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Søk i kliniske studier for: linked
Totalt 1874 resultater
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GCS Ramsay Santé pour l'Enseignement et la RechercheHar ikke rekruttert ennå
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRekrutteringBecker muskeldystrofiForente stater, Italia
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Tetra Discovery PartnersRekrutteringFragilt X-syndromForente stater
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Institute of Hematology & Blood Diseases HospitalRekruttering
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Poxel SAHar ikke rekruttert ennå
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PfizerRekrutteringHemofili A | Hemofili BHong Kong, Spania, Serbia, Tyrkia, Forente stater, Kina, Mexico, Sør-Afrika, India, Japan, Taiwan, Kroatia, Korea, Republikken, Oman, Italia, Canada, Frankrike
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Capricor Inc.RekrutteringSykdommer i nervesystemet | Genetiske sykdommer, medfødte | Genetiske sykdommer, X-linked | Muskelsykdommer | Nevromuskulære sykdommer | Muskeldystrofier | Muskellidelser, atrofisk | Muskeldystrofi, DuchenneForente stater
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Children's Hospital of Fudan UniversityRekruttering
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Bahçeşehir UniversityHar ikke rekruttert ennåDuchenne muskeldystrofi | Spinal muskelatrofi | Friske individer
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RekrutteringAmyotrofisk lateral sklerose | Kennedy sykdomFrankrike
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Second Hospital of Shanxi Medical UniversityHar ikke rekruttert ennå
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University College, LondonRekrutteringOrnithine Transcarbamylase mangelStorbritannia
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CSL BehringRekruttering
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Fu Xing Hospital, Capital Medical UniversityRekruttering
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Medical University of GdanskRekruttering
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TakedaRekruttering
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Chang Gung Memorial HospitalRekruttering
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Eunice Kennedy Shriver National Institute of Child...RekrutteringBARN syndrom | Smith Lemli Opitz syndrom | Lathosterolosis | DesmosterolosisForente stater
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St. Jude Children's Research HospitalRekrutteringHemofili B | GenterapiForente stater
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Medical University of WarsawRekruttering
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Sohag UniversityHar ikke rekruttert ennåDuchenne muskeldystrofiEgypt
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Amy K. Dickey, M.D.Wake Forest University Health Sciences; University of TexasRekrutteringErytropoetisk protoporfyri | X-bundet protoporfyriForente stater
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's... og andre samarbeidspartnereRekrutteringDuchenne muskeldystrofi | Becker muskeldystrofi | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofiForente stater
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Massachusetts General HospitalBoston Children's HospitalRekruttering
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Postgraduate Institute of Medical Education and...RekrutteringSkrumplever | Ascites HepatiskIndia
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRekrutteringRestless Legs Syndrome | AdrenoleukodystrofiForente stater, Nederland
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Université de SherbrookeRekruttering
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRekrutteringX-koblet hypohidrotisk ektodermal dysplasi (XLHED)Forente stater, Spania, Frankrike, Tyskland, Italia, Storbritannia
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Zynerba Pharmaceuticals, Inc.RekrutteringFragilt X-syndromForente stater, Australia, Storbritannia, Irland
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Duke UniversityRekruttering
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Stephen G. Kaler, MDRekrutteringMenkes sykdom | Occipital Horn SyndromForente stater
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CureDuchenneRekrutteringDuchenne muskeldystrofi | Becker muskeldystrofiForente stater
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Viking Therapeutics, Inc.RekrutteringAdrenomyeloneuropati Form (AMN) av X-koblet adrenoleukodystrofi (X-ALD)Forente stater, Frankrike, Tyskland, Italia, Storbritannia
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Zheng GuoHar ikke rekruttert ennåDiabetisk nefropati type 2
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National Institute of Neurological Disorders and...RekrutteringMotor Neuron sykdom | Spinal og Bulbar muskelatrofi | Kennedys sykdomForente stater
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Shanghai Children's HospitalRekrutteringAlport syndrom, X-LinkedKina
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I.R.A. Istituto Ricerche Applicate S.p.A.Opera CRO, a TIGERMED Group CompanyRekrutteringDysmorfisk lidelse (BDD) | Medfødt Labia Majora Hypotrofi | Postmenopausal Labia Majora HypotrofiItalia, Romania
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Assistance Publique - Hôpitaux de ParisRekrutteringAdrenoleukodystrofi | Adrenomyeloneuropati | Metakromatisk leukodystrofi | Leukoencefalopati med voksendebut med aksonale sfæroider og pigmenterte gliaFrankrike
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... og andre samarbeidspartnereRekrutteringX Linked Myotubular MyopatiStorbritannia, Canada, Forente stater
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Baylor College of MedicineChildren's National Research InstituteRekrutteringOrnithine Transcarbamylase mangel | Urea syklus lidelse | Karbamylfosfatsyntetasemangel | Argininosuccinic aciduria | Hyperargininemi | Citrullinemi 1 | ARGI-mangel | ASL-mangel | ASS mangel | NAGS-mangelForente stater
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbeidspartnereRekruttering
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University of Sao Paulo General HospitalPfizerRekruttering
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Assistance Publique - Hôpitaux de ParisHar ikke rekruttert ennåX-bundet hypofosfatemi (XLH)
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Nova Mentis Life Science CorpFourthWall TestingRekrutteringAutismespektrumforstyrrelse | Fra(X) syndromForente stater
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at... og andre samarbeidspartnereRekruttering
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Beacon TherapeuticsRekrutteringX-Linked Retinitis PigmentosaForente stater
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal... og andre samarbeidspartnereRekruttering
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Albina Nowak, MDSwiss National Science FoundationRekruttering
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University College, LondonRekruttering