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Kliniske forsøg med Mucopolysaccharidosis type 7
I alt 57316 resultater
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis Type II (MPS II)Forenede Stater, Canada
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GOIZETBioMarin PharmaceuticalRekruttering
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationAfsluttet
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Genzyme, a Sanofi CompanyAfsluttet
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JCR Pharmaceuticals Co., Ltd.AfsluttetMucopolysaccharidosis IForenede Stater, Brasilien, Japan
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LYSOGENEAfsluttetMucopolysaccharidosis IIIATyskland, Brasilien, Det Forenede Kongerige, Frankrig, Holland
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Inventiva PharmaAfsluttetMucopolysaccharidosis VIDet Forenede Kongerige, Frankrig, Tyskland, Portugal
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationAktiv, ikke rekrutterendeMucopolysaccharidoser | Mucopolysaccharidosis VI | Morquio A syndrom | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio syndrom A | Morquio syndromBrasilien
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BioMarin PharmaceuticalGodkendt til markedsføringMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Puerto Rico
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ArmaGen, IncAfsluttetMucopolysaccharidosis IBrasilien
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater
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Emory UniversityBioMarin PharmaceuticalAfsluttetGraviditet med Morquio Syndrom - Hvad er patienternes perspektiver og har ERT ændret dem? (MorqPreg)MPS - Mucopolysaccharidosis | Morquios sygdomForenede Stater
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudIkke rekrutterer endnuSanfilippo syndrom type CForenede Stater, Frankrig
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IV A | Mucopolysaccharidosis IVADet Forenede Kongerige
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REGENXBIO Inc.Tilmelding efter invitation
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ArmaGen, IncAfsluttetMucopolysaccharidosis IForenede Stater
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ArmaGen, IncAfsluttet
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis IBrasilien, Den Russiske Føderation
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ShireAfsluttetSanfilippo syndrom type BForenede Stater, Det Forenede Kongerige, Tyskland
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Det Forenede Kongerige, Canada, Tyskland
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JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMucopolysaccharidosis IIJapan
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JCR Pharmaceuticals Co., Ltd.AfsluttetMucopolysaccharidosis IIJapan
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVATaiwan, Forenede Stater, Italien, Det Forenede Kongerige
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Sangamo TherapeuticsAfsluttet
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National MPS SocietyMediResource Inc.AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoser | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVForenede Stater
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ArmaGen, IncAfsluttetMucopolysaccharidosis IBrasilien
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AO GENERIUMRekrutteringMetaboliske sygdomme | Mucopolysaccharidosis Type IIDen Russiske Føderation
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Denali Therapeutics Inc.Tilmelding efter invitationMucopolysaccharidosis IIForenede Stater, Canada, Belgien, Tjekkiet, Holland
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JCR Pharmaceuticals Co., Ltd.Tilmelding efter invitation
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REGENXBIO Inc.AfsluttetMucopolysaccharidosis IIBrasilien, Forenede Stater, Det Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVADet Forenede Kongerige, Forenede Stater, Tyskland
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis IIForenede Stater, Spanien, Det Forenede Kongerige, Tjekkiet, Frankrig, Canada, Italien, Belgien, Holland, Tyskland, Argentina, Sverige, Kalkun, Colombia, Brasilien
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AO GENERIUMAfsluttetMetaboliske sygdomme | Mucopolysaccharidosis Type IIDen Russiske Føderation
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Lundquist Institute for Biomedical Innovation at...Aktiv, ikke rekrutterendeMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IV AForenede Stater, Canada, Frankrig, Taiwan, Argentina, Colombia, Spanien, Kalkun, Japan, Saudi Arabien, Holland, Danmark, Korea, Republikken, Brasilien, Det Forenede Kongerige, Tyskland, Norge, Portugal, Italien, Qatar
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMorquio A syndrom | Mucopolysaccharidosis IV AForenede Stater
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Ultragenyx Pharmaceutical IncLedigSly Syndrom | Mucopolysaccharidosis VII | MPS VII
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Institut National de la Santé Et de la Recherche...RekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multipel Sulfatase mangel sygdom | Mucopolysaccharidosis IXFrankrig
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncAfsluttetGenoverførselsundersøgelse af ABO-102 hos patienter med mellem- og avanceret fase af MPS IIIA-sygdomMucopolysaccharidosis III | Sanfilippo syndrom | MPS IIIA | Sanfilippo AForenede Stater, Spanien, Australien
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis I | Hurler syndromForenede Stater
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTrukket tilbageMucopolysaccharidosis IV | Morquio A DiseaseDet Forenede Kongerige
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetHurler syndrom | Sanfilippo syndrom type A | Sanfilippo syndrom type BForenede Stater
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Poitiers University HospitalRekrutteringMR | PTX | HJERNE | 7 TESLAFrankrig
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Lundquist Institute for Biomedical Innovation at...Ikke rekrutterer endnuMucopolysaccharidosis III | Sanfilippo syndromForenede Stater
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncAktiv, ikke rekrutterendeMucopolysaccharidosis III | Sanfilippo syndrom | MPS IIIA | Sanfilippo AForenede Stater, Australien, Spanien
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater