- ICH GCP
- Registro degli studi clinici negli Stati Uniti
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Cerca studi clinici per: Orphan Diseases
Totale 376624 risultati
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The Cleveland ClinicTerminato
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M.D. Anderson Cancer CenterCompletatoMalattie linfoproliferative | Leucemia | Neoplasie ematologiche | Leucemia, linfocitica, cronicaStati Uniti
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University of FloridaCompletato
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Cellegy PharmaceuticalsCompletato
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completato
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University of MichiganCompletato
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FDA Office of Orphan Products DevelopmentSciClone PharmaceuticalsCompletato
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Children's Hospital Medical Center, CincinnatiCompletatoOsteopenia | Malattia di GaucherIsraele, Stati Uniti
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FDA Office of Orphan Products DevelopmentCompletato
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Beth Israel Deaconess Medical CenterCompletatoIperglicemia | Resistenza all'insulinaStati Uniti
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University of North CarolinaCompletatoOsteoporosi | Fibrosi cisticaStati Uniti
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United TherapeuticsCompletatoIpertensione polmonareStati Uniti
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Icahn School of Medicine at Mount SinaiCompletatoImmunodeficienza variabile comune
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Seattle Children's HospitalCompletatoDolore | Infante, neonato, malattie
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Massachusetts General HospitalCompletato
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University of PennsylvaniaTerminatoMalattia da carenza di ornitina transcarbamilasi
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OrfagenFDA Office of Orphan Products DevelopmentCompletato
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Swedish Orphan BiovitrumCompletato
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Swedish Orphan BiovitrumCompletatoFibrosi cistica | Insufficienza pancreatica esocrinaOlanda, Polonia
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Swedish Orphan BiovitrumCompletatoMucosite oraleStati Uniti
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Swedish Orphan BiovitrumCompletatoTirosinemia ereditaria, tipo IGermania, Regno Unito, Francia
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Swedish Orphan BiovitrumCompletatoMieloma multiplo | Linfoma non-Hodgkin
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Swedish Orphan BiovitrumCompletatoDolore neuropatico diabeticoRepubblica Ceca, Germania, Sud Africa
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Swedish Orphan BiovitrumAmgenCompletato
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Swedish Orphan BiovitrumAmgenCompletatoLinfoma | Leucemia | Cancro
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Swedish Orphan BiovitrumAmgenCompletatoNeoplasie ematologiche | Malattia del trapianto contro l'ospite
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Pastoral Activities and Service for AIDS Dar-Es-Salaam...King's College London; University of Cape TownSconosciuto
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University of EdinburghMedical Research Council; NHS LothianSconosciuto
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Swedish Orphan BiovitrumCompletato
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Orphan...Completato
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University of TennesseeFDA Office of Orphan Products DevelopmentCompletato
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UCSF Benioff Children's Hospital OaklandDepartment of Health and Human Services; FDA Office of Orphan Products DevelopmentCompletato
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Merit CudkowiczFDA Office of Orphan Products DevelopmentCompletatoMalattia di HuntingtonStati Uniti, Canada
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development e altri collaboratoriTerminatoMucopolisaccaridosi I | Malattie da accumulo lisosomiale | Compressione del midollo spinaleStati Uniti, Finlandia
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University of ArizonaFDA Office of Orphan Products DevelopmentTerminatoCoccidioidomicosiStati Uniti
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ISDINDigna Biotech S.L.CompletatoFibrosi della pelleSpagna, Regno Unito, Germania, Polonia, Ungheria, Italia
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BioprojetCompletatoNarcolessia | Cataplessia | Eccessiva sonnolenza diurnaSvizzera
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ISDINDigna Biotech S.L.CompletatoFibrosi della pelleRegno Unito, Spagna, Italia, Polonia, Germania, Ungheria
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Penn State UniversityRitirato
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BioprojetCompletatoDisordini del sonno | Narcolessia | Cataplessia | Eccessiva sonnolenza diurnaSvizzera
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EmphycorpCellular Sciences, inc.Completato
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompletatoAnemia di FanconiStati Uniti
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GenethonCompletatoDistrofia muscolare dei cingoli tipo 2C | Gamma-sarcoglicanopatiaFrancia
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Medical University of South CarolinaMerck Sharp & Dohme LLC; FDA Office of Orphan Products DevelopmentCompletatoOsteoporosiStati Uniti
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University of FlorenceCompletatoDotto arterioso, brevettoItalia
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AOP Orphan Pharmaceuticals AGCompletatoTrombocitemia essenzialeAustria, Repubblica Ceca, Francia, Germania, Ungheria, Italia, Lituania, Polonia, Singapore, Slovenia
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Institut National de la Santé Et de la Recherche...CompletatoArtrite idiopatica giovanile ad esordio sistemicoFrancia
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AmgenCompletato
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AmgenCompletato