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Kliniske forsøg med Facioscapulohumeral muskeldystrofi
I alt 50919 resultater
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Carl Zeiss Meditec, Inc.DataMed Devices Inc.AfsluttetTør AMD Med Macular DrusenForenede Stater
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ML Bio Solutions, Inc.RekrutteringLimb-Girdle Muskeldystrofi Type 2I (LGMD2I)Forenede Stater, Holland, Det Forenede Kongerige, Danmark, Australien, Italien, Norge
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Linda Pax LowesRekrutteringLimb-Girdle Muskeldystrofi Type 2A | Limb-Girdle Muskeldystrofi, Type 2EForenede Stater
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CureDuchenneRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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The Duchenne RegistryParent Project Muscular DystrophyRekruttering
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University Hospital, MontpellierUkendtMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofiFrankrig
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Rigshospitalet, DenmarkIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiDanmark
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Nationwide Children's HospitalParent Project Muscular DystrophyRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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University of FloridaChildren's Hospital of Philadelphia; National Institute of Arthritis and... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Catholic University, ItalyUkendtDuchennes muskeldystrofi | Beckers muskeldystrofiItalien
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Chaitanya Hospital, PuneUkendtMuskeldystrofi | Duchenne muskeldystrofi,Indien
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Medical University of GdanskRekrutteringDuchenne muskeldystrofi (DMD)Polen
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ItalfarmacoAfsluttetDuchenne muskeldystrofi (DMD)Italien
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Cairo UniversityAfsluttetMuskeldystrofi, Duchenne TypeEgypten
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Santhera PharmaceuticalsAfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater, Spanien, Holland, Sverige, Tyskland, Frankrig, Belgien, Det Forenede Kongerige, Italien, Irland, Schweiz, Østrig, Bulgarien, Ungarn, Israel
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Sarepta Therapeutics, Inc.AfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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Hospital RudolfstiftungOesterreichische MuskelforschungAfsluttetBærer af Duchenne muskeldystrofiØstrig
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General Hospital of Chinese Armed Police ForcesUkendtDuchenne muskeldystrofi (DMD)Kina
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Newcastle-upon-Tyne Hospitals NHS TrustRekrutteringBethlem myopati | Ullrich medfødt muskeldystrofi 1, Digenic, Col6A1/Col6A2 | Ullrich medfødt muskeldystrofi 1, autosomal recessiv | Ullrich medfødt muskeldystrofi 1, autosomal dominant | Bethlem Myopati 1, Autosomal Recessiv | UCMD | BTHLM1Det Forenede Kongerige
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Avidity Biosciences, Inc.RekrutteringMyotonisk dystrofi | Myotoniske lidelser | Myotoni | Myotonisk dystrofi type 1 (DM1) | Myotonisk dystrofi 1 | Myotonisk muskeldystrofi | DM1 | Dystrofi Myotonisk | Steinerts sygdom | SteinertForenede Stater
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Peking Union Medical College HospitalIkke rekrutterer endnuDuchenne muskeldystrofi (DMD)
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University of FloridaU.S. Army Medical Research and Development CommandRekrutteringDuchenne muskeldystrofi (DMD)Forenede Stater
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PTC TherapeuticsAfsluttetNonsene mutation Duchenne muskeldystrofiForenede Stater
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Ondokuz Mayıs UniversityAfsluttetDuchenne muskeldystrofi (DMD)Kalkun
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Sarepta Therapeutics, Inc.AfsluttetSikkerhedsundersøgelse af Eteplirsen til behandling af Duchennes muskeldystrofi i det tidlige stadieDuchenne muskeldystrofi (DMD)Forenede Stater
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Parent Project, ItalyAfsluttetDuchenne muskeldystrofi (DMD)Italien
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GenethonInstitute of MyologyAfsluttetDuchenne muskeldystrofi (DMD)Frankrig
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University Hospital, Basel, SwitzerlandAfsluttet
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteTrukket tilbageDuchenne muskeldystrofi (DMD)Forenede Stater
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Neurotech PharmaceuticalsThe Lowy Medical Research Institute LimitedAfsluttetMacular Telangiectasia Type 2Forenede Stater, Australien
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Neurotech PharmaceuticalsThe Emmes Company, LLC; The Lowy Medical Research Institute LimitedAfsluttetMacular Telangiectasia Type 2Forenede Stater, Australien
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Dyne TherapeuticsRekrutteringDuchenne muskeldystrofi (DMD)Forenede Stater, Belgien, Canada, Det Forenede Kongerige, Australien, Spanien, Italien
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiDanmark, Frankrig, Italien, Holland, Spanien, Det Forenede Kongerige
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Astellas Pharma IncAfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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Nippon Shinyaku Co., Ltd.Aktiv, ikke rekrutterende
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PfizerAfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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Sarepta Therapeutics, Inc.AfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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University Children's Hospital, ZurichUkendtDuchenne / Becker MuskeldystrofiSchweiz
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University Hospital, Basel, SwitzerlandAfsluttet
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Santhera PharmaceuticalsAfsluttetDuchenne muskeldystrofi (DMD)Belgien
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Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University of Iowa og andre samarbejdspartnereRekrutteringLembælte muskeldystrofi | Calpain-3-mangel ekstremitetsbælte Muskeldystrofi Type 2A | Lembælte muskeldystrofi Type R1 | LGMD2AForenede Stater, Holland, Det Forenede Kongerige
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Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Cure CMDCongenital Muscle Disease International RegistrTrukket tilbageLAMA2-MD (Merosin Deficient Congenital Muskeldystrofi, MDC1A)Forenede Stater
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ItalfarmacoAfsluttetDuchenne og Beckers muskeldystrofi | Polycytæmi VeraCanada
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University of MalagaIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiSpanien
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases...Ikke rekrutterer endnuMuskeldystrofi | Dyrke motion | Duchennes muskeldystrofi | Vasodilatation | DMD | Muskeldystrofi hos børn | Duchennes sygdom
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Gaziosmanpasa Research and Education HospitalAfsluttetDuchenne eller Becker muskeldystrofiKalkun
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The Lowy Medical Research Institute LimitedAktiv, ikke rekrutterendeMacular Telangiectasia Type 2Forenede Stater, Det Forenede Kongerige
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Neurotech PharmaceuticalsAfsluttetMacular Telangiectasia Type 2Forenede Stater, Australien, Tyskland
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Neurotech PharmaceuticalsAfsluttetMacular Telangiectasia Type 2Forenede Stater, Det Forenede Kongerige, Australien, Frankrig