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Søg i kliniske forsøg efter: Inborn Genetic Disease
I alt 383886 resultater
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Chia Tai Tianqing Pharmaceutical Group Nanjing...Ikke rekrutterer endnu
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... og andre samarbejdspartnereIkke rekrutterer endnu
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Spark Therapeutics, Inc.Rekruttering
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John ElfarIkke rekrutterer endnuKarpaltunnelsyndrom | Kompressionsneuropati
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Lise AksglædeIkke rekrutterer endnuKlinefelters syndrom
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Cystic Fibrosis FoundationRekrutteringCystisk fibrose | ForældrestatusForenede Stater
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Istituto Auxologico ItalianoRekruttering
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Istituto Auxologico ItalianoRekrutteringPrader-Willi syndromItalien
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Istituto Auxologico ItalianoRekrutteringVæksthormonmangel | Kort staturItalien
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IRCCS Fondazione Stella MarisRekrutteringFragilt X syndromItalien
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Zhongmou TherapeuticsIkke rekrutterer endnu
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Suzhou Municipal HospitalIkke rekrutterer endnuFamiliær hyperkolesterolæmi | Refraktær hyperkolesterolæmi
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ViGeneron GmbHRekruttering
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Halic UniversityRekrutteringCystisk fibrose | ForældreKalkun
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CorrectSequence Therapeutics Co., LtdRekrutteringBeta-thalassæmi majorKina
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRekrutteringLivskvalitet | Transthyretin amyloidose | Transthyretin amyloid kardiomyopati | Vildtype transthyretin-relateret (ATTR) amyloidoseDanmark
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Children's Hospital Medical Center, CincinnatiChildren's Hospital of Philadelphia; Emory University; Nemours Children's...Ikke rekrutterer endnu
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Rege Nephro Co., Ltd.RekrutteringAutosomal dominant polycystisk nyresygdom (ADPKD)Japan
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University Hospital, RouenIkke rekrutterer endnu
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases...Ikke rekrutterer endnuMuskeldystrofi | Dyrke motion | Duchennes muskeldystrofi | Vasodilatation | DMD | Muskeldystrofi hos børn | Duchennes sygdom
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South Egypt Cancer InstituteAssiut University; Shefa Al-orman Children Cancer HospitalRekruttering
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Ondokuz Mayıs UniversityRekrutteringLivskvalitet | Ufrivillig vandladning | Overgangsalderen | Wolmans sygdom | Psykologisk velværeKalkun
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Staidson (Beijing) Biopharmaceuticals Co., LtdRekruttering
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Assistance Publique - Hôpitaux de ParisIkke rekrutterer endnu
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UMC UtrechtAlfasigma S.p.A.; ReumaNederland; Autoimmune Research and Collaboration HubIkke rekrutterer endnuIgG4-relateret sygdom | Idiopatiske inflammatoriske myopatier | Behcets sygdomHolland
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Bioray LaboratoriesInstitute of Hematology & Hospital of Blood Diseases, Chinese Academy...Ikke rekrutterer endnu
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Agios Pharmaceuticals, Inc.Ikke rekrutterer endnuSeglcellesygdom | Nefropati
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Oslo University HospitalNorwegian National Advisory Unit on Rare Disorders, Oslo University HospitalRekrutteringCystisk fibrose hos børnNorge
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Bioray LaboratoriesNanfang Hospital, Southern Medical UniversityIkke rekrutterer endnuSeglcellesygdom
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Kirsehir Ahi Evran UniversitesiTC Erciyes UniversityIkke rekrutterer endnuBørn | Cystisk fibrose | Lungefunktioner | Mødre | Latter yoga | Latterterapi | Modstandsdygtighed, Psykologisk | Psykologisk sundhedKalkun
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRekrutteringFragilt X syndromSerbien
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BioMarin PharmaceuticalRekrutteringDuchennes muskeldystrofiSpanien, Det Forenede Kongerige
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Perha PharmaceuticalsGöteborg University; Proteas BioanalyticsRekruttering
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Ikke rekrutterer endnuTransfusionsafhængig beta-thalassæmiKina
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Meyer Children's Hospital IRCCSRekrutteringEpilepsi | Genetisk sygdomItalien
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Assiut UniversityIkke rekrutterer endnuBehcets sygdom og vaskulær involvering
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Eli Lilly and CompanyRekrutteringAtopisk dermatitisKina, Korea, Republikken
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Keymed Biosciences Co.LtdIkke rekrutterer endnu
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University Hospital, ToulouseIkke rekrutterer endnu
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Lynk Pharmaceuticals Co., LtdRekrutteringAtopisk dermatitisKina
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Pilar AzevedoQueen's University, Belfast; Medical University Innsbruck; Cystic Fibrosis... og andre samarbejdspartnereRekruttering
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Novilla PharmaceuticalsIkke rekrutterer endnuAkut smerte | Gigt Flare | Akut gigt gigtAustralien
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Walter Reed National Military Medical CenterRekrutteringSkjoldbruskkirtlen øjensygdom | Graves Oftalmopati | Graves sygdomForenede Stater
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Radboud University Medical CenterEnzyre B.V.Rekruttering
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Novartis PharmaceuticalsRekrutteringHyperkolesterolæmi | Familiær hyperkolesterolæmiJapan
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Assiut UniversityIkke rekrutterer endnuBehcets sygdom og vaskulær affektion
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Pole Sante Grace de DieuRekruttering
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RekrutteringType II Gauchers sygdomKina
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... og andre samarbejdspartnereRekrutteringPorfyri, akut intermitterendeNorge