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Søg i kliniske forsøg efter: Inborn errors of metabolism
I alt 431108 resultater
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Alexion Pharmaceuticals, Inc.Ikke rekrutterer endnuHypofosfatasiForenede Stater, Taiwan, Thailand, Vietnam, Det Forenede Kongerige, Korea, Republikken, Israel, Italien, Australien, Kalkun, Frankrig, Polen, Tyskland, Spanien, Belgien, Kina, Canada, Brasilien, Argentina, Mexico
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Alexion Pharmaceuticals, Inc.RekrutteringHypofosfatasiItalien, Spanien, Israel, Korea, Republikken, Belgien, Tyskland, Forenede Stater, Kina, Frankrig, Taiwan, Østrig, Japan, Indien, Australien, Argentina, Polen, Kalkun, Brasilien, Canada, Thailand, Det Forenede Kongerige, Slovakiet, Tj...
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncRekrutteringMellemkædet Acyl-CoA-dehydrogenase-mangelForenede Stater
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.RekrutteringMellemkædet Acyl-CoA-dehydrogenase-mangelForenede Stater
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Tasly Pharmaceutical Group Co., LtdIkke rekrutterer endnu
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UK Kidney AssociationRekrutteringVaskulitis | AL Amyloidose | Tuberøs sklerose | Fabrys sygdom | Cystinuri | Fokal Segmental Glomerulosklerose | IgA nefropati | Bartter syndrom | Pure Red Cell Aplasia | Membranøs nefropati | Atypisk hæmolytisk uræmisk syndrom | Autosomal dominant polycystisk nyresygdom | Cystinose | Nephronophthisis | BK nefropati | Calcip... og andre forholdDet Forenede Kongerige
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SanofiRekrutteringOsteochondrodysplasiAustralien, Spanien, Korea, Republikken, Kina, Italien
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Lysosomal and Rare Disorders Research and Treatment...Rekruttering
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First Affiliated Hospital Bengbu Medical CollegeRekruttering
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Boston Children's HospitalChildren's Hospital Medical Center, CincinnatiRekrutteringShwachman-diamant syndrom | Shwachman-Diamond Syndrome-lignendeForenede Stater
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Urica Therapeutics Inc.RekrutteringHyperurikæmi | GigtForenede Stater
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Oregon Health and Science UniversityUniversity of Oregon; Oregon State UniversityRekrutteringKulhydratintoleranceForenede Stater
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Assiut UniversityIkke rekrutterer endnuHjerte-kar-sygdomme | Wilsons sygdom
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SanofiRekruttering
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University Hospital OlomoucUniversity Hospital Ostrava; Tomas Bata Hospital, Czech Republic; General... og andre samarbejdspartnereRekrutteringCushings syndrom | Fæokromocytom | Binyrebarkcarcinom | Adrenal Cortex Sygdomme | Binyrebark adenom | Binyretumor | Adrenalektomi; Status | Binyremasse | Adrenal hyperplasi | Adrenal sygdom | Binyrebark tumor | Conn Adenoma | BinyremetastaseTjekkiet
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Sciotec Diagnostic Technologies GmbHIkke rekrutterer endnuFruktoseintoleranceØstrig
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Inozyme PharmaRekrutteringENERGY 3-undersøgelsen: Evaluering af effektivitet og sikkerhed af INZ-701 hos børn med ENPP1-mangelGeneraliseret arteriel forkalkning af spædbørn | Autosomal recessiv hypophosphatæmisk rakitt | Ectonucleotid Pyrophosphatase/Phosphodiesterase1 mangelForenede Stater, Det Forenede Kongerige, Canada
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Institut National de la Santé Et de la Recherche...RekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multipel Sulfatase mangel sygdom | Mucopolysaccharidosis IXFrankrig
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TakedaRekrutteringHunters syndromCanada, Frankrig
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Masonic Cancer Center, University of MinnesotaRekruttering
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SanofiRekrutteringFabrys sygdomForenede Stater
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Minovia Therapeutics Ltd.RekrutteringMitokondrielle sygdomme | Pearsons syndromIsrael
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Alexion Pharmaceuticals, Inc.Ikke rekrutterer endnu
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Second Affiliated Hospital, School of Medicine,...Ikke rekrutterer endnu
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Beijing Suncadia Pharmaceuticals Co., LtdIkke rekrutterer endnuHomozygot familiær hyperkolesterolæmi
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRekruttering
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NewAmsterdam PharmaRekrutteringDyslipidæmi | Hyperkolesterolæmi | Familiær hyperkolesterolæmi | Højt kolesterol | ASCVDForenede Stater
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Guangdong Provincial Hospital of Traditional Chinese...RekrutteringAkut smerte | Akupunktur | Akut gigt gigtKina
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Lumos DiagnosticsAptatek BiosciencesRekruttering
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National Institute of Diabetes and Digestive and...RekrutteringLipodystrofiForenede Stater
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Nacuity Pharmaceuticals, Inc.Rekruttering
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRekruttering
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Fundación Española de Hematología y HemoterapíaRekrutteringGauchers sygdom | Syre SphingoMyelinase mangelSpanien
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Virginia Commonwealth UniversityIkke rekrutterer endnuAmyloidose, arveligForenede Stater
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SanofiRekruttering
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MED-LIFE DISCOVERIES LPBioPharma Services, IncRekrutteringRhizomelic Chondrodysplasia PunctataCanada
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Ikke rekrutterer endnu
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Xinhua Hospital, Shanghai Jiao Tong University...Rekruttering
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Rekruttering
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Institut National de la Santé Et de la Recherche...RekrutteringNeurofibromatose type 1 | Iktyose | Ektodermal dysplasi | Albinisme | Pemphigus | Slimhinde Pemphigoid | Nedarvet Epidermolysis Bullosa | Palmoplantar Keratodermi | Incontinentia PigmentiFrankrig
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Centre Hospitalier Universitaire DijonIkke rekrutterer endnuKosaki overvækst syndrom | Penttinens syndromFrankrig
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... og andre samarbejdspartnereRekrutteringGlykogenopbevaringssygdom type II | Pompes sygdom (sen debut)Italien
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Merck Sharp & Dohme LLCRekrutteringHyperkolesterolæmi | Familiær hyperkolesterolæmiForenede Stater, Taiwan, Israel, Argentina, Japan, Korea, Republikken, Kalkun, Colombia, Kina, Mexico, Tyskland, Italien, Sydafrika, Spanien
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTDRekruttering
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Institut National de la Santé Et de la Recherche...RekrutteringPrader-Willi syndrom | Angelman syndrom | Beckwith-Wiedemanns syndrom | Pseudohypoparathyroidisme | Silver Russell syndrom | Forbigående neonatal diabetes mellitus | Temple syndrom | Kagami-Ogata syndrom | Familiær tidlig pubertetFrankrig
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Medical University of ViennaRekrutteringPompes sygdom | McArdles sygdomØstrig
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Beijing Tiantan HospitalRekruttering
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsIkke rekrutterer endnuArvelig amyloidose | Guillain-Barre syndrom | Kronisk inflammatorisk demyeliniserende polyneuropatiDet Forenede Kongerige
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRekrutteringIdiopatisk pulmonal hæmosiderose | LeflunomidKina
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GeneScience Pharmaceuticals Co., Ltd.Huashan HospitalRekrutteringGigt Flare | Akut gigtKina