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Kliniske forsøg med Mucopolysaccharidosis Type VII
I alt 58964 resultater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVATaiwan, Forenede Stater, Italien, Det Forenede Kongerige
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Tilmelding efter invitationSanfilippo syndrom type DForenede Stater
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Swedish Orphan BiovitrumAfsluttetSanfilippo syndrom type A (MPS IIIA)Forenede Stater, Kalkun
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Swedish Orphan BiovitrumAfsluttetSanfilippo syndrom type A (MPS IIIA)Forenede Stater, Tyskland, Kalkun
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ShireAfsluttetSanfilippo syndromHolland, Det Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Det Forenede Kongerige, Canada, Tyskland
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ArmaGen, IncAfsluttetMucopolysaccharidosis IBrasilien
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Sangamo TherapeuticsAfsluttetMucopolysaccharidosis II | MPS IIForenede Stater
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ShireAfsluttetHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater, Argentina, Mexico, Spanien, Det Forenede Kongerige
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ShireAfsluttetSanfilippo syndrom type AForenede Stater
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Sangamo TherapeuticsAfsluttet
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRekrutteringSanfilippo syndrom | MPS3Forenede Stater
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMorquio A syndrom | Mucopolysaccharidosis IV AForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVADet Forenede Kongerige, Forenede Stater, Tyskland
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalAfsluttetMPS IVA | Maroteaux Lamy syndrom | MPS VI | Morquio syndrom AForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IV AForenede Stater, Canada, Frankrig, Taiwan, Argentina, Colombia, Spanien, Kalkun, Japan, Saudi Arabien, Holland, Danmark, Korea, Republikken, Brasilien, Det Forenede Kongerige, Tyskland, Norge, Portugal, Italien, Qatar
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TakedaTakeda Development Center Americas, Inc.RekrutteringHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis I | Hurler syndromForenede Stater
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTrukket tilbageMucopolysaccharidosis IV | Morquio A DiseaseDet Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetEn klinisk vurderingsundersøgelse af forsøgspersoner med mucopolysaccharidosis IVA (Morquio syndrom)Morquio A syndrom | MPS IV A | Mucopolysaccharidosis IVAFrankrig, Det Forenede Kongerige, Taiwan, Forenede Stater, Argentina, Holland, Canada, Brasilien, Tyskland, Italien
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Duke UniversityRekruttering
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University of California, San FranciscoRekrutteringMPS IVA | MPS VIForenede Stater
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CENTOGENE GmbH RostockTrukket tilbageUdviklingsforsinkelse | Splenomegali | Hepatomegali | SkeletabnormiteterTyskland, Indien, Sri Lanka, Egypten
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Masonic Cancer Center, University of MinnesotaAfsluttetMucopolysaccharidosis | Hurler syndrom | Sphingolipidoser | Peroxisomale lidelser | Krabbes sygdom | Adrenoleukodystrofi (ALD) | Hunters syndrom | Sly Syndrom | Fucosidosis | Aspartylglucosaminuri | Alpha Mannosidose | Metakromatisk leukodystrofi (MLD) | Maroteaux-Lamy syndromForenede Stater
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Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo B syndrom)Det Forenede Kongerige
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological... og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Kognitiv tilbagegangForenede Stater
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Denali Therapeutics Inc.AfsluttetMucopolysaccharidosis IIDet Forenede Kongerige, Forenede Stater, Holland
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JCR Pharmaceuticals Co., Ltd.AfsluttetMucopolysaccharidosis IIBrasilien
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REGENXBIO Inc.Trukket tilbage
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Green Cross CorporationAfsluttetMucopolysaccharidosis IIKorea, Republikken
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaAfsluttet
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCAfsluttetMucopolysaccharidosis I | Scheie syndrom | Hurler syndrom | Hurler-Scheie syndromHolland, Frankrig, Tyskland, Det Forenede Kongerige
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IV | Morquios sygdomForenede Stater
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Samsung Medical CenterIkke rekrutterer endnuSanfilippo syndrom A
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ShireAfsluttetSanfilippo syndromForenede Stater, Spanien, Det Forenede Kongerige, Argentina, Frankrig, Tyskland, Italien, Holland
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesAfsluttet
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital... og andre samarbejdspartnereRekruttering
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GC Biopharma CorpRekrutteringMucopolysaccharidosis II | Hunters syndromKorea, Republikken
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Homology Medicines, IncTrukket tilbageMucopolysaccharidosis IIForenede Stater, Canada
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JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMucopolysaccharidosis IIBrasilien
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ShireAfsluttetMucopolysaccharidosis IIForenede Stater, Det Forenede Kongerige, Brasilien, Tyskland
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GlaxoSmithKlineAfsluttetMucopolysaccharidosis IIJapan
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Green Cross CorporationUkendtMucopolysaccharidosis II
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IVA (Morquio A syndrom)Australien
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JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis IIForenede Stater, Tyskland, Spanien, Frankrig, Brasilien, Argentina, Kalkun, Det Forenede Kongerige, Polen, Italien
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Denali Therapeutics Inc.Aktiv, ikke rekrutterendeMucopolysaccharidosis IIForenede Stater, Holland, Canada, Det Forenede Kongerige
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JCR Pharmaceuticals Co., Ltd.Afsluttet
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REGENXBIO Inc.Tilmelding efter invitation
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ArmaGen, IncAfsluttetMucopolysaccharidosis IIForenede Stater, Tyskland, Filippinerne
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development og andre samarbejdspartnereAfsluttetMucopolysaccharidosis I | Lysosomale opbevaringssygdomme | RygmarvskompressionForenede Stater, Finland