc.RekrutteringHæmofili | Hæmofili A med inhibitor | Han | Hæmofili B med inhibitorKina
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Beijing Suncadia Pharmaceuticals Co., LtdIkke rekrutterer endnuHomozygot familiær hyperkolesterolæmi
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CSL BehringRekruttering
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRekruttering
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Recursion Pharmaceuticals Inc.RekrutteringSolid tumor | APC-genmutation | AXIN1 genmutationForenede Stater
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University Hospital, AngersIkke rekrutterer endnu
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NewAmsterdam PharmaRekrutteringDyslipidæmi | Hyperkolesterolæmi | Familiær hyperkolesterolæmi | Højt kolesterol | ASCVDForenede Stater
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CSL BehringRekruttering
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Shandong UniversityIkke rekrutterer endnuPeutz-Jeghers syndrom | TyndtarmspolypKina
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ECOG-ACRIN Cancer Research GroupNational Cancer Institute (NCI)RekrutteringHodgkin lymfom | Non-Hodgkin lymfomForenede Stater
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Gazi UniversityRekrutteringPrimære immundefektsygdommeKalkun
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Assiut UniversityRekrutteringBehcets sygdom med multisystem involveringEgypten
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National Institute of Diabetes and Digestive and...RekrutteringLipodystrofiForenede Stater
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Cliniques universitaires Saint-Luc- Université...RekrutteringInfertilitet, Mand | Klinefelters syndromBelgien
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Mario Negri Institute for Pharmacological ResearchRekrutteringSund og rask | Autosomal dominant polycystisk nyre | Atypisk hæmolytisk uræmisk syndrom | Membranoproliferativ glomerulonefritisItalien
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University of Nevada, Las VegasRekrutteringDowns syndromForenede Stater
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RekrutteringDuchennes muskeldystrofiForenede Stater
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Baylor College of MedicineSouthern Star Research Pty Ltd.Ikke rekrutterer endnuVaskulært Ehlers-Danlos syndromForenede Stater
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Fundación Española de Hematología y HemoterapíaRekrutteringGauchers sygdom | Syre SphingoMyelinase mangelSpanien
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Institute of Hematology & Blood Diseases HospitalRekrutteringGenterapi | Transfusionsafhængig beta-thalassæmiKina
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Virginia Commonwealth UniversityMuscular Dystrophy AssociationRekrutteringLGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2YForenede Stater
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Hoffmann-La RocheRekrutteringHæmofili ASpanien, Canada, Forenede Stater, New Zealand, Italien, Polen
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University of Kansas Medical CenterIkke rekrutterer endnuFedme | Alzheimers sygdom | Downs syndromForenede Stater
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Dartmouth-Hitchcock Medical CenterRekrutteringCystisk fibroseForenede Stater
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Hasan Kalyoncu UniversityIkke rekrutterer endnuHæmofili A | Hæmofili B | HæmofiliKalkun
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Assiut UniversityIkke rekrutterer endnuHæmofili A | Hæmofili B
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Tri-Service General HospitalRekrutteringSvær hæmofili A uden inhibitorTaiwan
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Istanbul University - Cerrahpasa (IUC)Rekruttering
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Laurent ServaisSYSNAVRekrutteringDuchennes muskeldystrofi | Myotonisk dystrofi 1 | Medfødt muskeldystrofi | Centronukleær myopati | Charcot-Marie-Tooth | Fascioscapulohumeral muskeldystrofiBelgien
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Institut National de la Santé Et de la Recherche...Rekruttering
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Masonic Cancer Center, University of MinnesotaNational Institutes of Health (NIH)RekrutteringFanconi Anæmi | Mundhulekarcinom | Alkohol-relateret karcinomForenede Stater
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Stephanie B. Seminara, MDRekrutteringKallmanns syndrom | Hypogonadotropisk hypogonadisme | Forsinket pubertet | Reproduktiv lidelseForenede Stater
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Assistance Publique - Hôpitaux de ParisIkke rekrutterer endnuParadentose | Trisomi 21Frankrig
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Changhua Christian HospitalRekrutteringTranskraniel magnetisk stimulering | Spinocerebellære ataksierTaiwan
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Egyptian Chinese UniversityBenha UniversityRekrutteringDuchennes muskeldystrofiEgypten
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MED-LIFE DISCOVERIES LPBioPharma Services, IncRekrutteringRhizomelic Chondrodysplasia PunctataCanada
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... og andre samarbejdspartnereRekrutteringALS | Kennedys sygdom | MND (motorisk neuronsygdom) | PLS | PMA - Progressiv muskelatrofi | PBP - Progressiv Bulbar PareseForenede Stater, Italien
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PERROD GuillaumeIkke rekrutterer endnu
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Columbia UniversityRekruttering
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Hacettepe UniversityRekruttering
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University Health Network, TorontoTakara Bio Inc.RekrutteringRecidiverende eller refraktær kronisk lymfatisk leukæmi | Relapserende eller refraktær lille lymfatisk lymfom | Recidiverende eller refraktær CD19+ B-celle lymfomCanada
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Rekruttering
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All India Institute of Medical Sciences, New DelhiRekruttering
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X syndromForenede Stater
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Institut National de la Santé Et de la Recherche...RekrutteringNeurofibromatose type 1 | Iktyose | Ektodermal dysplasi | Albinisme | Pemphigus | Slimhinde Pemphigoid | Nedarvet Epidermolysis Bullosa | Palmoplantar Keratodermi | Incontinentia PigmentiFrankrig
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... og andre samarbejdspartnereRekrutteringGlykogenopbevaringssygdom type II | Pompes sygdom (sen debut)Italien
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Institut National de la Santé Et de la Recherche...Rekruttering
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Tobias MoserRekrutteringNedsat hørelse | Otoferlin-relateret auditiv synaptopatiTyskland