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임상 시험 검색 : Genetic disease, inborn
총 18602 건
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Caroline Michaela KistorpSanofi아직 모집하지 않음
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National Institute of Allergy and Infectious Diseases...모병
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...아직 모집하지 않음
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University of AarhusAarhus University Hospital모병
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The University of Queensland아직 모집하지 않음
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Universidad Politecnica de MadridHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario Ramon... 그리고 다른 협력자들모병
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Blueskin AS모병건선 | 아토피 피부염 | 백반증 | 탈모증 원형덴마크
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University of Rochester아직 모집하지 않음
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Kathelijn FischerRadboud University Medical Center; University Medical Center Groningen; Maastricht University... 그리고 다른 협력자들모병
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Oman Medical Speciality BoardArmed Forces Hospital, Oman아직 모집하지 않음위기에 처한 낫적혈구병
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Qilu Hospital of Shandong University모병
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics Support...모병
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Societa Italiana di Dermatologia Medica, Chirurgica...모병
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LEO Pharma아직 모집하지 않음
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Suzhou Alphamab Co., Ltd.모병
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research Institute모병
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University of ValenciaAsociación de Fibrosis Quística - Comunidad Valenciana아직 모집하지 않음
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University Hospital, Toulouse아직 모집하지 않음
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Hangzhou Yirui Pharmaceutical Technology Co., Ltd아직 모집하지 않음
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BioMarin Pharmaceutical모병
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Rady Pediatric Genomics & Systems Medicine Institute모병
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Massachusetts General HospitalJohns Hopkins University아직 모집하지 않음
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Inozyme PharmaGACI Global아직 모집하지 않음ATP 결합 카세트 서브패밀리 C 구성원 6 결핍 | 엑토뉴클레오티드 피로포스파타제/포스포디에스테라제 1 결핍
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Vertex Pharmaceuticals Incorporated모병
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical University아직 모집하지 않음
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Children's Hospital Medical Center, CincinnatiMakerere University; Ministry of Health, Uganda; Mulago Hospital, Uganda모병
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Marco CapogrossoRoche-Genentech아직 모집하지 않음
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Kind Pharmaceuticals LLC아직 모집하지 않음
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Bangabandhu Sheikh Mujib Medical University, Dhaka...모병
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Shanghai Institute Of Biological ProductsThe First Affiliated Hospital of Henan University of Science and Technology; First Affiliated... 그리고 다른 협력자들모병
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham Women's and...아직 모집하지 않음알캅톤뇨증 | 호모시스틴; 대사 장애 | 티로신혈증, 제1형 | 티로신혈증, 제2형 | 티로신혈증, 제3형 | MSUD(메이플 시럽 소변 질환)