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Kliniske forsøg med Ichthyosis, X-Linked
I alt 3692 resultater
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Kyowa Kirin Co., Ltd.Aktiv, ikke rekrutterende
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Astellas Gene TherapiesAktiv, ikke rekrutterendeX-forbundet myotubulær myopatiForenede Stater, Canada, Frankrig, Tyskland
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Masonic Cancer Center, University of MinnesotaRekruttering
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Minoryx Therapeutics, S.L.RekrutteringCerebral adrenoleukodystrofi (cALD)Forenede Stater, Brasilien, Argentina
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Poxel SAIkke rekrutterer endnu
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD)Forenede Stater, Frankrig, Tyskland, Italien, Holland, Det Forenede Kongerige
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bluebird bioAfsluttetCerebral adrenoleukodystrofi (CALD)Forenede Stater, Tyskland, Argentina, Australien, Frankrig, Det Forenede Kongerige
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ShireAfsluttetHunters syndromSpanien, Forenede Stater, Canada, Det Forenede Kongerige, Frankrig, Australien, Mexico
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Masonic Cancer Center, University of MinnesotaTrukket tilbageCerebral adrenoleukodystrofi
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Northwestern UniversityTrukket tilbageBØRN syndrom | Smith Lemli Opitz syndrom | Syndrome ikthyoser | Conradi syndrom
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University of California, DavisNational Institute of Mental Health (NIMH)AfsluttetFragil X-præmutationForenede Stater
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRekrutteringCerebral adrenoleukodystrofi (CALD)Forenede Stater
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Poxel SAIkke rekrutterer endnu
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Masonic Cancer Center, University of MinnesotaRekrutteringCerebral adrenoleukodystrofi | Adrenoleukodystrofi | ALD (adrenoleukodystrofi)Forenede Stater
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige, Canada
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Onofre, Aurora Pujol, M.D.Afsluttet
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaAfsluttet
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St. James's Hospital, IrelandUniversity of Dublin, Trinity College; Science Foundation IrelandRekrutteringAtopisk dermatitis | Psoriasis Vulgaris | Ichthyosis VulgarisIrland
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University Hospital ErlangenPervormance GmbHAfsluttetX-forbundet hypohidrotisk ektodermal dysplasi | Træningsinduceret stigning i kropstemperaturenTyskland
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National Human Genome Research Institute (NHGRI)RekrutteringEksem | Atopisk dermatitis | Ichthyosis VulgarisForenede Stater
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Hospices Civils de LyonIkke rekrutterer endnuX-Linked Hypophosphatemic Rickets
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InnoVec Biotherapeutics Inc.Peking Union Medical College HospitalRekrutteringØjensygdomme | Nethindedegeneration | Nethindesygdom | RetinoschisisKina
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National Institute of Allergy and Infectious Diseases...RekrutteringGranulom | Granulomatøs sygdom, kronisk | Leukocyt sygdom | Genetisk sygdom, X-forbundet | Genetisk sygdom, medfødtForenede Stater
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BiogenAfsluttetChoroideræmiForenede Stater, Tyskland, Frankrig
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Duke UniversityFoundation Fighting BlindnessTrukket tilbageChoroideræmiForenede Stater
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... og andre samarbejdspartnereAfsluttet
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University of AlbertaAfsluttet
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Sangamo TherapeuticsAktiv, ikke rekrutterendeHæmofili B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIForenede Stater
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... og andre samarbejdspartnereRekrutteringALS | Kennedys sygdom | MND (motorisk neuronsygdom) | PLS | PMA - Progressiv muskelatrofi | PBP - Progressiv Bulbar PareseForenede Stater, Italien
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIForenede Stater, Canada
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4D Molecular TherapeuticsAktiv, ikke rekrutterendeChoroideræmiForenede Stater
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4D Molecular TherapeuticsAfsluttet
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustAfsluttet
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STZ eyetrialUniversity Hospital TuebingenAfsluttet
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRekrutteringRestless Legs Syndrome | AdrenoleukodystrofiForenede Stater, Holland
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases...RekrutteringX-bundet hypofosfatæmi | Hypofosfatæmisk rakitt | Hypophosphatemisk rakitt, X-Linked DominantForenede Stater
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Minoryx Therapeutics, S.L.Aktiv, ikke rekrutterendeCerebral adrenoleukodystrofiSpanien, Tyskland, Frankrig, Argentina
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Ramsay Générale de SantéDr Béatrice DaoudUkendtTin X Ray | LungeparenkymFrankrig
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BiogenAfsluttetChoroideræmiForenede Stater, Finland, Frankrig, Danmark, Holland, Tyskland, Det Forenede Kongerige, Canada
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BiogenAfsluttetChoroideræmiForenede Stater
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRekrutteringPyruvat dehydrogenase kompleks mangel | Pyruvat dehydrogenase E1 alfa-mangel | Pyruvat Dehydrogenase E1-Beta mangel | Pyruvat dehydrogenase E2 mangel | Pyruvat Dehydrogenase Phosphatase mangelDet Forenede Kongerige
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National Institute of Allergy and Infectious Diseases...RekrutteringKronisk granulomatøs sygdom (CGD) | X-forbundet kronisk granulomatøs sygdomForenede Stater
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Soma JyonouchiBaylor College of MedicineAfsluttetX-bundet trombocytopeni | Wiskott-Aldrich syndrom (WAS)Forenede Stater
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The Catholic University of KoreaAfsluttetMetabolisk syndrom X | Metabolisk kardiovaskulært syndrom | Insulinresistenssyndrom X | Dysmetabolisk syndrom XKorea, Republikken
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NightstaRx Ltd, a Biogen CompanyAfsluttetChoroideræmiFinland, Forenede Stater, Canada, Danmark, Holland, Tyskland, Det Forenede Kongerige, Brasilien, Frankrig
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Bio Products LaboratoryAfsluttetAlmindelig variabel immundefekt | Primære immundefektsygdomme | X-bundet agammaglobulinæmi | Hyperimmunoglobulin M syndromForenede Stater
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Spark TherapeuticsAfsluttetChoroideræmi | CHM (choroideremia) genmutationerForenede Stater
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Shenzhen Second People's HospitalGuangzhou Women and Children's Medical Center; Shenzhen UniversityRekrutteringAdrenoleukodystrofi | Metakromatisk leukodystrofiKina
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Gillette Children's Specialty HealthcareAfsluttetCerebral Parese | Muskeldystrofi | Osteopeni | Rett syndrom | Spinal muskelatrofi | Spina BifidaForenede Stater