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Clinical Trials on X-bundet adrenoleukodystrofi in United Kingdom
I alt 1783 resultater
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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Stanford UniversityAfsluttetIntellektuel handicap | Fragilt X syndromForenede Stater
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Edimer PharmaceuticalsAktiv, ikke rekrutterendeX-bundet hypohidrotisk ektodermal dysplasiForenede Stater, Det Forenede Kongerige, Frankrig, Tyskland, Italien
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases...AfsluttetHypophosphatemisk rakitt, X Linked DominantForenede Stater
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Rett Syndrome Research TrustDuke UniversityAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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SwanBio Therapeutics, Inc.RekrutteringAMN | AMN-genmutation | X-ALDHolland, Forenede Stater
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Rett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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Hugo W. Moser Research Institute at Kennedy Krieger...Afsluttet
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasAfsluttetX-Linked Retinitis PigmentosaDet Forenede Kongerige, Forenede Stater
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University of FloridaAudentes TherapeuticsAfsluttetX-bundet myotubulær myopatiForenede Stater
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Neurogene Inc.RekrutteringRett syndromForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetRett syndromForenede Stater
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationAfsluttet
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University of North Carolina, Chapel HillAfsluttetFragilt X syndrom | Psykose | AutismespektrumforstyrrelserForenede Stater
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Ovid Therapeutics Inc.Afsluttet
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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Edison Pharmaceuticals IncTrukket tilbage
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgAfsluttet
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Rett Syndrome Research TrustVanderbilt University Medical CenterAfsluttetRett syndromForenede Stater
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Stanford UniversityAfsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuel udviklingsforstyrrelse (IDD)Forenede Stater
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National Institute of Allergy and Infectious Diseases...RekrutteringX-bundet svær kombineret immundefekt (XSCID)Forenede Stater
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspenderetSvær kombineret immundefektsygdom, X-bundetForenede Stater
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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ACADIA Pharmaceuticals Inc.Afsluttet
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Indiana UniversityAfsluttetFragilt X syndrom | AutismespektrumforstyrrelserForenede Stater
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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ACADIA Pharmaceuticals Inc.Afsluttet
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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Janssen Research & Development, LLCJanssen Research & Development, LLCAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater, Canada, Israel, Det Forenede Kongerige, Spanien, Danmark, Frankrig, Belgien, Italien, Holland, Schweiz
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUkendtWiskott-Aldrich syndrom | Leukocytadhæsionsmangelsyndrom | X-forbundet agammaglobulinæmi | X-Linked Hyper IgM SyndromeForenede Stater
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Masonic Cancer Center, University of MinnesotaTrukket tilbage
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Nido Biosciences, Inc.RekrutteringSpinal og Bulbar muskelatrofi | Kennedys sygdomKorea, Republikken, Danmark, Italien, Det Forenede Kongerige
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REGENXBIO Inc.AfsluttetMucopolysaccharidosis IIBrasilien, Forenede Stater, Det Forenede Kongerige
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige
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Janssen Research & Development, LLCJanssen Research & Development, LLCAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaBelgien, Canada, Forenede Stater, Israel, Det Forenede Kongerige, Spanien, Danmark, Frankrig, Italien, Holland, Schweiz
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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ProgenaBiomeRekrutteringAutismespektrumforstyrrelse | Autistisk lidelse | Autisme | Autisme, Akinetisk | Autisme; Atypisk | Autisme; Psykopati | Autisme skrøbeligt syndrom X | Autisme med høje kognitive evner | Autisme-relateret taleforsinkelse | Autisme, modtagelighed for, 6 | Autismespektrumforstyrrelse højfungerende | Autistisk tænkning og andre forholdForenede Stater
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RespireRxFRAXA Research FoundationAfsluttetFragilt X syndrom | AutismeForenede Stater
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)AfsluttetAdrenoleukodystrofi | AdrenomyeloneuropatiForenede Stater
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater