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Clinical Trials on Stargardt-lignende makuladystrofi in United Kingdom
I alt 503 resultater
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater
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Rare Disease Research, LLCSarepta Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Cedars-Sinai Medical CenterAfsluttet
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater
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Eli Lilly and CompanyAfsluttetMuskeldystrofi, DuchenneTyskland, Forenede Stater, Spanien, Belgien, Frankrig, Italien, Taiwan, Holland, Kalkun, Korea, Republikken, Argentina, Canada, Japan, Puerto Rico, Den Russiske Føderation, Det Forenede Kongerige
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRekrutteringBeckers muskeldystrofiForenede Stater, Italien
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Cooperative International Neuromuscular Research...Afsluttet
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Sarepta Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National...AfsluttetDuchennes muskeldystrofiForenede Stater
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University of MichiganMidwest Eye BanksAfsluttetStargardts sygdomForenede Stater
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Aktiv, ikke rekrutterendeFacioscapulohumeral muskeldystrofiForenede Stater
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesIkke længere tilgængeligMedfødt muskeldystrofi på grund af Lamin A/C-mutationForenede Stater
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Solid Biosciences Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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Solid Biosciences Inc.Aktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.AfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of... og andre samarbejdspartnereAfsluttetKardiomyopati | Duchenne muskeldystrofi (DMD)Forenede Stater
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital... og andre samarbejdspartnereRekruttering
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterende
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Benitec Biopharma, Inc.RekrutteringOculopharyngeal muskeldystrofiForenede Stater
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University of FloridaAfsluttet
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsAfsluttetBeckers muskeldystrofi | Sund frivilligForenede Stater
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PfizerRekrutteringDuchennes muskeldystrofiForenede Stater
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Akashi TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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Epirium Bio Inc.AfsluttetBeckers muskeldystrofiForenede Stater
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Afsluttet
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Avidity Biosciences, Inc.Tilmelding efter invitationDuchennes muskeldystrofi | DMD | Exon 44 | DuchenneForenede Stater
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Children's Hospital Medical Center, CincinnatiAktiv, ikke rekrutterendeMuskuloskeletale abnormiteter | Duchennes muskeldystrofiForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetMeddelelse | Genetisk sygdomForenede Stater
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Capricor Inc.Aktiv, ikke rekrutterende
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Newcastle UniversityRekrutteringMyotonisk dystrofiDet Forenede Kongerige
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National Eye Institute (NEI)Aktiv, ikke rekrutterendeNethindedegeneration | ABCA4-relaterede retinopatierForenede Stater
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REGENXBIO Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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NS Pharma, Inc.Aktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater, Canada
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PTC TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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Catabasis PharmaceuticalsAfsluttetMuskeldystrofi, DuchenneForenede Stater
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Processa PharmaceuticalsAfsluttetDuchennes muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater, Korea, Republikken, Italien, Det Forenede Kongerige, Canada, Polen, Spanien, Frankrig, Tyskland, Belgien, Australien, Tjekkiet, Serbien, Grækenland, Argentina, Bulgarien, Danmark, Ungarn, Indien, Irland, Israel, Me... og mere
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)AfsluttetDuchennes muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...Afsluttet
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Nanoscope Therapeutics Inc.Afsluttet
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Nanoscope Therapeutics Inc.Tilmelding efter invitationStargardts sygdomForenede Stater
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Craig McDonald, MDCardero Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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PfizerAktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater
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Processa PharmaceuticalsAfsluttet
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Sarepta Therapeutics, Inc.Rekruttering
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Sarepta Therapeutics, Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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PTC TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater, Canada
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PTC TherapeuticsAfsluttet