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Kliniske forsøg med X-Linked Dystoni Parkinsonisme
I alt 1605 resultater
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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University Hospital, Basel, SwitzerlandNovartisAfsluttet
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Stanford UniversityAfsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuel udviklingsforstyrrelse (IDD)Forenede Stater
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Children's Hospital Medical Center, CincinnatiIkke rekrutterer endnuAutismespektrumforstyrrelse | Fragilt X syndrom
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige
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NeuroVia, Inc.UkendtX-forbundet adrenoleukodystrofiForenede Stater
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Indiana UniversityAfsluttetFragilt X syndrom | AutismespektrumforstyrrelserForenede Stater
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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Universitaire Ziekenhuizen KU LeuvenKU LeuvenAfsluttetMeddelelse | Forældre-barn relationer | Opførsel, barnBelgien
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUkendtWiskott-Aldrich syndrom | Leukocytadhæsionsmangelsyndrom | X-forbundet agammaglobulinæmi | X-Linked Hyper IgM SyndromeForenede Stater
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RekrutteringRett syndrom | Rett syndrom, atypisk | RTTForenede Stater
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Thomas S. ScanlanTrukket tilbageAdrenomyeloneuropati | X-forbundet adrenoleukodystrofiForenede Stater
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Institute for Neurodegenerative DisordersAfsluttetParkinsons sygdom | Alzheimers sygdom | Mild kognitiv svækkelse | Fragilt X syndrom | Huntingtons sygdom | Autistiske Spektrum ForstyrrelserForenede Stater
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Nova Mentis Life Science CorpKGK Science Inc.SuspenderetKognitiv dysfunktion | Fragilt X syndrom | OpførselCanada
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RespireRxFRAXA Research FoundationAfsluttetFragilt X syndrom | AutismeForenede Stater
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ProgenaBiomeRekrutteringAutismespektrumforstyrrelse | Autistisk lidelse | Autisme | Autisme, Akinetisk | Autisme; Atypisk | Autisme; Psykopati | Autisme skrøbeligt syndrom X | Autisme med høje kognitive evner | Autisme-relateret taleforsinkelse | Autisme, modtagelighed for, 6 | Autismespektrumforstyrrelse højfungerende | Autistisk tænkning og andre forholdForenede Stater
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyAfsluttetEpilepsi | Livskvalitet | Dysbiose | Rett syndromItalien
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Newron Pharmaceuticals SPAAfsluttetRett syndromForenede Stater, Indien, Det Forenede Kongerige, Australien, Italien
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCDKL5 | Rett syndrom | MECP2 duplikering | FOXG1 lidelserForenede Stater
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Cliniques universitaires Saint-Luc- Université...RekrutteringParkinsons sygdomBelgien
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom | MECP2 duplikationsforstyrrelse | Rett-relateret lidelseForenede Stater
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Rigshospitalet, DenmarkAfsluttet
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD) | Adrenoleukodystrofi (ALD) | X-forbundet adrenoleukodystrofi (X-ALD)Forenede Stater, Det Forenede Kongerige, Argentina, Canada, Tyskland, Italien, Holland
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Ariel UniversityAssociazione Italiana Rett (AIRETT)Ikke rekrutterer endnuRett syndromItalien
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetRett syndrom | CDKL5 lidelse | MECP2 Duplikationslidelse | FOXG1 syndromForenede Stater
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Janssen Pharmaceutical K.K.RekrutteringX-Linked Retinitis PigmentosaJapan
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University og andre samarbejdspartnereRekrutteringX-Linked Retinitis PigmentosaKina
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Janssen Pharmaceutical K.K.RekrutteringX-Linked Retinitis PigmentosaJapan
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bluebird bioAktiv, ikke rekrutterendeCerebral adrenoleukodystrofi (CALD) | Adrenoleukodystrofi (ALD) | X-forbundet adrenoleukodystrofi (X-ALD)Forenede Stater, Argentina, Australien, Brasilien, Frankrig, Tyskland, Holland, Det Forenede Kongerige, Italien