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Kliniske forsøg med X-bundet svær kombineret immundefekt
I alt 1621 resultater
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Stanford UniversityAfsluttetUdviklingshæmning | Fragilt X syndromForenede Stater
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University Hospital, ToursAfsluttetSunde frivillige | Autisme | Fragilt-X syndrom (FXS)Frankrig
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University Hospital, BrestUkendtDysautonomi | Maskulinitet | MECP2-relateret svær neonatal encefalopatiFrankrig
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Stanford UniversityAfsluttetIntellektuel handicap | Fragilt X syndromForenede Stater
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... og andre samarbejdspartnereAfsluttetDowns syndrom | Fragilt X syndromSpanien
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Viking Therapeutics, Inc.RekrutteringAdrenomyeloneuropati Form (AMN) af X-bundet adrenoleukodystrofi (X-ALD)Forenede Stater, Frankrig, Tyskland, Italien, Det Forenede Kongerige
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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ACADIA Pharmaceuticals Inc.Afsluttet
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Afsluttet
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Rett Syndrome Research TrustDuke UniversityAfsluttet
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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Assistance Publique Hopitaux De MarseilleAfsluttet
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Medical University of ViennaAfsluttet
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases...AfsluttetHypophosphatemisk rakitt, X Linked DominantForenede Stater
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Rekruttering
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Neurogene Inc.RekrutteringRett syndromForenede Stater
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University of SienaRekruttering
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Vyant BioIkke rekrutterer endnu
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Rett Syndrome Research TrustVanderbilt University Medical CenterAfsluttetRett syndromForenede Stater
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHAfsluttetRett syndromCanada, Australien, Det Forenede Kongerige
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ACADIA Pharmaceuticals Inc.Afsluttet
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Rett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetRett syndromForenede Stater
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Ukendt
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Assistance Publique Hopitaux De MarseilleUkendt
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationAfsluttet
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Sheba Medical CenterUltragenyx Pharmaceutical IncUkendt
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Central Hospital, Nancy, FranceAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...Afsluttet
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Sheba Medical CenterUkendt
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Maastricht University Medical CenterAfsluttet
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet