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Søg i kliniske forsøg efter: Genetic diseases, Inborn
I alt 18719 resultater
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Hoffmann-La RocheSarepta Therapeutics, Inc.Rekruttering
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Martin DichgansRekrutteringCerebral amyloid angiopatiTyskland
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Hacettepe UniversityIkke rekrutterer endnu
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Innovent Biologics (Suzhou) Co. Ltd.RekrutteringSkjoldbruskkirteløjensygdom, TEDKina
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First Affiliated Hospital Xi'an Jiaotong UniversityRekruttering
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Affiliated Hospital of Guangdong Medical UniversityIkke rekrutterer endnuHæmofili B uden inhibitor
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Vanderbilt University Medical CenterRekrutteringDuchennes muskeldystrofiForenede Stater
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Liverpool Heart and Chest Hospital NHS Foundation...Ikke rekrutterer endnuCystisk fibrose
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Maastricht University Medical CenterRekruttering
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Royal Brompton & Harefield NHS Foundation TrustIkke rekrutterer endnuCystisk fibroseDet Forenede Kongerige
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BiocadRekrutteringHæmofili BDen Russiske Føderation
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Zhejiang UniversityIkke rekrutterer endnuHæmofili B uden inhibitor
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Massachusetts General HospitalJohns Hopkins UniversityRekrutteringNeurofibromatose 1Forenede Stater
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Eli Lilly and CompanyRekrutteringSund og rask | Atopisk dermatitisJapan, Forenede Stater
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Amicus TherapeuticsRekrutteringPompes sygdomForenede Stater, Tyskland
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Motric BioRekrutteringSlag | Multipel sclerose | Cerebral Parese | Rygmarvsskader | Dystoni | Muskelspasticitet | Arvelig spastisk paraplegi | Hypertoni, muskelForenede Stater
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Université de Reims Champagne-ArdenneIkke rekrutterer endnu
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Lysosomal and Rare Disorders Research and Treatment...RekrutteringKnoglesygdomme | Gauchers sygdomForenede Stater
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Johns Hopkins UniversityDoris Duke Charitable FoundationRekrutteringAtopisk dermatitisForenede Stater
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Keymed Biosciences Co.LtdIkke rekrutterer endnu
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West China HospitalRekruttering
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University College, LondonRekrutteringArvelig sensorisk neuropati type IDet Forenede Kongerige
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRekruttering
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Puerta de Hierro University HospitalParc Taulí Hospital UniversitariRekruttering
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Xiaoping LuoRekrutteringBarndom kort staturKina
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Shanghai Belief-Delivery BioMed Co., LtdShanghai MYGT Biopharmaceutical LLCRekruttering
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Sling Therapeutics, Inc.RekrutteringØjensygdomme | Sygdomme i det endokrine system | Skjoldbruskkirtelsygdomme | Skjoldbruskkirtlen øjensygdom | Graves Oftalmopati | Eksophthalmos | Orbitale sygdomme | Thyreoideaassocieret oftalmopati | Graves orbitopati | Proptosis | IGF1R | HashimotoForenede Stater
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Verve Therapeutics, Inc.Ikke rekrutterer endnuHyperkolesterolæmi | Aterosklerotisk kardiovaskulær sygdom | Heterozygot familiær hyperkolesterolæmiNew Zealand, Det Forenede Kongerige
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Hospices Civils de LyonIkke rekrutterer endnuLowry Wood syndrom | Roifman syndrom | Taybi Linders syndrom | Microcephalic Osteodysplastic Primordial Dwarfism Type I og IIIFrankrig
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Emory UniversityNational Center for Complementary and Integrative Health (NCCIH)Rekruttering
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SVR GroupIkke rekrutterer endnu
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Hacettepe UniversityIkke rekrutterer endnuDuchennes muskeldystrofiKalkun
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Novo Nordisk A/SRekruttering
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Novozymes A/SAnalyze & RealizeIkke rekrutterer endnu
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Centre Hospitalier Universitaire de la RéunionRekrutteringLipodystrofi | Dunnigan syndromGenforening
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Hoffmann-La RocheRekrutteringSkjoldbruskkirtlen øjensygdomKorea, Republikken, Det Forenede Kongerige, Forenede Stater, Canada, Kina, Israel, Frankrig, Spanien
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The 923rd Hospital of Joint Logistics Support Force...Guangzhou Reforgene Medicine Co., Ltd.RekrutteringHæmoglobinopatier | Arvelige sygdomme | Alpha Thalassæmi Hæmoglobin H Konstant SpringKina
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University of RochesterUnited States Department of DefenseRekruttering
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Memorial Sloan Kettering Cancer CenterRekrutteringSolid tumor | Neuroblastom | Solid tumor, voksen | Primær hjernetumor | Fast karcinom | Gliom af lav kvalitet | Tumor i centralnervesystemet | Ildfast kræft | CNS-tumor, voksen | CNS-tumorer | NF1 | Plexiformt neurofibrom | CNS-tumor, barndom | Optic Pathway Gliomas | MAP Kinase familie genmutationForenede Stater
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Newark Beth Israel Medical CenterGenentech, Inc.Ikke rekrutterer endnu
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Medical University of South CarolinaRekrutteringHypermobilt Ehlers-Danlos syndrom | Ehlers-Danlos syndrom | Hypermobil spektrumforstyrrelseForenede Stater
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Universitair Ziekenhuis BrusselIkke rekrutterer endnu
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Keratoplasty Alliance InternationalRekrutteringHornhindesygdom | Hornhindetransplantationsfejl | Endotel hornhindedystrofi | Afvisning af hornhindetransplantationForenede Stater
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Edgewise Therapeutics, Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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SanofiRegeneron PharmaceuticalsRekrutteringModerat til svær atopisk dermatitisCanada
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Azidus BrasilCellavita Pesquisa Científica LtdaIkke rekrutterer endnuHuntingtons sygdom
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National Institute of Allergy and Infectious Diseases...RekrutteringEksem | Atopisk dermatitisForenede Stater
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Weill Medical College of Cornell UniversityNational Cancer Institute (NCI)RekrutteringKolorektal cancer | Endometriecancer | Arvelige kræftsyndromerForenede Stater
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National Human Genome Research Institute (NHGRI)RekrutteringMetabolisk sygdom | Purin-pyrimidin metabolisme | AICDA, OMIM *605257, Immundefekt med Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A, OMIM *606224, Anæmi, hæmolytisk, på grund af UMPH1-mangel | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064, Millers syndrom... og andre forholdForenede Stater
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Vanderbilt University Medical CenterRekrutteringDuchennes muskeldystrofiForenede Stater