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Studi clinici sponsorizzati da Rare Disease Research, LLC
Totale 261 risultati
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatoDistrofia muscolare di DuchenneStati Uniti
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoSindromi mielodisplastiche | Porpora, Trombocitopenica | Anemia, aplastica | Aplasia eritrocitaria, pura | Sindromi da insufficienza del midollo osseo | Emoglobinuria, parossistica | Leucemia, linfocitariaStati Uniti
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoAnemia, aplasticaStati Uniti
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoSindrome mielodisplasicaStati Uniti
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletatoMalattie cerebellari | Sindrome da atassia episodicaStati Uniti, Canada, Regno Unito
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... e altri collaboratoriCompletatoSindrome di Andersen-Tawil | Sindrome di AndersenStati Uniti, Canada, Italia, Regno Unito
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... e altri collaboratoriCompletatoMalattie cerebrali, metaboliche, congenite | Deficit di ornitina transcarbamilasi | Disturbo del ciclo dell'ureaStati Uniti
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Centre for Human Drug Research, NetherlandsRecordati Rare DiseasesCompletatoMicosi fungoideOlanda
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Deka Research and DevelopmentCVS Kidney Care LLC.Attivo, non reclutanteMalattia renale allo stadio terminaleStati Uniti
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Deka Research and DevelopmentCVS Kidney Care LLC.CompletatoMalattia renale allo stadio terminaleStati Uniti
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Clinical Alliance for Research & Education - Infectious...Cubist Pharmaceuticals LLCTerminato
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletatoDisturbi miotonici | Miotonia congenita | Miotonie non distroficheCanada, Stati Uniti, Regno Unito
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University of Alabama at BirminghamPorphyria Rare Disease Clinical Research ConsortiumCompletatoProtoporfiria eritropoietica (EPP)Stati Uniti
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite temporaleStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoDeterminazione dei biomarcatori dell'attività della malattia negli individui con poliarterite nodosaPoliarterite nodosaStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriReclutamentoArterite a cellule giganti | Poliangioite microscopica | Poliarterite nodosa | Arterite di Takayasu | Granulomatosi eosinofila con poliangioite (Churg-Strauss) | Granulomatosi con poliangioite (di Wegener)Stati Uniti, Canada, Tacchino
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare Diseases...CompletatoArterite a cellule giganti | Arterite di TakayasuStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoGranulomatosi di WegenerStati Uniti
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoProtocollo longitudinale per granulomatosi con poliangioite (di Wegener) e poliangioite microscopicaPoliangioite microscopica | Granulomatosi associata a poliangioite | Di WegenerStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite di TakayasuStati Uniti, Canada
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ETS Wound Care, LLCProfessional Education and Research InstituteCompletatoPiede diabetico | Ulcera del piede diabetico | Ulcera al piedeStati Uniti
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Clinical Alliance for Research & Education - Infectious...GlaxoSmithKlineSconosciutoInfezioni da HIV | LipodistrofiaStati Uniti
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletatoDisturbi del ciclo dell'urea, congeniti | Disturbo del ciclo dell'urea | Aciduria Argininosuccinica | Deficit di Argininosuccinato LiasiStati Uniti
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... e altri collaboratoriTerminatoSindrome di Andersen-TawilStati Uniti
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite di TakayasuStati Uniti, Canada
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University College, LondonNIHR Rare Diseases Translational Research Collaboration; Barts Cardiovascular...ReclutamentoMutazione del gene Lamin A/C | Cardiomiopatia dilatativa, familiareRegno Unito
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International Centre for Diarrhoeal Disease Research...CARE Bangladesh; Gram Bikash Kendra (GBK); CARE USAReclutamento
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... e altri collaboratoriCompletatoProtoporfiria eritropoietica | PPE | XLP | Protoporfiria legata all'X | XLPP | Protoporfiria eritropoietica dominante legata all'X | XLEPP | XLDPStati Uniti
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsReclutamentoDeficit del trasportatore monocarbossilato 8 | Sindrome di Allan-Herndon-DudleyStati Uniti, Regno Unito, Olanda
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoLupus eritematoso sistemico
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National Center for Research Resources (NCRR)Stanford UniversityCompletato
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)Northwestern UniversityCompletato
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoDiabete Insipido, Nefrogenico
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoCarenza di ormone della crescita
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National Center for Research Resources (NCRR)Scripps ClinicCompletato
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National Center for Research Resources (NCRR)Mayo ClinicCompletatoPoliradiculoneuropatia, demielinizzante infiammatoria cronica
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoEpidermolisi bollosa acquisita
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoInfezioni da HIV | Sindrome da immunodeficienza acquisita | Sindrome da deperimento dell'HIV
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoEncefalopatia epatica | Cirrosi | Ipertensione portale
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National Center for Research Resources (NCRR)Emory UniversityCompletatoMorbo di Parkinson
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National Center for Research Resources (NCRR)Northwestern UniversitySconosciutoDiabete insipido
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National Center for Research Resources (NCRR)Stanford UniversityCompletatoGlomerulonefrite IGA
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)Boston UniversityCompletato
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoSindrome da immunodeficienza acquisita | Retinite da citomegalovirus
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National Center for Research Resources (NCRR)Northwestern UniversityCompletato
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Children's Hospital Medical Center, CincinnatiNational Center for Research Resources (NCRR); Rare Diseases Clinical Research...CompletatoProteinosi alveolare polmonareStati Uniti, Germania, Italia, Giappone