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Clinical Trials on Mucopolysaccharidosis VI in United States
I alt 165 resultater
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LYSOGENEAfsluttetMucopolysaccharidosis IIIATyskland, Brasilien, Det Forenede Kongerige, Frankrig, Holland
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REGENXBIO Inc.Tilmelding efter invitation
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Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo B syndrom)Spanien, Forenede Stater, Brasilien, Det Forenede Kongerige, Portugal, Italien
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Sangamo TherapeuticsAfsluttet
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Orchard TherapeuticsRekrutteringMPS-IH (Hurler syndrom)Holland, Forenede Stater, Italien, Det Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVATaiwan, Forenede Stater, Italien, Det Forenede Kongerige
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ArmaGen, IncAfsluttetMucopolysaccharidosis IForenede Stater
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMorquio A syndrom | Mucopolysaccharidosis IV AForenede Stater
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BioMarin PharmaceuticalGodkendt til markedsføringMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Puerto Rico
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IV A | Mucopolysaccharidosis IVADet Forenede Kongerige
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis I | Hurler syndromForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Det Forenede Kongerige, Canada, Tyskland
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVADet Forenede Kongerige, Forenede Stater, Tyskland
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Ultragenyx Pharmaceutical IncAfsluttet
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Lundquist Institute for Biomedical Innovation at...Ikke rekrutterer endnuMucopolysaccharidosis III | Sanfilippo syndromForenede Stater
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncAfsluttetGenoverførselsundersøgelse af ABO-102 hos patienter med mellem- og avanceret fase af MPS IIIA-sygdomMucopolysaccharidosis III | Sanfilippo syndrom | MPS IIIA | Sanfilippo AForenede Stater, Spanien, Australien
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis Type II (MPS II)Forenede Stater, Brasilien
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis Type II (MPS II)Forenede Stater, Canada
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Ultragenyx Pharmaceutical IncAfsluttetMucopolysaccharidosis | Sly Syndrom | MPS VII | MPS 7Forenede Stater
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological... og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Kognitiv tilbagegangForenede Stater
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BioMarin PharmaceuticalICON plcAfsluttetMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater, Det Forenede Kongerige, Australien, Taiwan, Belgien, Malaysia, Østrig, Canada, Portugal, Frankrig, Irland, Tjekkiet, Danmark, Italien, Holland, Polen, Puerto Rico
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudIkke rekrutterer endnuSanfilippo syndrom type CForenede Stater, Frankrig
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Ultragenyx Pharmaceutical IncAfsluttetMucopolysaccharidosis | Sly Syndrom | Mucopolysaccharidosis VII | MPS VIISpanien, Forenede Stater, Portugal
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncAktiv, ikke rekrutterendeMucopolysaccharidosis III | Sanfilippo syndrom | MPS IIIA | Sanfilippo AForenede Stater, Australien, Spanien
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IV AForenede Stater, Canada, Frankrig, Taiwan, Argentina, Colombia, Spanien, Kalkun, Japan, Saudi Arabien, Holland, Danmark, Korea, Republikken, Brasilien, Det Forenede Kongerige, Tyskland, Norge, Portugal, Italien, Qatar
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IV | Morquios sygdomForenede Stater
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTrukket tilbageMucopolysaccharidosis IV | Morquio A DiseaseDet Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetEn klinisk vurderingsundersøgelse af forsøgspersoner med mucopolysaccharidosis IVA (Morquio syndrom)Morquio A syndrom | MPS IV A | Mucopolysaccharidosis IVAFrankrig, Det Forenede Kongerige, Taiwan, Forenede Stater, Argentina, Holland, Canada, Brasilien, Tyskland, Italien
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JCR Pharmaceuticals Co., Ltd.Tilmelding efter invitation
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ShireAfsluttetSanfilippo syndrom type BForenede Stater, Det Forenede Kongerige, Tyskland
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Ultragenyx Pharmaceutical IncAfsluttetMucopolysaccharidosis | Sly Syndrom | Mucopolysaccharidosis VII | MPS VIIForenede Stater, Brasilien, Mexico, Portugal
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Lysosomale opbevaringssygdomme | RygmarvskompressionForenede Stater, Finland
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REGENXBIO Inc.AfsluttetMucopolysaccharidosis IIBrasilien, Forenede Stater, Det Forenede Kongerige
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Ultragenyx Pharmaceutical IncPRA Health SciencesRekrutteringSly Syndrom | Mucopolysaccharidosis VII | MPS VII | MPS 7Forenede Stater, Tyskland, Brasilien, Argentina, Frankrig, Holland, Portugal, Spanien, Kalkun
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Hurlers syndrom | Hurler-Scheie syndrom | Scheies syndromForenede Stater
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Denali Therapeutics Inc.Tilmelding efter invitationMucopolysaccharidosis IIForenede Stater, Canada, Belgien, Tjekkiet, Holland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurler syndrom | Hurler-Scheie syndromHolland, Frankrig, Tyskland, Det Forenede Kongerige
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ShireAfsluttetHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater, Argentina, Mexico, Spanien, Det Forenede Kongerige
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Hurler-Scheie syndrom | Hurlers syndromForenede Stater, Canada, Tyskland
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis IIForenede Stater, Spanien, Det Forenede Kongerige, Tjekkiet, Frankrig, Canada, Italien, Belgien, Holland, Tyskland, Argentina, Sverige, Kalkun, Colombia, Brasilien
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurlers syndrom | Hurler-Scheie syndromForenede Stater, Canada, Det Forenede Kongerige, Brasilien, Tyskland, Italien, Holland
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TakedaTakeda Development Center Americas, Inc.RekrutteringHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetHurler syndrom | Sanfilippo syndrom type A | Sanfilippo syndrom type BForenede Stater
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Manchester University NHS Foundation TrustOrchard TherapeuticsRekrutteringMucopolysaccharidoserDet Forenede Kongerige
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ShireAfsluttetMucopolysaccharidosis (MPS)Forenede Stater, Canada, Det Forenede Kongerige, Kalkun, Italien, Mexico, Spanien
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis | Hurler syndrom | Sphingolipidoser | Peroxisomale lidelser | Krabbes sygdom | Adrenoleukodystrofi (ALD) | Hunters syndrom | Sly Syndrom | Fucosidosis | Aspartylglucosaminuri | Alpha Mannosidose | Metakromatisk leukodystrofi (MLD) | Maroteaux-Lamy syndromForenede Stater
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REGENXBIO Inc.Trukket tilbage
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REGENXBIO Inc.Tilmelding efter invitation