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Kliniske forsøg med Faktor X-mangel
I alt 13905 resultater
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Assiut UniversityUkendt
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Novartis PharmaceuticalsRekrutteringNLRC4-GOF, AIFEC (autoinflammation med infantil enterocolitis), XIAP-mangel, CDC42-mutationerForenede Stater, Canada, Det Forenede Kongerige, Kalkun, Spanien, Frankrig, Japan, Tjekkiet, Italien
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterAfsluttetX-Linked Dystoni ParkinsonismeFilippinerne
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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Hospices Civils de LyonIkke rekrutterer endnuX-Linked Hypophosphatemic Rickets
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Kyowa Kirin Pharmaceutical Development LtdAfsluttetX-forbundet hypofosfatæmiDet Forenede Kongerige
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Virginia Commonwealth UniversityCSL BehringAfsluttetHæmofili A | Hæmofili B | D-vitamin mangelForenede Stater
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Ultragenyx Pharmaceutical IncAktiv, ikke rekrutterendeOrnithin Transcarbamylase (OTC) mangelCanada, Forenede Stater, Frankrig, Spanien, Det Forenede Kongerige
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University Hospital, Basel, SwitzerlandNovartisAfsluttet
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Duke UniversityNational Institute of Allergy and Infectious Diseases (NIAID); University... og andre samarbejdspartnereRekrutteringAlmindelig variabel immundefekt | X-bundet agammaglobulinæmi | Primær immundefekt | Primære antistofmangler | CVID | XLA | Sekundær hypogammaglobulinæmiForenede Stater
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CSL BehringAfsluttetAlmindelig variabel immundefekt | X-bundet agammaglobulinæmi | Autosomal recessiv agammaglobulinæmiTyskland, Det Forenede Kongerige, Frankrig, Italien, Polen, Rumænien, Spanien, Sverige, Schweiz
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The University of Hong KongQueen Mary Hospital, Hong Kong; Kowloon Hospital, Hong Kong; Castle Peak... og andre samarbejdspartnereAfsluttetSkizofreni | Skizofrenispektrum og andre psykotiske lidelser | Metabolisk syndrom xHong Kong
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NiKang Therapeutics, Inc.RekrutteringNyrekræft | Nyre-neoplasmer | Nyrecellekarcinom | Klarcellet nyrecellekarcinom | Hypoxi | Metastatisk nyrecellekarcinom | Tilbagevendende nyrecellekarcinom | Nyrekræft | Avanceret nyrecellekarcinom | Renale neoplasmer | ccRCC | Refraktært nyrecellekarcinom | Hypoxiinducerbar faktor (HIF) | HIF2α-hæmmer | Hypoxiinducerbar... og andre forholdForenede Stater
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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Sahlgrenska University Hospital, SwedenTilmelding efter invitationTransplantation | Absolut uterin faktor infertilitet | Mrk AnomaliSverige
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases...RekrutteringX-bundet hypofosfatæmi | Hypofosfatæmisk rakitt | Hypophosphatemisk rakitt, X-Linked DominantForenede Stater
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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Bio Products LaboratoryAfsluttetPrimær immundefekt | Wiskott-Aldrich syndrom | Hypogammaglobulinæmi | Almindelig variabel hypogammaglobulinæmi | X-bundet hypogammaglobulinæmi | Immundefekt med Hyper-IgMForenede Stater
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National Cancer Institute (NCI)RekrutteringKræft | HIV | Kronisk granulomatøs sygdom | Dock 8 mangelForenede Stater
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Ultragenyx Pharmaceutical IncRekrutteringKlinisk undersøgelse af DTX301 AAV-medieret genoverførsel for ornithin transcarbamylase (OTC) mangelOTC-mangelForenede Stater, Portugal, Italien, Spanien, Det Forenede Kongerige, Japan, Canada, Tyskland, Frankrig, Argentina, Holland, Brasilien
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University College, LondonRekrutteringOrnithin Transcarbamylase mangelDet Forenede Kongerige
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Arcturus Therapeutics, Inc.Aktiv, ikke rekrutterendeOrnithin Transcarbamylase mangelForenede Stater
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Arcturus Therapeutics, Inc.AfsluttetOrnithin Transcarbamylase mangelNew Zealand
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Translate Bio, Inc.Trukket tilbageOrnithin Transcarbamylase mangel
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Baylor College of MedicineChildren's National Research InstituteRekrutteringOrnithin Transcarbamylase mangel | Urea cyklus lidelse | Carbamylphosphatsyntetasemangel | Argininoravsyresyre | Hyperargininæmi | Citrullinæmi 1 | ARGI mangel | ASL mangel | ASS mangel | NAGS-mangelForenede Stater
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University of the Philippines Manila - Philippine...LedigX-Linked Dystoni ParkinsonismeFilippinerne
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... og andre samarbejdspartnereRekrutteringIntellektuel handicap | Autismespektrumforstyrrelse | Fragilt X syndrom | Udviklingshæmning | Medfødt anomali | Facioscapulohumeral muskeldystrofi 1Forenede Stater