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Kliniske studier på Trombocitopenia ligada al cromosoma X
Totalt 123 resultater
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Soma JyonouchiBaylor College of MedicineFullførtX-bundet trombocytopeni | Wiskott-Aldrich syndrom (WAS)Forente stater
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Rush University Medical CenterEmory UniversityPåmelding etter invitasjonTuberøs sklerose | Fragilt X-syndrom | Rett syndrom | Hamartoma syndrom, multippel | Angelman syndrom | Kreatinmangel, X-bundet | Telomert 22Q13 Monosomy Syndrome | Kromosom 15Q, delvis slettingForente stater
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Federal Research Institute of Pediatric Hematology...FullførtWiskott-Aldrich syndromDen russiske føderasjonen
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Federal Research Institute of Pediatric Hematology...RekrutteringWiskott-Aldrich syndromDen russiske føderasjonen
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsAvsluttetBlør | Trombocytopeni | Wiskott-Aldrich syndromForente stater
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Novartis PharmaceuticalsAvsluttet
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Sheba Medical CenterElMindA LtdRekrutteringFragilt X Associated Tremor-ataxia Syndrome | FXTASIsrael
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Ovid Therapeutics Inc.FullførtFragilt X-syndrom (FXS)Forente stater
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Guido A. Davidzon, MD, SMTilbaketrukket
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Tetra Discovery PartnersFullførtFragilt X-syndrom | Fra(X) syndrom | FXSForente stater
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...FullførtFragilt X-syndromForente stater
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Seaside Therapeutics, Inc.Fullført
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)FullførtFragilt X-syndromForente stater
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRekrutteringNevroatferdsmanifestasjoner | Genetiske sykdommer, X-linked | Intellektuell funksjonshemming | Fragilt X-syndrom | Kjønnskromosomforstyrrelser | Fragilt X Mental Retardation Syndrome | Trinukleotid gjentatt utvidelse | Fra(X) syndrom | FXS | Mental retardasjon, X LinkedForente stater, Canada
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Fullført
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...Fullført
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Craig EricksonHealx LimitedRekrutteringFragilt X-syndromForente stater
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Elizabeth Berry-KravisFullførtFragilt X-syndromForente stater
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Novartis PharmaceuticalsFullførtFragilt X-syndromForente stater, Spania
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUkjent
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Hoffmann-La RocheFullførtFragilt X-syndromForente stater
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Hoffmann-La RocheFullførtFragilt X-syndromFrankrike, Spania, Forente stater, Peru, Canada, Storbritannia, Chile, Argentina, Mexico, Sverige
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Yolanda de Diego OteroFullført
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Seaside Therapeutics, Inc.FullførtFragilt X-syndromForente stater
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Seaside Therapeutics, Inc.AvsluttetFragilt X-syndromForente stater
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X-syndromForente stater
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Esoterix Genetic Laboratories, LLCUkjentFragilt X-syndromForente stater
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IRCCS Fondazione Stella MarisRekrutteringFragilt X-syndromItalia
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRekrutteringFragilt X-syndromSerbia
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringFragilt X-syndromForente stater
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Tetra Discovery PartnersRekrutteringFragilt X-syndromForente stater
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Zynerba Pharmaceuticals, Inc.RekrutteringFragilt X-syndromForente stater, Australia, Storbritannia, Irland
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Zynerba Pharmaceuticals, Inc.Påmelding etter invitasjonFragilt X-syndromForente stater, Storbritannia, New Zealand, Australia
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National Institute of Mental Health (NIMH)FullførtFriske Frivillige | Fragilt X-syndromForente stater
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis...Fullført
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Zynerba Pharmaceuticals, Inc.FullførtFragilt X-syndromForente stater, New Zealand, Australia
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterFullført
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Novartis PharmaceuticalsFullførtFragilt X-syndromForente stater, Sveits, Tyskland, Australia, Canada, Danmark, Frankrike, Italia, Spania, Storbritannia
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Stanford UniversityFullførtFragilt X-syndromForente stater
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University of California, DavisFullførtFragilt X-syndrom | Genetiske sykdommerForente stater
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Parc de Salut MarFullført
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University of California, DavisFullført
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Université de SherbrookeFRAXA Research FoundationFullført
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University of California, DavisThe National Fragile X FoundationFullført
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Alcobra Ltd.FullførtFragilt X-syndromForente stater, Israel
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Novartis PharmaceuticalsAvsluttetFragilt X-syndromTyskland, Forente stater, Sveits, Australia, Canada, Danmark, Frankrike, Italia, Storbritannia, Spania
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Seaside Therapeutics, Inc.FullførtFragilt X-syndromForente stater
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Stanford UniversityFullført
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Massachusetts General HospitalNational Institutes of Health (NIH)UkjentSunn | Fragilt X-syndromForente stater
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... og andre samarbeidspartnereHar ikke rekruttert ennåFragilt X-syndrom