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Søg i kliniske forsøg efter: Inborn Genetic Disease
I alt 383886 resultater
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Clinuvel Europe LimitedRekruttering
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Belite Bio, IncIkke rekrutterer endnuStargardts sygdom 1 | STGD1Forenede Stater
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University of Mississippi Medical CenterUniversity of Alabama at BirminghamRekruttering
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Beam Therapeutics Inc.Ikke rekrutterer endnuAlpha 1-Antitrypsin mangelDet Forenede Kongerige
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AbbVieRekruttering
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RTI InternationalRekrutteringSeglcellesygdomForenede Stater
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University of UtahRekrutteringTourettes syndrom | Tic lidelser | Tics | Tourettes syndrom hos børn | Tourettes syndrom i ungdomsårene | Vokal Tic | Motor Tic | Tics/SkælvenForenede Stater
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Yonsei UniversityRekrutteringTarm Behcet sygdomKorea, Republikken
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AkesoRekruttering
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Viridian Therapeutics, Inc.RekrutteringSkjoldbruskkirtlen øjensygdomForenede Stater
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BioMarin PharmaceuticalIkke rekrutterer endnuIdiopatisk kort statur
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AstraZenecaParexelRekrutteringDilateret kardiomyopatiForenede Stater
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Shanghai Ninth People's Hospital Affiliated to...RekrutteringNeurofibromatose 1 | Plexiformt neurofibromKina
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The First Affiliated Hospital of Zhejiang Chinese...RekrutteringInflammatorisk respons | Tourettes syndrom hos børn | FødevareintoleranceKina
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Regeneron PharmaceuticalsIntellia TherapeuticsIkke rekrutterer endnu
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IRCCS Eugenio MedeaRekrutteringMyotonisk dystrofi 1Italien
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IRCCS Eugenio MedeaRekrutteringMuskeldystrofier | Beckers muskeldystrofi | Lembælte muskeldystrofi | Facio-Scapulo-Humeral DystrofiItalien
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Assiut UniversityIkke rekrutterer endnu
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Ray Therapeutics, Inc.The Vision Research and Assessment Institute (VRAI)RekrutteringRetinitis PigmentosaForenede Stater
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)Ikke rekrutterer endnuSmerte | Seglcellesygdom
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Apollo Therapeutics LtdIkke rekrutterer endnuMyelodysplastisk syndrom med overskydende blaster | Akut myeloid leukæmi, i tilbagefald | Akut myeloid leukæmi refraktær | Myelodysplastisk Syndrom Akut Myeloid Leukæmi
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Enzyre B.V.Indiana Hemophilia & Thrombosis CenterIkke rekrutterer endnu
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Chugai PharmaceuticalIkke rekrutterer endnuAntifosfolipidsyndrom (APS) | Immun trombocytopeni (ITP) | Dermatomyositis (DM) | Bullous Pemfigoid (BP) | Behçets syndrom (BS) | Immunmedieret nekrotiserende myopati (IMNM)Forenede Stater, Japan
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Hospices Civils de LyonRekruttering
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Centre Hospitalier Universitaire de la RéunionRekruttering
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Massachusetts General Hospitaln-Lorem FoundationIkke rekrutterer endnu
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Medical University of WarsawRekrutteringSkjoldbruskkirtlen øjensygdom | Oftalmopati | Orbitopati, GravesPolen
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Fondazione Policlinico Universitario Agostino Gemelli...RekrutteringDuchennes muskeldystrofi | Naturhistorie | Motor funktion; RetarderingItalien
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Harmony Biosciences, LLCRekrutteringPrader-Willi syndromForenede Stater
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Instituto de Investigación Hospital Universitario...Rekruttering
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)Rekruttering
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University of Kansas Medical CenterRekrutteringCystisk fibroseForenede Stater
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Children's Hospital of PhiladelphiaIkke rekrutterer endnu
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AstraZenecaRekruttering
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Editas Medicine, Inc.Ikke rekrutterer endnuSeglcellesygdom | Hæmoglobinopatier | Transfusionsafhængig beta-thalassæmi
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OctapharmaRekruttering
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University Hospital, ToulouseIkke rekrutterer endnu
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West China HospitalIkke rekrutterer endnuKunstig intelligens | Atopisk dermatitis
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Chang Gung UniversityRekruttering
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Technoderma Medicines Inc.Therapeutics, Inc.Rekruttering
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University of MalagaIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiSpanien
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Fondazione SISA (Societa Italiana per lo Studio...RekrutteringFamiliær hyperkolesterolæmi | Genetisk lidelseItalien
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Seoul National University HospitalIkke rekrutterer endnuMuskeldystrofi, Duchenne | Øvre ekstremitet | Ortotiske enhederKorea, Republikken
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AstraZenecaIkke rekrutterer endnuNeurofibromatose 1 | Neurofibrom, Plexiform
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Cliniques universitaires Saint-Luc- Université...RekrutteringSjældne sygdomme | Medfødte metabolismefejlBelgien
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Xuanwu Hospital, BeijingIkke rekrutterer endnu
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Peking University Third HospitalRekrutteringSkjoldbruskkirtlen øjensygdomKina
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Alnylam PharmaceuticalsRekrutteringArvelig amyloidose, transthyretin-relateret | Asymptomatisk bærertilstandFrankrig
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Children's National Research InstituteThe Hospital for Sick Children; Ann & Robert H Lurie Children's Hospital... og andre samarbejdspartnereRekruttering