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Clinical Trials on Duchennes muskeldystrofi in United Kingdom
I alt 17794 resultater
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Insmed IncorporatedMuscular Dystrophy AssociationAfsluttet
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RTI InternationalUniversity of North Carolina, Chapel HillTilmelding efter invitationTuberøs sklerose | Downs syndrom | Duchennes muskeldystrofi | Prader-Willi syndrom | Fragilt X syndrom | Rett syndrom | Turners syndrom | Williams syndrom | Angelman syndrom | Kromosom 22q11.2 deletionssyndrom | Klinefelters syndrom | Phelan-McDermid syndrom | Dup15Q syndrom | Smith Magenis syndromForenede Stater
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State University of New York at BuffaloAktiv, ikke rekrutterendeFuchs dystrofiForenede Stater
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Boston Children's HospitalMuscular Dystrophy AssociationRekrutteringCentronukleær myopati | Myotubulær myopati | Nemaline myopati | Central kernesygdom | Medfødt fibertype disproportion | Multiminicore sygdom | Stiv rygsøjle muskeldystrofi | Udefineret medfødt myopatiForenede Stater
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National Heart, Lung, and Blood Institute (NHLBI)AfsluttetKardiomyopati, hypertrofisk | Muskeldystrofi, OculopharyngealForenede Stater
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Acceleron Pharma Inc. (a wholly owned subsidiary...AfsluttetCharcot-Marie-Tooth sygdom | Facioscapulohumeral muskeldystrofiForenede Stater, Spanien, Canada
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Wake Forest University Health SciencesAfsluttetFuchs dystrofi | Cystoid makulært ødemForenede Stater
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Medical College of WisconsinAfsluttetGrå stær | Fuchs' hornhindedystrofiForenede Stater
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University of ManchesterBritish Society for the Study of Vulval DiseaseAfsluttetVulva kræft | Lav Planus | Vulvar Lichen Sclerosus | Selvundersøgelse | Vulval intraepitelial neoplasi | Vulval kræft | Vulval Intraepitelial Neoplasia Med Lichen SclerosusDet Forenede Kongerige
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Harmony Biosciences, LLCAktiv, ikke rekrutterendeMyotonisk dystrofi 1 | Overdreven søvnighed i dagtimerneForenede Stater, Canada
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MeiraGTx UK II LtdAfsluttet
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GlaxoSmithKlineAfsluttet
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FDA Office of Orphan Products DevelopmentAfsluttetMuskeldystrofierForenede Stater
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Edgewise Therapeutics, Inc.AfsluttetMuskeldystrofierForenede Stater
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National Heart, Lung, and Blood Institute (NHLBI)Afsluttet
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University College, LondonRekrutteringIkke-dystrofisk myotoniDet Forenede Kongerige
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Massachusetts Eye and Ear InfirmaryRekrutteringFuchs' endotel hornhindedystrofiForenede Stater
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Wake Forest University Health SciencesAfsluttet
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Cornea Research Foundation of AmericaAfsluttetBulløs keratopati | Fuchs' endotel hornhindedystrofi | Iridocornealt endotelsyndrom | Posterior polymorf dystrofiForenede Stater
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University of Texas Southwestern Medical CenterTrukket tilbageCornea epiteldystrofiForenede Stater
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Rekruttering
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King's College LondonUniversity College, LondonAfsluttetRecessiv dystrofisk epidermolysis BullosaDet Forenede Kongerige
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King's College LondonUkendtRecessiv dystrofisk epidermolysis BullosaDet Forenede Kongerige
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Edgewise Therapeutics, Inc.AfsluttetSygdomme i nervesystemet | Genetiske sygdomme, medfødte | Muskuloskeletale sygdomme | Muskelsygdomme | Neuromuskulære sygdomme | Muskeldystrofier | Muskellidelser, atrofisk | Sund frivilligForenede Stater
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ML Bio Solutions, Inc.Aktiv, ikke rekrutterende
