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Clinical Trials on X-bundet adrenoleukodystrofi in United Kingdom
I alt 1783 resultater
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RekrutteringRett syndrom | Rett syndrom, atypisk | RTTForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetVækstsvigt | X-bundet svær kombineret immundefekt (XSCID) | VæksthormonresistensForenede Stater
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Denali Therapeutics Inc.AfsluttetMucopolysaccharidosis IIDet Forenede Kongerige, Forenede Stater, Holland
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Hugo W. Moser Research Institute at Kennedy Krieger...AfsluttetAdrenoleukodystrofiForenede Stater
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige
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Mitsubishi Tanabe Pharma America Inc.RekrutteringErytropoietisk protoporfyri (EPP) | X-forbundet protoporfyri (XLP)Forenede Stater, Spanien, Frankrig, Japan, Det Forenede Kongerige, Italien, Australien, Polen, Bulgarien, Tjekkiet, Holland
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasiForenede Stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringAutismespektrumforstyrrelse | Fragilt X syndrom | Udviklingsforsinkelse | Genetisk lidelse | Asperger lidelseForenede Stater
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCDKL5 | Rett syndrom | MECP2 duplikering | FOXG1 lidelserForenede Stater
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringAutismespektrumforstyrrelse | Autistisk lidelse | Fragilt X syndrom | Aspergers syndromForenede Stater
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GenethonAktiv, ikke rekrutterendeX-forbundet kronisk granulomatøs sygdomDet Forenede Kongerige
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Denali Therapeutics Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis IIForenede Stater, Holland, Canada, Det Forenede Kongerige
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom | MECP2 duplikationsforstyrrelse | Rett-relateret lidelseForenede Stater
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NightstaRx Ltd, a Biogen CompanyAfsluttetX-Linked Retinitis PigmentosaForenede Stater, Frankrig, Det Forenede Kongerige, Finland, Holland, Tyskland, Canada
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Manchester University NHS Foundation TrustAfsluttetMucopolysaccharidosis Type IIDet Forenede Kongerige
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Applied Genetic Technologies CorpAfsluttetX-Linked Retinitis PigmentosaForenede Stater
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrAfsluttet
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Great Ormond Street Hospital for Children NHS Foundation...Trukket tilbageGranulomatøs sygdom, Kronisk, X-bundet, VariantDet Forenede Kongerige
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National Institute of Allergy and Infectious Diseases...AfsluttetImmunproliferativ lidelseForenede Stater
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4D Molecular TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetRett syndrom | CDKL5 lidelse | MECP2 Duplikationslidelse | FOXG1 syndromForenede Stater
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Beacon TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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Beacon TherapeuticsRekruttering
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Beacon TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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National Institute of Allergy and Infectious Diseases...UkendtX-forbundne kombinerede immundefektsygdommeForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetAlvorlig kombineret immundefektForenede Stater
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ShireAfsluttetMucopolysaccharidosis IIForenede Stater, Det Forenede Kongerige, Brasilien, Tyskland
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Beacon TherapeuticsTilmelding efter invitationX-Linked Retinitis PigmentosaForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetGenetiske sygdomme, X-forbundet | Lymfoproliferativ sygdom | X-forbundet lymfoproliferativ sygdomForenede Stater
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ShireAfsluttetHunters syndromDet Forenede Kongerige, Forenede Stater, Brasilien
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige
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Masonic Cancer Center, University of MinnesotaAfsluttetSeglcellesygdom | Thalassæmi | Cerebral adrenoleukodystrofi | Arvelige stofskifteforstyrrelser | Højrisiko hæmatologiske lidelserForenede Stater
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ShireAfsluttetHunters syndromForenede Stater, Spanien, Canada, Det Forenede Kongerige, Mexico, Australien, Frankrig
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRekrutteringRestless Legs Syndrome | AdrenoleukodystrofiForenede Stater, Holland
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Edimer PharmaceuticalsAfsluttetX-forbundet hypohidrotisk ektodermal dysplasiForenede Stater
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JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis IIForenede Stater, Tyskland, Spanien, Frankrig, Brasilien, Argentina, Kalkun, Det Forenede Kongerige, Polen, Italien
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ShireAfsluttetHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater, Argentina, Mexico, Spanien, Det Forenede Kongerige
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiForenede Stater
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustAfsluttet
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Atsena Therapeutics Inc.RekrutteringX-bundet retinoschisisForenede Stater
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Applied Genetic Technologies CorpAfsluttetX-bundet retinoschisisForenede Stater
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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Ionis Pharmaceuticals, Inc.RekrutteringMethyl CpG Binding Protein 2 (MECP2) DuplikationssyndromForenede Stater
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRekrutteringPyruvat dehydrogenase kompleks mangel | Pyruvat dehydrogenase E1 alfa-mangel | Pyruvat Dehydrogenase E1-Beta mangel | Pyruvat dehydrogenase E2 mangel | Pyruvat Dehydrogenase Phosphatase mangelDet Forenede Kongerige
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State University of New York - Upstate Medical...AfsluttetFamiliær encefalopati med neuroserpin-inklusionskroppe | X-bundet mental retardering | Medfødt lodret talus | Idiopatisk generaliseret epilepsi | Familiær demensForenede Stater
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Tilmelding efter invitationIntellektuel handicap | Downs syndrom | Attention Deficit Hyperactivity Disorder | Fragilt X syndromForenede Stater
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Fairview University Medical CenterAfsluttetImmunologiske mangelsyndromer | Almindelig variabel immundefekt | Alvorlig kombineret immundefekt | Kronisk granulomatøs sygdom | Hæmofagocytisk lymfohistiocytose | Wiskott-Aldrich syndrom | Pode versus værtssygdom | X-bundet agammaglobulinæmi | Chediak-Higashi syndrom | Virus-associeret hæmofagocytisk syndrom og andre forholdForenede Stater
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Applied Genetic Technologies CorpFoundation Fighting BlindnessAfsluttetX-bundet retinoschisis | XLRSForenede Stater
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Novartis PharmaceuticalsAfsluttetSpinal og Bulbar muskelatrofiForenede Stater, Tyskland, Italien, Danmark
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University of California, San DiegoRocket Pharmaceuticals Inc.Rekruttering