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Kliniske forsøg med Emery-Dreifuss muskeldystrofi
I alt 714 resultater
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Fulcrum TherapeuticsAktiv, ikke rekrutterendeFacioscapulohumeral muskeldystrofi 1Holland
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Peking Union Medical College HospitalIkke rekrutterer endnuDuchenne muskeldystrofi (DMD)
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CureDuchenneRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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University of FloridaU.S. Army Medical Research and Development CommandRekrutteringDuchenne muskeldystrofi (DMD)Forenede Stater
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The Duchenne RegistryParent Project Muscular DystrophyRekruttering
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Ondokuz Mayıs UniversityAfsluttetDuchenne muskeldystrofi (DMD)Kalkun
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Sarepta Therapeutics, Inc.AfsluttetSikkerhedsundersøgelse af Eteplirsen til behandling af Duchennes muskeldystrofi i det tidlige stadieDuchenne muskeldystrofi (DMD)Forenede Stater
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Parent Project, ItalyAfsluttetDuchenne muskeldystrofi (DMD)Italien
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University Hospital, MontpellierUkendtMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofiFrankrig
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GenethonInstitute of MyologyAfsluttetDuchenne muskeldystrofi (DMD)Frankrig
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University Hospital, Basel, SwitzerlandAfsluttet
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteTrukket tilbageDuchenne muskeldystrofi (DMD)Forenede Stater
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Medical University of GdanskRekrutteringDuchenne muskeldystrofi (DMD)Polen
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ItalfarmacoAfsluttetDuchenne muskeldystrofi (DMD)Italien
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Santhera PharmaceuticalsAfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater, Spanien, Holland, Sverige, Tyskland, Frankrig, Belgien, Det Forenede Kongerige, Italien, Irland, Schweiz, Østrig, Bulgarien, Ungarn, Israel
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Sarepta Therapeutics, Inc.AfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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General Hospital of Chinese Armed Police ForcesUkendtDuchenne muskeldystrofi (DMD)Kina
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Grete Andersen, MDAfsluttetFSHD - Facioscapulohumeral muskeldystrofiDanmark
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RSPR Pharma ABAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiSverige
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National Institute of Neurological Disorders and...AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterende
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityAfsluttetMuskeldystrofier | Lembælte muskeldystrofiForenede Stater, Danmark
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaIkke rekrutterer endnuOptrævling af metabolisk involvering i facioscapulohumeral dystrofi gennem metabolomics (METIN-FSHD)Facioscapulohumeral muskeldystrofi
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Centre Hospitalier Universitaire de NiceAfsluttetMuskeldystrofierFrankrig
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University of RochesterAfsluttetFacioscapulohumeral muskeldystrofiForenede Stater
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University of Kansas Medical CenterNational Institutes of Health (NIH)AfsluttetFacioscapulohumeral muskeldystrofiForenede Stater
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofi | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofiForenede Stater
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Assistance Publique - Hôpitaux de ParisIkke rekrutterer endnu
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University of MonsRekrutteringFacioscapulohumeral muskeldystrofiBelgien
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Centre Hospitalier Universitaire de NiceRekrutteringFacioscapulohumeral muskeldystrofiFrankrig
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Newcastle UniversityRekrutteringFacioscapulohumeral muskeldystrofiDet Forenede Kongerige
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Hillel Yaffe Medical CenterRekruttering
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Aktiv, ikke rekrutterendeFacioscapulohumeral muskeldystrofiForenede Stater
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Robert Jones and Agnes Hunt Orthopaedic and District...AfsluttetFacioscapulohumeral muskeldystrofi
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationAfsluttetFacioscapulohumeral muskeldystrofiForenede Stater, Australien
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Rigshospitalet, DenmarkUkendtOculopharyngeal muskeldystrofiDanmark
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Centre Hospitalier Universitaire de NiceAfsluttetFacioscapulohumeral muskeldystrofiFrankrig
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Asklepios Biopharmaceutical, Inc.RekrutteringMuskeldystrofi | Lembælte muskeldystrofi | LGMD2I | LGMD | Limb-Girdle Muskeldystrofi Type 2 | LGMD2 | FKRP | FKRP-mutation | Fukutin-relateret proteinForenede Stater
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PTC TherapeuticsAfsluttetNonsene mutation Duchenne muskeldystrofiForenede Stater
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Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Rigshospitalet, DenmarkUkendtFacioscapulohumeral muskeldystrofi 1aDanmark
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Cure CMDCongenital Muscle Disease International RegistrTrukket tilbageLAMA2-MD (Merosin Deficient Congenital Muskeldystrofi, MDC1A)Forenede Stater
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Ning Wang, MD., PhD.Rekruttering
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Centre Hospitalier Universitaire de NiceRekrutteringFacioscapulohumeral muskeldystrofi type 2Frankrig, Italien, Spanien
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Cairo UniversityAfsluttetMuskeldystrofi, Duchenne TypeEgypten
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Hospital RudolfstiftungOesterreichische MuskelforschungAfsluttetBærer af Duchenne muskeldystrofiØstrig
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Fondazione Policlinico Universitario Agostino Gemelli...Rekruttering
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Bioblast Pharma Ltd.Afsluttet
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Rigshospitalet, DenmarkIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiDanmark
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Dyne TherapeuticsRekrutteringDuchenne muskeldystrofi (DMD)Forenede Stater, Belgien, Canada, Det Forenede Kongerige, Australien, Spanien, Italien