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Kliniske forsøg med X-bundet lymfoproliferativt syndrom 2
I alt 4378 resultater
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Central Hospital, Nancy, FranceAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...Afsluttet
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Sheba Medical CenterUkendt
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Maastricht University Medical CenterAfsluttet
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... og andre samarbejdspartnereIkke rekrutterer endnuFragilt X syndrom
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Stanford UniversityThe John Merck FundAfsluttetFragilt X syndrom | Forstyrrende adfærdForenede Stater
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Stanford UniversityAfsluttetUdviklingshæmning | Fragilt X syndromForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetImmunproliferativ lidelseForenede Stater
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttet
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Neuren Pharmaceuticals Limitedrettsyndrome.orgAfsluttet
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkendtRett syndromDanmark, Israel
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Rigshospitalet, DenmarkAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncAfsluttet
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Boston Children's HospitalInternational Rett Syndrome FoundationAfsluttet
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The Cleveland ClinicAfsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationAfsluttet
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National Taiwan University HospitalUkendt
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Maastricht University Medical CenterAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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Stanford UniversityAfsluttetIntellektuel handicap | Fragilt X syndromForenede Stater
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Stanford UniversityAfsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuel udviklingsforstyrrelse (IDD)Forenede Stater
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetRett syndrom | CDKL5 lidelse | MECP2 Duplikationslidelse | FOXG1 syndromForenede Stater
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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Shenzhen Geno-Immune Medical InstituteUkendt
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)AfsluttetFragilt X syndromForenede Stater
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... og andre samarbejdspartnereRekrutteringX Linked Myotubular MyopatiDet Forenede Kongerige, Canada, Forenede Stater
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Newcastle-upon-Tyne Hospitals NHS TrustRekrutteringX-bundet myotubulær myopati | Centronukleær myopati | Myotubulær myopati | Myotubulær myopati 1 | Myotubulær (Centronuclear) myopati | Centronuclear Myopati, X-LinkedDet Forenede Kongerige
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyAfsluttetEpilepsi | Livskvalitet | Dysbiose | Rett syndromItalien
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Newron Pharmaceuticals SPAAfsluttetRett syndromForenede Stater, Indien, Det Forenede Kongerige, Australien, Italien
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCDKL5 | Rett syndrom | MECP2 duplikering | FOXG1 lidelserForenede Stater
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X syndromForenede Stater