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Kliniske forsøg med X-forbundet hypofosfatæmi
I alt 3855 resultater
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Rett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetRett syndromForenede Stater
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Ukendt
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Assistance Publique Hopitaux De MarseilleUkendt
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationAfsluttet
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Sheba Medical CenterUltragenyx Pharmaceutical IncUkendt
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Central Hospital, Nancy, FranceAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...Afsluttet
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Sheba Medical CenterUkendt
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Maastricht University Medical CenterAfsluttet
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Astellas Gene TherapiesAfsluttetX-bundet myotubulær myopatiForenede Stater, Frankrig, Det Forenede Kongerige, Canada, Tyskland
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University of FloridaAudentes TherapeuticsAfsluttetX-bundet myotubulær myopatiForenede Stater
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Great Ormond Street Hospital for Children NHS Foundation...UkendtX-bundet svær kombineret immundefektDet Forenede Kongerige
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University of North Carolina, Chapel HillAfsluttetFragilt X syndrom | Psykose | AutismespektrumforstyrrelserForenede Stater
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspenderetSvær kombineret immundefektsygdom, X-bundetForenede Stater
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterAfsluttetX-Linked Dystoni ParkinsonismeFilippinerne
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Ovid Therapeutics Inc.Afsluttet
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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Stanford UniversityAfsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuel udviklingsforstyrrelse (IDD)Forenede Stater
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Kyowa Kirin Korea Co., Ltd.RekrutteringFGF23-relateret hypofosfatæmisk rakitt og osteomalaciKorea, Republikken
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University Hospital, Basel, SwitzerlandNovartisAfsluttet
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National Institute of Allergy and Infectious Diseases...RekrutteringX-bundet svær kombineret immundefekt (XSCID)Forenede Stater
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Assistance Publique - Hôpitaux de ParisAfsluttetX-bundet svær kombineret immundefektFrankrig
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University of the Philippines Manila - Philippine...LedigX-Linked Dystoni ParkinsonismeFilippinerne
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige