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Clinical Trials on Mukopolysakkaridose in United States
Totalt 161 resultater
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Immusoft of CA, Inc.RekrutteringMukopolysakkaridose IH/S | Mukopolysakkaridose ISForente stater
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbeidspartnereFullførtMukopolysakkaridose type IIIA | Mukopolysakkaridose Type IIIBForente stater
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Masonic Cancer Center, University of MinnesotaRekrutteringMukopolysakkaridose type I | Hematopoetisk celletransplantasjonForente stater
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Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMukopolysakkaridose III-AForente stater
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Abeona Therapeutics, IncAvsluttetMukopolysakkaridose III-BForente stater, Tyskland, Frankrike
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...FullførtMukopolysakkaridose VI | Mukopolysakkaridose IV AForente stater
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Allievex CorporationFullførtMukopolysakkaridose Type IIIB | Mukopolysakkaridose type 3 B | MPS III B | MPS 3 BForente stater, Spania, Tyrkia, Taiwan, Australia, Colombia, Tyskland, Storbritannia
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncPåmelding etter invitasjonMukopolysakkaridose III-AForente stater, Australia, Spania
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VI | Mukopolysakkaridose Type IV | Mukopolysakkaridose type VIIForente stater, Canada
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose type IForente stater
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Abeona Therapeutics, IncAvsluttetMukopolysakkaridose type 3 BForente stater, Tyskland, Frankrike, Spania
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Lundquist Institute for Biomedical Innovation at...FullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VIForente stater
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Alexion PharmaceuticalsFullførtMukopolysakkaridose IIIBForente stater, Storbritannia, Spania
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Masonic Cancer Center, University of MinnesotaAvsluttetHurler syndrom | Mukopolysakkaridose Type IH | MPS IForente stater
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationFullført
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BioMarin PharmaceuticalFullført
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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BioMarin PharmaceuticalFullførtMukopolysakkaridose VIForente stater
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Allievex CorporationFullførtMukopolysakkaridose Type IIIB | MPS III BForente stater, Taiwan, Spania, Colombia, Tyskland, Storbritannia, Tyrkia
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LYSOGENEAktiv, ikke rekrutterendeMukopolysakkaridose type IIIATyskland, Forente stater, Storbritannia, Frankrike, Nederland
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Denali Therapeutics Inc.RekrutteringMukopolysakkaridose type IIIAForente stater
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Masonic Cancer Center, University of MinnesotaFullført
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ShireAvsluttetSanfilippo syndrom | Mukopolysakkaridose (MPS)Forente stater, Storbritannia, Spania, Tyskland, Frankrike, Italia, Nederland
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Emory UniversityBioMarin PharmaceuticalAvsluttetMukopolysakkaridose type IVAForente stater
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Emory UniversityBioMarin PharmaceuticalFullførtMPS - Mukopolysakkaridose | Morquio sykdomForente stater
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JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMukopolysakkaridose IForente stater, Brasil, Japan
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... og andre samarbeidspartnereAktiv, ikke rekrutterendeMukopolysakkaridose type IIIAStorbritannia
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Allievex CorporationAktiv, ikke rekrutterendeMukopolysakkaridose Type IIIB | MPS III BTyskland, Forente stater, Tyrkia, Storbritannia, Colombia, Spania, Taiwan
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Allievex CorporationAktiv, ikke rekrutterendeMukopolysakkaridose Type IIIBForente stater, Tyskland, Spania, Argentina, Australia, Brasil, Colombia, Taiwan, Tyrkia
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JCR Pharmaceuticals Co., Ltd.FullførtMukopolysakkaridose IForente stater, Brasil, Japan
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REGENXBIO Inc.Aktiv, ikke rekrutterendeHurler syndrom | Hurler-Scheie syndrom | Mukopolysakkaridose type I (MPS I)Forente stater, Brasil, Israel
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Alexion PharmaceuticalsFullførtMPS IIIB (Sanfilippo Syndrome)Spania, Nederland, Storbritannia, Forente stater, Brasil
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ShireFullførtMukopolysakkaridose (MPS)Storbritannia, Nederland
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtKrabbe sykdom | Mukopolysakkaridose type II (MPS II) | Mukopolysakkaridose type I (MPS I) | Mukopolysakkaridose type III (MPS III) | Mukopolysakkaridose type VI (MPS VI)Forente stater
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Alexion PharmaceuticalsAvsluttetMukopolysakkaridose III, Type B (MPS IIIB) | Sanfilippo BStorbritannia
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Joyce FoxUltragenyx Pharmaceutical IncIkke lenger tilgjengeligMukopolysakkaridose type 7Forente stater
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Sangamo TherapeuticsAvsluttet
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Nadia Ali, PhDBioMarin PharmaceuticalFullførtMorquio A syndrom | Mukopolysakkaridose IV AForente stater
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National MPS SocietyMediResource Inc.AvsluttetMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridoser | Mukopolysakkaridose VI | Mukopolysakkaridose IVForente stater
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Orchard TherapeuticsRekrutteringMPS-IH (Hurler syndrom)Nederland, Forente stater, Italia, Storbritannia
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BioMarin PharmaceuticalFullførtMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVATaiwan, Forente stater, Italia, Storbritannia
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Lundquist Institute for Biomedical Innovation at...Aktiv, ikke rekrutterendeMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridose VIForente stater
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REGENXBIO Inc.Påmelding etter invitasjon
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Masonic Cancer Center, University of MinnesotaFullførtMukopolysakkaridose I | Hurler syndromForente stater
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Alexion PharmaceuticalsAvsluttetMPS IIIB (Sanfilippo B-syndrom)Spania, Forente stater, Brasil, Storbritannia, Portugal, Italia
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAStorbritannia, Forente stater, Tyskland
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Lundquist Institute for Biomedical Innovation at...AvsluttetMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridose VIForente stater
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ArmaGen, IncFullførtMukopolysakkaridose IForente stater
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Inventiva PharmaFullførtMukopolysakkaridose VIStorbritannia, Frankrike, Tyskland, Portugal