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Food and Drug Administration (FDA)National Eye Institute (NEI)RekrutteringAldersrelateret makuladegeneration | Nethindedegeneration | Retinitis Pigmentosa | Usher syndromer | Kegledystrofi | Stangdystrofi | Keglestangsdystrofi | Hydroxychloroquin retinopati | Sen-debuterende retinal degeneration | StangkegledystrofiForenede Stater
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Duke UniversityAfsluttet
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Kowa Research Institute, Inc.RekrutteringFuchs endotel hornhindedystrofiForenede Stater, Tyskland, Spanien, Canada, Det Forenede Kongerige, Danmark
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Children's National Research InstituteAktiv, ikke rekrutterendeGenetiske sygdomme, medfødte | Muskuloskeletale sygdomme | Muskeldystrofier | HjertefibroseForenede Stater
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Massachusetts Eye and Ear InfirmaryRekrutteringFuchs endotel hornhindedystrofiForenede Stater
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Price Vision GroupAfsluttetBulløs keratopati | Fuchs' DystrofiForenede Stater, Tyskland
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Kowa Research Institute, Inc.RekrutteringFuchs endotel hornhindedystrofiForenede Stater, Det Forenede Kongerige, Spanien, Tyskland, Canada, Danmark
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The Cleveland ClinicNational Eye Institute (NEI)AfsluttetNethindeløsning | Epiretinal membran | Fuchs endoteldystrofi | Macula hulForenede Stater
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health Clinical Center (CC); National Institute... og andre samarbejdspartnereAktiv, ikke rekrutterendeGenetisk lidelseForenede Stater
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NYU Langone HealthNational Eye Institute (NEI)Aktiv, ikke rekrutterendeFuchs dystrofi | Hornhindelidelser | Tidligere operationForenede Stater
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Cornea Research Foundation of AmericaAfsluttetHornhindeødem | Fuchs' DystrofiForenede Stater
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Kowa Research Institute, Inc.AfsluttetFuchs' endotel hornhindedystrofiForenede Stater, Australien, Tyskland, Spanien, Danmark
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Trefoil Therapeutics, Inc.AfsluttetEndotel dysfunktion | Endoteldystrofi i hornhinden | Pseudofakisk bulløs keratopati | Fuchs endotel hornhindedystrofiForenede Stater
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Institut National de la Santé Et de la Recherche...UkendtRecessiv dystrofisk epidermolysis BullosaFrankrig, Det Forenede Kongerige
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaAfsluttetAchromatopsiDet Forenede Kongerige, Forenede Stater
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MeiraGTx UK II LtdJanssen Research & Development, LLCAfsluttet
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Retrotope, Inc.AfsluttetInfantil neuroaksonal dystrofi | INADForenede Stater
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaAfsluttet
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EmmecellAktiv, ikke rekrutterendeEndotel dysfunktion | Hornhindeødem | Fuchs dystrofi | Endoteldystrofi i hornhinden | Bulløs keratopati | Pseudofakisk bulløs keratopati | Hornhindeendotel dysfunktion | Fuchs endotel hornhindedystrofi | Moderat hornhindeendoteldekompensationForenede Stater
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Retrotope, Inc.Aktiv, ikke rekrutterendeInfantil neuroaksonal dystrofiForenede Stater
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Duke UniversityAfsluttet
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PYC TherapeuticsRekrutteringNethindedystrofi | PRPF31 Mutationsassocieret retinal dystrofi | RP11Forenede Stater
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University Hospital, Basel, SwitzerlandInstitute of Molecular and Clinical Ophthalmology BaselRekrutteringNethindedystrofierForenede Stater, Schweiz, Kina, Tyskland, Ungarn, Italien, Det Forenede Kongerige
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National Institute of Neurological Disorders and...RekrutteringMuskeldystrofi | Perifer neuropati | Normal fysiologi | Motorisk neuronsygdomForenede Stater
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National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye... og andre samarbejdspartnereAfsluttetHornhindesygdom | Fuchs dystrofi | Pseudofakisk hornhindeødemForenede Stater