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Kliniske forsøg med Angelman syndrom
I alt 76268 resultater
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Ovid Therapeutics Inc.AfsluttetPrimær sygdom eller tilstand, der undersøges: Angelmans syndrom (AS)Forenede Stater, Australien, Tyskland, Israel, Holland
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University of OxfordHoffmann-La Roche; Foundation for Angelman Syndrome Therapeutics UKRekruttering
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Fondazione per la Ricerca Ospedale MaggioreAfsluttet
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Ovid Therapeutics Inc.AfsluttetAngelman syndromForenede Stater, Israel
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Boston Children's HospitalAfsluttetAngelman syndromForenede Stater
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Ultragenyx Pharmaceutical IncIkke rekrutterer endnuAngelman syndromForenede Stater, Australien, Canada, Tyskland, Det Forenede Kongerige, Israel, Frankrig, Spanien
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Puerta de Hierro University HospitalParc Taulí Hospital UniversitariRekruttering
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Foundation for Angelman Syndrome Therapeutics,...Queensland University of TechnologyRekruttering
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The Emmes Company, LLCBoston Children's Hospital; Ionis Pharmaceuticals, Inc.AfsluttetAngelman syndromForenede Stater
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Fudan UniversityAfsluttet
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Hoffmann-La RocheAktiv, ikke rekrutterendeAngelman syndromForenede Stater, Spanien, Holland, Italien
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Ionis Pharmaceuticals, Inc.BiogenAktiv, ikke rekrutterendeAngelman syndromForenede Stater, Israel, Italien, Frankrig, Australien, Det Forenede Kongerige
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University of Colorado, DenverAfsluttet
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Neuren Pharmaceuticals LimitedRekruttering
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University of South FloridaAfsluttet
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Ovid Therapeutics Inc.AfsluttetAngelman syndromForenede Stater, Israel
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Wen-Hann TanBaylor College of Medicine; University of California, San Francisco; Vanderbilt... og andre samarbejdspartnereAfsluttet
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Puerta de Hierro University HospitalAfsluttet
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Boston Children's HospitalBaylor College of Medicine; Vanderbilt University Medical Center; Children... og andre samarbejdspartnereAfsluttet
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Centre Hospitalier Universitaire de LiegeCentre Hospitalier Régional de la Citadelle; SYSNAVRekrutteringAngelman syndromBelgien
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Hoffmann-La RocheRekrutteringAngelman syndromForenede Stater, Australien, Spanien, Italien, Frankrig, Tyskland
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... og andre samarbejdspartnereRekruttering
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Ultragenyx Pharmaceutical IncAktiv, ikke rekrutterendeAngelman syndromForenede Stater, Det Forenede Kongerige, Canada, Australien, Frankrig, Tyskland, Spanien, Israel
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IRCCS Eugenio MedeaRekruttering
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Bennett LavensteinAfsluttet
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IRCCS Eugenio MedeaRekrutteringEpilepsi | Angelman syndrom | Dup15q syndromItalien
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BiogenAfsluttetAngelman syndrom | Kromosom 15q duplikation (dup15q) syndromForenede Stater
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Hoffmann-La RocheAfsluttet
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... og andre samarbejdspartnereAfsluttetSygdomme i nervesystemet | Angelman syndromForenede Stater
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Ovid Therapeutics Inc.Afsluttet
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University of Wisconsin, MadisonUltragenyx Pharmaceutical IncAfsluttetPrader-Willi syndrom | Angelman syndromForenede Stater
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University Hospital, ToulouseRekrutteringEpilepsi | Prader-Willi syndrom | Angelman syndrom | Smith-Magenis syndrom | X Fragilt SyndromFrankrig
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Rush University Medical CenterEmory UniversityTilmelding efter invitationTuberøs sklerose | Fragilt X syndrom | Rett syndrom | Hamartoma syndrom, multipel | Angelman syndrom | Kreatinmangel, X-bundet | Telomerisk 22Q13 Monosomy Syndrome | Kromosom 15Q, delvis sletningForenede Stater
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston Children's Hospital og andre samarbejdspartnereAfsluttetPrader-Willi syndrom | Rett syndrom | Angelman syndrom | SøvnproblemerForenede Stater
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Institut National de la Santé Et de la Recherche...RekrutteringPrader-Willi syndrom | Angelman syndrom | Beckwith-Wiedemanns syndrom | Pseudohypoparathyroidisme | Silver Russell syndrom | Forbigående neonatal diabetes mellitus | Temple syndrom | Kagami-Ogata syndrom | Familiær tidlig pubertetFrankrig
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National Institute of Neurological Disorders and...Baylor College of MedicineAfsluttetPrader-Willi syndrom | DiGeorges syndrom | Williams syndrom | Angelman syndrom | Smith-Magenis syndrom | Kromosomabnormiteter | Shprintzen syndromForenede Stater
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Aston UniversityIkke rekrutterer endnuSyndromer med tørre øjne | Computer Vision Syndrome
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University... og andre samarbejdspartnereAfsluttetPrader-Willi syndrom | DiGeorges syndrom | 22q11 deletionssyndrom | Angelman syndrom | Trisomi 21 | Trisomi 18 | Trisomi 13 | Monosomi X | Kønskromosomafvigelser | 1p36 deletionssyndrom | Cri-du-Chat syndromForenede Stater, Australien, Irland, Spanien, Sverige, Det Forenede Kongerige
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SCRI Development Innovations, LLCNovartis PharmaceuticalsAfsluttetMyelodysplastiske syndromer (MDS)Forenede Stater
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PersImmune, IncUniversity of California, San DiegoUkendt
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TJ Biopharma Co., Ltd.Rekruttering
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RekrutteringMyelodysplastiske syndromer (MDS)Forenede Stater, Israel
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AbbVieCelgene; Genentech, Inc.AfsluttetMyelodysplastiske syndromer (MDS)Forenede Stater, Australien, Tyskland
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AbbVieGenentech, Inc.Aktiv, ikke rekrutterendeMyelodysplastiske syndromer (MDS)Forenede Stater, Australien, Canada, Frankrig, Tyskland, Italien, Det Forenede Kongerige
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The First Affiliated Hospital with Nanjing Medical...UkendtMyelodysplastiske syndromer (MDS)Kina
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RTI InternationalUniversity of North Carolina, Chapel HillTilmelding efter invitationTuberøs sklerose | Downs syndrom | Duchennes muskeldystrofi | Prader-Willi syndrom | Fragilt X syndrom | Rett syndrom | Turners syndrom | Williams syndrom | Angelman syndrom | Kromosom 22q11.2 deletionssyndrom | Klinefelters syndrom | Phelan-McDermid syndrom | Dup15Q syndrom | Smith Magenis syndromForenede Stater
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National Cancer Institute (NCI)AfsluttetTidligere behandlede myelodysplastiske syndromer | Sekundære myelodysplastiske syndromer | de Novo Myelodysplastiske SyndromerForenede Stater
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)AfsluttetTidligere behandlede myelodysplastiske syndromer | Sekundære myelodysplastiske syndromer | de Novo Myelodysplastiske SyndromerForenede Stater
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Benjamin TomlinsonRekrutteringMyelodysplastiske syndromer | MDS/MPN Crossover syndromerForenede Stater
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The University of Texas Health Science Center,...RekrutteringNeuropsykiatriske syndromerForenede Stater